Fabry Disease Registry & Pregnancy Sub-registry
Launched by GENZYME, A SANOFI COMPANY · Sep 13, 2005
Trial Information
Current as of July 24, 2025
Recruiting
Keywords
ClinConnect Summary
The Fabry Disease Registry and Pregnancy Sub-registry is an ongoing study that gathers information about people with Fabry disease, a genetic condition that affects how the body processes certain fats. This program is observational, meaning that it doesn’t involve any experimental treatments. Instead, patients receive regular medical care from their doctors, and their health outcomes are monitored over time. The main goals of the registry are to better understand how Fabry disease varies in different individuals, track its progression, and help improve patient care. For pregnant women with Fabry disease, the Pregnancy Sub-registry specifically looks at pregnancy outcomes, collecting information about their health and the health of their babies.
To participate in the Fabry Registry, individuals need to have a confirmed diagnosis of Fabry disease, which can be determined through specific enzyme tests or genetic testing. For the Pregnancy Sub-registry, women must be enrolled in the main registry and either currently pregnant or have been pregnant in the past. Participants can expect to provide information about their medical history and pregnancy, and if they agree, their baby's growth will be tracked for up to three years after birth. Overall, this research aims to improve understanding and care for those living with Fabry disease.
Gender
ALL
Eligibility criteria
- • Inclusion Criteria
- • Fabry Registry: All patients with a confirmed diagnosis of Fabry disease who have signed the informed consent and patient authorization form(s) are eligible for inclusion. Confirmed diagnosis is defined as a documented deficiency in plasma or leukocyte αGAL (alpha-galactosidase) enzyme activity and/or mutation(s) in the gene coding for αGAL.
- * Fabry Pregnancy Sub-registry:
- * Eligible women must:
- • be enrolled in the Fabry Registry.
- • be pregnant, or have been pregnant with appropriate medical documentation available.
- • provide a signed informed consent and authorization form(s) to participate in the Sub-Registry prior to any Sub-Registry-related data collection being performed.
- • Exclusion Criteria Fabry Registry: There are no exclusion criteria. Fabry Pregnancy Sub-registry: There are no exclusion criteria.
About Genzyme, A Sanofi Company
Genzyme, a Sanofi company, is a global leader in biotechnology dedicated to developing innovative therapies for rare and complex diseases. With a strong focus on patient-centric solutions, Genzyme leverages advanced research and development capabilities to address unmet medical needs across various therapeutic areas, including neurology, oncology, and genetic disorders. Committed to scientific excellence and collaboration, Genzyme aims to improve patient outcomes through the discovery and commercialization of high-quality biopharmaceuticals, while upholding the highest standards of safety and efficacy in clinical trials.
Contacts
Jennifer Cobb
Immunology at National Institute of Allergy and Infectious Diseases (NIAID)
Locations
Sofia, , Bulgaria
Taichung, , Taiwan
L'hospitalet De Llobregat, Cataluña, Spain
New Orleans, Louisiana, United States
Minneapolis, Minnesota, United States
Rochester, New York, United States
Caba, Buenos Aires, Argentina
Turku, , Finland
Nizhny Novgorod, , Russian Federation
Pécs, , Hungary
Minneapolis, Minnesota, United States
New York, New York, United States
Irvine, California, United States
Birmingham, Alabama, United States
Birmingham, Alabama, United States
Phoenix, Arizona, United States
Tucson, Arizona, United States
Little Rock, Arkansas, United States
Little Rock, Arkansas, United States
Aurora, California, United States
Irvine, California, United States
Los Angeles, California, United States
Los Angeles, California, United States
Los Angeles, California, United States
Orange, California, United States
Palo Alto, California, United States
Sacramento, California, United States
Sacramento, California, United States
San Bernardino, California, United States
San Diego, California, United States
San Francisco, California, United States
New Haven, Connecticut, United States
Washington, District Of Columbia, United States
Coral Springs, Florida, United States
Gainesville, Florida, United States
Jacksonville, Florida, United States
Miami, Florida, United States
Oakland, Florida, United States
Tampa, Florida, United States
Decatur, Georgia, United States
Chicago, Illinois, United States
Chicago, Illinois, United States
Indianapolis, Indiana, United States
Iowa City, Iowa, United States
Kansas City, Kansas, United States
Louisville, Kentucky, United States
Baton Rouge, Louisiana, United States
New Orleans, Louisiana, United States
Portland, Maine, United States
Baltimore, Maryland, United States
Boston, Massachusetts, United States
Boston, Massachusetts, United States
Boston, Massachusetts, United States
Springfield, Massachusetts, United States
Ann Arbor, Michigan, United States
Detroit, Michigan, United States
Grand Rapids, Michigan, United States
Grand Rapids, Michigan, United States
Minneapolis, Minnesota, United States
Minneapolis, Minnesota, United States
Minneapolis, Minnesota, United States
Columibia, Missouri, United States
Saint Louis, Missouri, United States
Billings, Montana, United States
Helena, Montana, United States
Omaha, Nebraska, United States
Las Vegas, Nevada, United States
Camden, New Jersey, United States
Hackensack, New Jersey, United States
Morristown, New Jersey, United States
New Brunswick, New Jersey, United States
Paterson, New Jersey, United States
Manhasset, New York, United States
New York, New York, United States
New York, New York, United States
New York, New York, United States
Rochester, New York, United States
Syracuse, New York, United States
Valhalla, New York, United States
Charlotte, North Carolina, United States
Durham, North Carolina, United States
Cincinnati, Ohio, United States
Cleveland, Ohio, United States
Cleveland, Ohio, United States
Columbus, Ohio, United States
Columbus, Ohio, United States
Dublin, Ohio, United States
Portland, Oregon, United States
Portland, Oregon, United States
Danville, Pennsylvania, United States
Hershey, Pennsylvania, United States
Philadelphia, Pennsylvania, United States
Philadelphia, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Providence, Rhode Island, United States
Greenville, South Carolina, United States
Nashville, Tennessee, United States
Dallas, Texas, United States
Fort Worth, Texas, United States
Salt Lake City, Utah, United States
Charlottesville, Virginia, United States
Fairfax, Virginia, United States
Norfolk, Virginia, United States
Seattle, Washington, United States
Seattle, Washington, United States
Tacoma, Washington, United States
Milwaukee, Wisconsin, United States
Calgary, Alberta, Canada
Halifax, Nova Scotia, Canada
Létavértes, , Hungary
Pécs, , Hungary
Sopron, , Hungary
Niigata, , Japan
Busan, , Korea, Republic Of
Dubai, , United Arab Emirates
Yangsan, , Korea, Republic Of
Indianapolis, Indiana, United States
Boston, Massachusetts, United States
Slovenj Gradec, , Slovenia
Kingston, Ontario, Canada
Létavértes, , Hungary
Sopron, , Hungary
Columibia, Missouri, United States
Syracuse, New York, United States
Columbus, Ohio, United States
Dublin, Ohio, United States
Curitiba, Paraná, Brazil
Calgary, Alberta, Canada
Würzburg, , Germany
Seoul, , Korea, Republic Of
Slovenj Gradec, , Slovenia
New Haven, Connecticut, United States
Chicago, Illinois, United States
Portland, Maine, United States
La Coruña, , Spain
Secunderabad, , India
Seattle, Washington, United States
Santiago, , Chile
Kuala Lumpur, , Malaysia
Tao Yuan County, , Taiwan
Birmingham, Alabama, United States
Sacramento, California, United States
San Bernardino, California, United States
San Francisco, California, United States
Jacksonville, Florida, United States
Chicago, Illinois, United States
Kansas City, Kansas, United States
Baton Rouge, Louisiana, United States
Portland, Maine, United States
Boston, Massachusetts, United States
Ann Arbor, Michigan, United States
Detroit, Michigan, United States
Saint Louis, Missouri, United States
Las Vegas, Nevada, United States
Morristown, New Jersey, United States
New Brunswick, New Jersey, United States
Manhasset, New York, United States
New York, New York, United States
New York, New York, United States
Rochester, New York, United States
Charlotte, North Carolina, United States
Dublin, Ohio, United States
Philadelphia, Pennsylvania, United States
Salt Lake City, Utah, United States
Charlottesville, Virginia, United States
Tacoma, Washington, United States
Buenos Aires, , Argentina
Westmead, New South Wales, Australia
Brisbane, Queensland, Australia
Antwerp, , Belgium
Antwerp, , Belgium
Brussels, , Belgium
Liège, , Belgium
Cuiabá, Mato Grosso, Brazil
Florianopolis, Santa Catarina, Brazil
São Paulo, , Brazil
Toronto, Ontario, Canada
Santiago, , Chile
Shanghai, , China
Turku, , Finland
Bordeaux, , France
Gießen, , Germany
Kowloon, , Hong Kong
Firenze, , Italy
Yangsan, Gyeongsangnam Do, Korea, Republic Of
Busan, , Korea, Republic Of
Jeju Si, , Korea, Republic Of
Bergen, , Norway
A Coruña, , Spain
Barcelona, , Spain
Tarragona, , Spain
Göteborg, , Sweden
Tainan City, , Taiwan
Tainan City, , Taiwan
Taipei City, , Taiwan
London, , United Kingdom
London, , United Kingdom
Salford, , United Kingdom
Marseille, , France
Barakaldo, , Spain
Birmingham, Alabama, United States
Jacksonville, Florida, United States
Irvine, California, United States
Chicago, Illinois, United States
Recife, Pernambuco, Brazil
Kobe, , Japan
Niigata, , Japan
Tampa, Florida, United States
Abeno Ku, Osaka, Japan
Las Vegas, Nevada, United States
Sherbrooke, Quebec, Canada
Bassano Del Grappa (Vi), , Italy
Firenze, , Italy
Dubai, , United Arab Emirates
Kaohsiung Hsien,, , Taiwan
Taichung City, , Taiwan
Los Angeles, California, United States
Orange, California, United States
Philadelphia, Pennsylvania, United States
Bruxelles, , Belgium
Kowloon, , Hong Kong
Roma, , Italy
Setagaya, Tokyo, Japan
Putz City, Chia Yi, , Taiwan
Aurora, Colorado, United States
Saint Louis, Missouri, United States
New Orleans, Louisiana, United States
Fort Worth, Texas, United States
Antwerpen, , Belgium
Niigata Shi, Niigata, Japan
La Coruña, , Spain
Tarragona, , Spain
Los Angeles, California, United States
Ann Arbor, Michigan, United States
New Brunswick, New Jersey, United States
Philadelphia, Pennsylvania, United States
Nashville, Tennessee, United States
Jette, , Belgium
Leuven, , Belgium
Uberlândia, Minas Gerais, Brazil
Bron Cedex, , France
Coral Springs, Florida, United States
Decatur, Georgia, United States
Providence, Rhode Island, United States
Beijing, , China
Daejeon, , Korea, Republic Of
Seoul, , Korea, Republic Of
Putz City, Chia Yi, , Taiwan
Coral Springs, Florida, United States
Washington, District Of Columbia, United States
Firenze, , Italy
Milano, , Italy
Chiba, , Japan
Washington, District Of Columbia, United States
Tampa, Florida, United States
Berlin, , Germany
Kolkata, , India
Cleveland, Ohio, United States
Bangkok, , Thailand
Herston, Queensland, Australia
Porto, , Portugal
Seattle, Washington, United States
Kuala Lumpur, , Malaysia
Phoenix, Arizona, United States
Indianapolis, Indiana, United States
Marseille, , France
Manchester, , United Kingdom
Niigata Shi, Niigata, Japan
Minneapolis, Minnesota, United States
Rimini, , Italy
Udine, , Italy
Providence, Rhode Island, United States
Ahmedabad, , India
Vellore, , India
Tainan, , Taiwan
Birmingham, Alabama, United States
Jacksonville, Florida, United States
Baton Rouge, Louisiana, United States
Boston, Massachusetts, United States
Springfield, Massachusetts, United States
San Bernardino, California, United States
Minneapolis, Minnesota, United States
Morristown, New Jersey, United States
New York, New York, United States
Charlotte, North Carolina, United States
Danville, Pennsylvania, United States
Hershey, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Dallas, Texas, United States
Catamarca, , Argentina
La Rioja, , Argentina
Parkville, Victoria, Australia
Bruxelles, , Belgium
Cuiabá, Mato Grosso, Brazil
Vancouver, British Columbia, Canada
Vancouver, British Columbia, Canada
London, Ontario, Canada
Antofagasta, , Chile
Coquimbo, , Chile
Bogotá, , Colombia
Rijena, , Croatia
Tartu, , Estonia
Turku, , Finland
Berlin, , Germany
Budapest, , Hungary
Secunderabad, , India
Monza (Mb), , Italy
Vittoria (Rg), , Italy
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Vilnius, , Lithuania
Manila, , Philippines
Warszawa, , Poland
Lisboa, , Portugal
Moscow, , Russian Federation
Novi Sad, , Serbia
Barcelona, , Spain
Barcelona, , Spain
Chiayi, , Taiwan
Hualien, , Taiwan
New Taipei City, , Taiwan
Taipei, , Taiwan
Bangkok, , Thailand
Bangkok, , Thailand
London, , United Kingdom
Hanoi, , Vietnam
Palo Alto, California, United States
Saint Louis, Missouri, United States
Portland, Oregon, United States
Ciudad Autónoma De Buenos Aires, Buenos Aires, Argentina
Jinan, , China
Nanjing, , China
Modena, , Italy
Vilnius, , Lithuania
Barakaldo, , Spain
Morristown, New Jersey, United States
Antwerpen, , Belgium
Nangoku Shi, Kochi, Japan
Callao, , Peru
San Diego, California, United States
Washington, District Of Columbia, United States
Paterson, New Jersey, United States
Manhasset, New York, United States
Greenville, South Carolina, United States
Vellore, , India
San Diego, California, United States
Little Rock, Arkansas, United States
Little Rock, Arkansas, United States
New Haven, Connecticut, United States
Antwerpen, , Belgium
Brussels, , Belgium
Campinas, São Paulo, Brazil
Halifax, Nova Scotia, Canada
Montreal, Quebec, Canada
Copenhagen, , Denmark
Ahmedabad, , India
Udine, , Italy
Setagaya, Tokyo, Japan
Chiba, , Japan
Callao, , Peru
Bucuresti, , Romania
Barcelona, , Spain
Tainan, , Taiwan
Belfast, , United Kingdom
Birmingham, , United Kingdom
Sherbrooke, Quebec, Canada
Kolkata, , India
Louisville, Kentucky, United States
New York, New York, United States
Durham, North Carolina, United States
Cleveland, Ohio, United States
Seattle, Washington, United States
Buenos Aires, , Argentina
Moncton, New Brunswick, Canada
Tainan, , Taiwan
Bucuresti, , Romania
Edmonton, Alberta, Canada
St Priest En Jarez, , France
Jakarta, , Indonesia
Cluj Napoca, , Romania
Brasília, Distrito Federal, Brazil
Jacksonville, Florida, United States
Boston, Massachusetts, United States
Seattle, Washington, United States
København ø, , Denmark
Little Rock, Arkansas, United States
Gainesville, Florida, United States
Jacksonville, Florida, United States
Iowa City, Iowa, United States
Louisville, Kentucky, United States
Ann Arbor, Michigan, United States
Camden, New Jersey, United States
Manhasset, New York, United States
New York, New York, United States
Dallas, Texas, United States
Parkville, Victoria, Australia
Cuiabá, Mato Grosso, Brazil
Edmonton, Alberta, Canada
Halifax, Nova Scotia, Canada
Toronto, Ontario, Canada
Montreal, Quebec, Canada
Beijing, , China
Rijena, , Croatia
Bordeaux, , France
Limoges Cedex, , France
Strasbourg, , France
Gießen, , Germany
Würzburg, , Germany
Genova, , Italy
Milano, , Italy
Monza (Mb), , Italy
Vittoria (Rg), , Italy
Seoul, , Korea, Republic Of
Yangsan, , Korea, Republic Of
Amsterdam, , Netherlands
Amsterdam, , Netherlands
Manila, , Philippines
Porto, , Portugal
Bucuresti, , Romania
Barcelona, , Spain
Barcelona, , Spain
Tarragona, , Spain
Stockholm, , Sweden
Chiayi, , Taiwan
Bangkok, , Thailand
Detroit, Michigan, United States
Barcelona, , Spain
Sacramento, California, United States
Iquique, , Chile
Vilnius, , Lithuania
La Coruña, , Spain
Oakland, Florida, United States
Tacoma, Washington, United States
Buenos Aires, , Argentina
Brasília, , Brazil
Campinas, , Brazil
Cuiabá, , Brazil
Curitiba, , Brazil
Ourinhos, , Brazil
Uberlândia, , Brazil
København, , Denmark
La Coruna, , Spain
La Coruna, , Spain
Tampa, Florida, United States
La Coruña, , Spain
Irvine, California, United States
Portland, Maine, United States
Baltimore, Maryland, United States
Grand Rapids, Michigan, United States
Tacoma, Washington, United States
Adelaide, South Australia, Australia
Recife, Pernambuco, Brazil
São Paulo, , Brazil
Zagreb, , Croatia
London, , United Kingdom
Manchester, , United Kingdom
Hangzhou, , China
Kaohsiung City, , Taiwan
Oakland, California, United States
Irvine, California, United States
New York, New York, United States
St. John's, Newfoundland And Labrador, Canada
Kobe Shi, Hyogo, , Japan
Little Rock, Arkansas, United States
San Bernardino, California, United States
Kansas City, Kansas, United States
Grand Rapids, Michigan, United States
Omaha, Nebraska, United States
Las Vegas, Nevada, United States
Cleveland, Ohio, United States
Philadelphia, Pennsylvania, United States
Salt Lake City, Utah, United States
Norfolk, Virginia, United States
La Rioja, , Argentina
Santa Fe, , Argentina
Westmead, New South Wales, Australia
Herston, Queensland, Australia
Curitiba, Paraná, Brazil
Recife, Pernambuco, Brazil
Florianopolis, Santa Catarina, Brazil
São Paulo, , Brazil
Calgary, Alberta, Canada
Vancouver, British Columbia, Canada
Moncton, New Brunswick, Canada
Toronto, Ontario, Canada
Antofagasta, , Chile
Coquimbo, , Chile
Copenhagen, , Denmark
Kobe Shi, Hyogo, , Japan
Yangsan Si, Gyeongsangnam Do, Korea, Republic Of
Busan, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Kuwait, , Kuwait
Vilnius, , Lithuania
Bergen, , Norway
Lisboa, , Portugal
Novi Sad, , Serbia
Singapore, , Singapore
Göteborg, , Sweden
Kaohsiung Hsien,, , Taiwan
Vallenar, , Chile
Taichung City, , Taiwan
Taipei, , Taiwan
Taipei, , Taiwan
Bangkok, , Thailand
London, , United Kingdom
London, , United Kingdom
Manchester, , United Kingdom
Hanoi, , Vietnam
Sofia, , Bulgaria
St. John's, Newfoundland And Labrador, Canada
Los Angeles, California, United States
Tapejara, Rio Grande Do Sul, Brazil
London, , United Kingdom
Daejeon, , Korea, Republic Of
Salford, , United Kingdom
Miami, Florida, United States
Decatur, Georgia, United States
Boston, Massachusetts, United States
Barcelona, , Spain
Garches, , France
Orange, California, United States
Taipei, , Taiwan
Udine, , Italy
Firenze, , Italy
Torino, , Italy
Belfast, , United Kingdom
Palo Alto, California, United States
Cleveland, Ohio, United States
Providence, Rhode Island, United States
Nizhny Novgorod, , Russian Federation
New Taipei City, , Taiwan
Seoul, , Korea, Republic Of
Baton Rouge, Louisiana, United States
Catamarca, , Argentina
Liège, , Belgium
Valhalla, New York, United States
Charlotte, North Carolina, United States
Columbus, Ohio, United States
Fort Worth, Texas, United States
Westmead, New South Wales, Australia
Uberlândia, Minas Gerais, Brazil
Winnipeg, Manitoba, Canada
Bucuresti, , Romania
Barcelona, , Spain
Palo Alto, California, United States
Omaha, Nebraska, United States
Budapest, , Hungary
Sacramento, California, United States
Grand Rapids, Michigan, United States
Garches, , France
Seoul, , Korea, Republic Of
Hualien, , Taiwan
Cincinnati, Ohio, United States
Feira De Santana, Bahia, Brazil
London, , United Kingdom
Bratislava, , Slovakia
Dallas, Texas, United States
Paterson, New Jersey, United States
Taipei, , Taiwan
Vallenar, , Chile
Little Rock, Arkansas, United States
Los Angeles, California, United States
Los Angeles, California, United States
Sacramento, California, United States
New Haven, Connecticut, United States
Gainesville, Florida, United States
Miami, Florida, United States
Aurora, Illinois, United States
Iowa City, Iowa, United States
Louisville, Kentucky, United States
Baltimore, Maryland, United States
Boston, Massachusetts, United States
Springfield, Massachusetts, United States
Grand Rapids, Michigan, United States
Minneapolis, Minnesota, United States
Columibia, Missouri, United States
Billings, Montana, United States
Helena, Montana, United States
Syracuse, New York, United States
Cincinnati, Ohio, United States
Columbus, Ohio, United States
Portland, Oregon, United States
Portland, Oregon, United States
Danville, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Greenville, South Carolina, United States
Nashville, Tennessee, United States
Fairfax, Virginia, United States
Seattle, Washington, United States
Milwaukee, Wisconsin, United States
Curitiba, Paraná, Brazil
Tapejara, Rio Grande Do Sul, Brazil
Ourinhos, São Paulo, Brazil
Moncton, New Brunswick, Canada
Kingston, Ontario, Canada
Jinan, , China
Limoges, , France
Strasbourg, , France
Tokyo, , Japan
Seoul, Gyeonggi Do, Korea, Republic Of
Amsterdam, , Netherlands
Amsterdam, , Netherlands
A Coruña, , Spain
Kaohsiung City, , Taiwan
Taipei City, , Taiwan
Taoyuan City, , Taiwan
Dublin, Ohio, United States
Danville, Pennsylvania, United States
Kaohsiung City, , Taiwan
Khon Kaen, , Thailand
Cambridge, Cambridgeshire, United Kingdom
Little Rock, Arkansas, United States
Münster, , Germany
Chicago, Illinois, United States
Modena, , Italy
Napoli, , Italy
Birmingham, Alabama, United States
Phoenix, Arizona, United States
Tucson, Arizona, United States
Los Angeles, California, United States
Oakland, California, United States
Sacramento, California, United States
San Francisco, California, United States
Denver, Colorado, United States
Decatur, Georgia, United States
Chicago, Illinois, United States
Detroit, Michigan, United States
Grand Rapids, Michigan, United States
Helena, Montana, United States
Hackensack, New Jersey, United States
Columbus, Ohio, United States
Philadelphia, Pennsylvania, United States
Salt Lake City, Utah, United States
Caba, Buenos Aires, Argentina
Westmead, New South Wales, Australia
Florianopolis, Santa Catarina, Brazil
Limoges Cedex, , France
Marseille, , France
Saint Priest En Jarez, , France
Stockholm, , Sweden
Milano, , Italy
Seoul, Seoul Teukbyeolsi, Korea, Republic Of
Seoul, Seoul Teukbyeolsi, Korea, Republic Of
Manchester, , United Kingdom
Hershey, Pennsylvania, United States
Al Mubarraz, , Saudi Arabia
Tucson, Arizona, United States
Grand Rapids, Michigan, United States
Philadelphia, Pennsylvania, United States
Fort Worth, Texas, United States
Seoul, , Korea, Republic Of
Gainesville, Florida, United States
Indianapolis, Indiana, United States
Feira De Santana, Bahia, Brazil
New York, New York, United States
Kaohsiung, , Taiwan
Chicago, Illinois, United States
Charlottesville, Virginia, United States
Bratislava, , Slovakia
Denver, Colorado, United States
Brasília, Distrito Federal, Brazil
Ourinhos, São Paulo, Brazil
San Francisco, California, United States
Helena, Montana, United States
Portland, Oregon, United States
Portland, Oregon, United States
Tapejara, Rio Grande Do Sul, Brazil
Suwon Si, , Korea, Republic Of
Warszawa, , Poland
Vancouver, British Columbia, Canada
Campinas, São Paulo, Brazil
New York, New York, United States
Minneapolis, Minnesota, United States
Rochester, New York, United States
Oakland, California, United States
Orange, California, United States
Boston, Massachusetts, United States
Camden, New Jersey, United States
Cleveland, Ohio, United States
São Paulo, , Brazil
Columbus, Ohio, United States
Sofia, , Bulgaria
Calgary, Alberta, Canada
Létavértes, , Hungary
Sopron, , Hungary
Milano, , Italy
Kobe, Hyogo, Japan
Seoul, , Korea, Republic Of
Suwon Si, , Korea, Republic Of
Kuwait, , Kuwait
Saint Peterburg, , Russian Federation
Kaohsiung, , Taiwan
Taichung, , Taiwan
Taichung, , Taiwan
Taipei, , Taiwan
Birmingham, England, United Kingdom
Salford, Manchester, United Kingdom
New York, New York, United States
Cambridge, Cambridgeshire, United Kingdom
Birmingham, , United Kingdom
Valhalla, New York, United States
Cleveland, Ohio, United States
Billings, Montana, United States
Toronto, Ontario, Canada
Jeonnam, , Korea, Republic Of
Seoul, , Korea, Republic Of
Coral Springs, Florida, United States
Miami, Florida, United States
Valhalla, New York, United States
Fairfax, Virginia, United States
New Orleans, Louisiana, United States
Los Angeles, California, United States
Norfolk, Virginia, United States
Abeno Ku, Osaka, Japan
Greenville, South Carolina, United States
Hackensack, New Jersey, United States
Cleveland, Ohio, United States
Hershey, Pennsylvania, United States
Uberlândia, Minas Gerais, Brazil
Yangsan, Gyeongsangnam Do, Korea, Republic Of
Barakaldo, Pais Vasco, Spain
Khon Kaen, , Thailand
Münster, , Germany
San Diego, California, United States
Springfield, Massachusetts, United States
Birmingham, Alabama, United States
Phoenix, Arizona, United States
Tucson, Arizona, United States
Baltimore, Maryland, United States
Boston, Massachusetts, United States
Columibia, Missouri, United States
Billings, Montana, United States
Columbus, Ohio, United States
Pittsburgh, Pennsylvania, United States
Seattle, Washington, United States
Tacoma, Washington, United States
Ciudad Autónoma De Buenos Aires, Buenos Aires, Argentina
Adelaide, South Australia, Australia
Antwerpen, , Belgium
Leuven, , Belgium
Seraing, , Belgium
Campinas, São Paulo, Brazil
Saint Priest En Jarez, , France
Jakarta, , Indonesia
Jalan Pahang, , Malaysia
Cluj Napoca, , Romania
Moscow, , Russian Federation
Barcelona, , Spain
Tainan, , Taiwan
Jacksonville, Florida, United States
Irvine, California, United States
Barcelona, , Spain
Birmingham, , United Kingdom
Hackensack, New Jersey, United States
New Brunswick, New Jersey, United States
Fairfax, Virginia, United States
Perth, Western Australia, Australia
Brussels, , Belgium
Jette, , Belgium
Bron Cedex, , France
Los Angeles, California, United States
Minneapolis, Minnesota, United States
Rimini, , Italy
Torino, , Italy
Jeju Si, , Korea, Republic Of
Los Angeles, California, United States
Lille, , France
Vigo, , Spain
Pécs, , Hungary
Milwaukee, Wisconsin, United States
Brussel, , Belgium
København ø, , Denmark
Tartu, , Estonia
Birmingham, Alabama, United States
Oakland, Virginia, United States
Nanjing, , China
Bangkok, , Thailand
Syracuse, New York, United States
Durham, North Carolina, United States
Cincinnati, Ohio, United States
Nashville, Tennessee, United States
Charlottesville, Virginia, United States
Shanghai, , China
Bogotá, , Colombia
Zagreb, , Croatia
Praha 2, , Czechia
Jeonnam, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Saint Peterburg, , Russian Federation
Boston, Massachusetts, United States
Brasília, Distrito Federal, Brazil
Strasbourg, , France
Santa Fe, , Argentina
Perth, Western Australia, Australia
Barcelona, , Spain
Buenos Aires, , Argentina
London, Ontario, Canada
Hangzhou, , China
Jinan, , China
Minneapolis, Minnesota, United States
Norfolk, Virginia, United States
Curitiba, , Brazil
Campinas, , Brazil
Ourinhos, , Brazil
Roma, , Italy
Vilnius, , Lithuania
Al Mubarraz, , Saudi Arabia
Kansas City, Kansas, United States
Praha 2, , Czechia
Milwaukee, Wisconsin, United States
Ourinhos, São Paulo, Brazil
Napoli, , Italy
Tao Yuan County, , Taiwan
Sacramento, California, United States
Iowa City, Iowa, United States
Nangoku Shi, Kochi, Japan
Cambridge, Cambridgeshire, United Kingdom
Omaha, Nebraska, United States
Paterson, New Jersey, United States
Brussels, , Belgium
Feira De Santana, Bahia, Brazil
Vigo, , Spain
Minneapolis, Minnesota, United States
Durham, North Carolina, United States
Seraing, , Belgium
Yangsan Si, Gyeongsangnam Do, Korea, Republic Of
Singapore, , Singapore
Sofia, , Bulgaria
Winnipeg, Manitoba, Canada
Iquique, , Chile
Lille, , France
Bassano Del Grappa (Vi), , Italy
Genova, , Italy
Jalan Pahang, , Malaysia
Patients applied
Trial Officials
Study Director
Study Director
Genzyme, a Sanofi Company
Timeline
First submit
Trial launched
Trial updated
Estimated completion
Not reported
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