Fabry Disease Registry & Pregnancy Sub-registry
Launched by GENZYME, A SANOFI COMPANY · Sep 13, 2005
Trial Information
Current as of July 23, 2025
Recruiting
Keywords
ClinConnect Summary
The Fabry Disease Registry and Pregnancy Sub-registry is an ongoing study that gathers information about people with Fabry disease, a genetic condition that affects how the body processes certain fats. This program is observational, meaning that it doesn’t involve any experimental treatments. Instead, patients receive regular medical care from their doctors, and their health outcomes are monitored over time. The main goals of the registry are to better understand how Fabry disease varies in different individuals, track its progression, and help improve patient care. For pregnant women with Fabry disease, the Pregnancy Sub-registry specifically looks at pregnancy outcomes, collecting information about their health and the health of their babies.
To participate in the Fabry Registry, individuals need to have a confirmed diagnosis of Fabry disease, which can be determined through specific enzyme tests or genetic testing. For the Pregnancy Sub-registry, women must be enrolled in the main registry and either currently pregnant or have been pregnant in the past. Participants can expect to provide information about their medical history and pregnancy, and if they agree, their baby's growth will be tracked for up to three years after birth. Overall, this research aims to improve understanding and care for those living with Fabry disease.
Gender
ALL
Eligibility criteria
- • Inclusion Criteria
- • Fabry Registry: All patients with a confirmed diagnosis of Fabry disease who have signed the informed consent and patient authorization form(s) are eligible for inclusion. Confirmed diagnosis is defined as a documented deficiency in plasma or leukocyte αGAL (alpha-galactosidase) enzyme activity and/or mutation(s) in the gene coding for αGAL.
- * Fabry Pregnancy Sub-registry:
- * Eligible women must:
- • be enrolled in the Fabry Registry.
- • be pregnant, or have been pregnant with appropriate medical documentation available.
- • provide a signed informed consent and authorization form(s) to participate in the Sub-Registry prior to any Sub-Registry-related data collection being performed.
- • Exclusion Criteria Fabry Registry: There are no exclusion criteria. Fabry Pregnancy Sub-registry: There are no exclusion criteria.
About Genzyme, A Sanofi Company
Genzyme, a Sanofi company, is a global leader in biotechnology dedicated to developing innovative therapies for rare and complex diseases. With a strong focus on patient-centric solutions, Genzyme leverages advanced research and development capabilities to address unmet medical needs across various therapeutic areas, including neurology, oncology, and genetic disorders. Committed to scientific excellence and collaboration, Genzyme aims to improve patient outcomes through the discovery and commercialization of high-quality biopharmaceuticals, while upholding the highest standards of safety and efficacy in clinical trials.
Contacts
Jennifer Cobb
Immunology at National Institute of Allergy and Infectious Diseases (NIAID)
Locations
Phoenix, Arizona, United States
Little Rock, Arkansas, United States
Los Angeles, California, United States
Los Angeles, California, United States
Orange, California, United States
Palo Alto, California, United States
Sacramento, California, United States
San Bernardino, California, United States
San Diego, California, United States
San Francisco, California, United States
New Haven, Connecticut, United States
Washington, District Of Columbia, United States
Gainesville, Florida, United States
Jacksonville, Florida, United States
Miami, Florida, United States
Decatur, Georgia, United States
Chicago, Illinois, United States
Indianapolis, Indiana, United States
Iowa City, Iowa, United States
Louisville, Kentucky, United States
Baltimore, Maryland, United States
Boston, Massachusetts, United States
Springfield, Massachusetts, United States
Ann Arbor, Michigan, United States
Detroit, Michigan, United States
Minneapolis, Minnesota, United States
Minneapolis, Minnesota, United States
Saint Louis, Missouri, United States
Omaha, Nebraska, United States
Las Vegas, Nevada, United States
Hackensack, New Jersey, United States
Morristown, New Jersey, United States
New Brunswick, New Jersey, United States
Paterson, New Jersey, United States
Manhasset, New York, United States
New York, New York, United States
New York, New York, United States
Rochester, New York, United States
Syracuse, New York, United States
Cleveland, Ohio, United States
Columbus, Ohio, United States
Dublin, Ohio, United States
Philadelphia, Pennsylvania, United States
Philadelphia, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Providence, Rhode Island, United States
Greenville, South Carolina, United States
Dallas, Texas, United States
Charlottesville, Virginia, United States
Norfolk, Virginia, United States
Seattle, Washington, United States
Seattle, Washington, United States
Tacoma, Washington, United States
Milwaukee, Wisconsin, United States
Ciudad Autónoma De Buenos Aires, Buenos Aires, Argentina
Buenos Aires, , Argentina
Westmead, New South Wales, Australia
Bruxelles, , Belgium
Leuven, , Belgium
Calgary, Alberta, Canada
Edmonton, Alberta, Canada
Vancouver, British Columbia, Canada
Winnipeg, Manitoba, Canada
Moncton, New Brunswick, Canada
London, Ontario, Canada
Toronto, Ontario, Canada
Sherbrooke, Quebec, Canada
Bogotá, , Colombia
København ø, , Denmark
Pécs, , Hungary
Ahmedabad, , India
Kolkata, , India
Secunderabad, , India
Vellore, , India
Jakarta, , Indonesia
Udine, , Italy
Busan, , Korea, Republic Of
Daejeon, , Korea, Republic Of
Jeonnam, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Yangsan, , Korea, Republic Of
Kuwait, , Kuwait
Jalan Pahang, , Malaysia
Kuala Lumpur, , Malaysia
Amsterdam, , Netherlands
Manila, , Philippines
Warszawa, , Poland
Singapore, , Singapore
Bratislava, , Slovakia
Chiayi, , Taiwan
Hualien, , Taiwan
Kaohsiung Hsien,, , Taiwan
Kaohsiung, , Taiwan
New Taipei City, , Taiwan
Putz City, Chia Yi, , Taiwan
Taichung City, , Taiwan
Tainan, , Taiwan
Tainan, , Taiwan
Taipei, , Taiwan
Taipei, , Taiwan
Tao Yuan County, , Taiwan
Bangkok, , Thailand
Bangkok, , Thailand
Bangkok, , Thailand
Khon Kaen, , Thailand
Dubai, , United Arab Emirates
Birmingham, , United Kingdom
London, , United Kingdom
London, , United Kingdom
London, , United Kingdom
Manchester, , United Kingdom
Salford, , United Kingdom
Hanoi, , Vietnam
Birmingham, Alabama, United States
Birmingham, Alabama, United States
Tucson, Arizona, United States
Little Rock, Arkansas, United States
Aurora, California, United States
Irvine, California, United States
Los Angeles, California, United States
Sacramento, California, United States
Coral Springs, Florida, United States
Oakland, Florida, United States
Tampa, Florida, United States
Chicago, Illinois, United States
Kansas City, Kansas, United States
Baton Rouge, Louisiana, United States
New Orleans, Louisiana, United States
Portland, Maine, United States
Boston, Massachusetts, United States
Boston, Massachusetts, United States
Grand Rapids, Michigan, United States
Grand Rapids, Michigan, United States
Minneapolis, Minnesota, United States
Columibia, Missouri, United States
Billings, Montana, United States
Helena, Montana, United States
Camden, New Jersey, United States
New York, New York, United States
Valhalla, New York, United States
Charlotte, North Carolina, United States
Durham, North Carolina, United States
Cincinnati, Ohio, United States
Cleveland, Ohio, United States
Columbus, Ohio, United States
Portland, Oregon, United States
Portland, Oregon, United States
Danville, Pennsylvania, United States
Hershey, Pennsylvania, United States
Nashville, Tennessee, United States
Fort Worth, Texas, United States
Salt Lake City, Utah, United States
Fairfax, Virginia, United States
Caba, Buenos Aires, Argentina
Catamarca, , Argentina
La Rioja, , Argentina
Santa Fe, , Argentina
Westmead, New South Wales, Australia
Herston, Queensland, Australia
Adelaide, South Australia, Australia
Parkville, Victoria, Australia
Perth, Western Australia, Australia
Antwerpen, , Belgium
Antwerpen, , Belgium
Brussels, , Belgium
Brussel, , Belgium
Liège, , Belgium
Seraing, , Belgium
Feira De Santana, Bahia, Brazil
Brasília, Distrito Federal, Brazil
Cuiabá, Mato Grosso, Brazil
Uberlândia, Minas Gerais, Brazil
Curitiba, Paraná, Brazil
Recife, Pernambuco, Brazil
Tapejara, Rio Grande Do Sul, Brazil
Florianopolis, Santa Catarina, Brazil
Campinas, São Paulo, Brazil
Ourinhos, São Paulo, Brazil
São Paulo, , Brazil
Sofia, , Bulgaria
Sofia, , Bulgaria
Vancouver, British Columbia, Canada
St. John's, Newfoundland And Labrador, Canada
Halifax, Nova Scotia, Canada
Halifax, Nova Scotia, Canada
Kingston, Ontario, Canada
Toronto, Ontario, Canada
Montreal, Quebec, Canada
Antofagasta, , Chile
Coquimbo, , Chile
Iquique, , Chile
Santiago, , Chile
Vallenar, , Chile
Beijing, , China
Shanghai, , China
Rijena, , Croatia
Zagreb, , Croatia
Praha 2, , Czechia
Copenhagen, , Denmark
Tartu, , Estonia
Turku, , Finland
Bordeaux, , France
Bron Cedex, , France
Garches, , France
Lille, , France
Limoges Cedex, , France
Marseille, , France
Saint Priest En Jarez, , France
Strasbourg, , France
Berlin, , Germany
Gießen, , Germany
Münster, , Germany
Würzburg, , Germany
Budapest, , Hungary
Létavértes, , Hungary
Pécs, , Hungary
Sopron, , Hungary
Bassano Del Grappa (Vi), , Italy
Firenze, , Italy
Firenze, , Italy
Genova, , Italy
Milano, , Italy
Milano, , Italy
Modena, , Italy
Monza (Mb), , Italy
Napoli, , Italy
Rimini, , Italy
Roma, , Italy
Torino, , Italy
Vittoria (Rg), , Italy
Nangoku Shi, Kochi, Japan
Abeno Ku, Osaka, Japan
Setagaya, Tokyo, Japan
Chiba, , Japan
Kobe Shi, Hyogo, , Japan
Niigata, , Japan
Busan, , Korea, Republic Of
Jeju Si, , Korea, Republic Of
Seoul, , Korea, Republic Of
Suwon Si, , Korea, Republic Of
Yangsan, , Korea, Republic Of
Vilnius, , Lithuania
Vilnius, , Lithuania
Amsterdam, , Netherlands
Bergen, , Norway
Callao, , Peru
Lisboa, , Portugal
Porto, , Portugal
Bucuresti, , Romania
Bucuresti, , Romania
Cluj Napoca, , Romania
Moscow, , Russian Federation
Nizhny Novgorod, , Russian Federation
Saint Peterburg, , Russian Federation
Al Mubarraz, , Saudi Arabia
Novi Sad, , Serbia
Slovenj Gradec, , Slovenia
Barakaldo, , Spain
Barcelona, , Spain
Barcelona, , Spain
Barcelona, , Spain
Barcelona, , Spain
Barcelona, , Spain
Barcelona, , Spain
La Coruña, , Spain
La Coruña, , Spain
Tarragona, , Spain
Vigo, , Spain
Göteborg, , Sweden
Stockholm, , Sweden
Kaohsiung City, , Taiwan
Taichung, , Taiwan
Taipei, , Taiwan
Dubai, , United Arab Emirates
Cambridge, Cambridgeshire, United Kingdom
Belfast, , United Kingdom
Létavértes, , Hungary
Hangzhou, , China
Phoenix, Arizona, United States
Little Rock, Arkansas, United States
Los Angeles, California, United States
Los Angeles, California, United States
Orange, California, United States
Palo Alto, California, United States
Sacramento, California, United States
San Bernardino, California, United States
San Diego, California, United States
San Francisco, California, United States
Aurora, Colorado, United States
New Haven, Connecticut, United States
Washington, District Of Columbia, United States
Gainesville, Florida, United States
Jacksonville, Florida, United States
Jacksonville, Florida, United States
Miami, Florida, United States
Oakland, Florida, United States
Decatur, Georgia, United States
Chicago, Illinois, United States
Indianapolis, Indiana, United States
Iowa City, Iowa, United States
Louisville, Kentucky, United States
Baltimore, Maryland, United States
Boston, Massachusetts, United States
Springfield, Massachusetts, United States
Ann Arbor, Michigan, United States
Detroit, Michigan, United States
Minneapolis, Minnesota, United States
Minneapolis, Minnesota, United States
Saint Louis, Missouri, United States
Omaha, Nebraska, United States
Las Vegas, Nevada, United States
Hackensack, New Jersey, United States
Morristown, New Jersey, United States
New Brunswick, New Jersey, United States
Paterson, New Jersey, United States
Manhasset, New York, United States
New York, New York, United States
New York, New York, United States
Rochester, New York, United States
Syracuse, New York, United States
Cleveland, Ohio, United States
Columbus, Ohio, United States
Dublin, Ohio, United States
Philadelphia, Pennsylvania, United States
Philadelphia, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Providence, Rhode Island, United States
Greenville, South Carolina, United States
Dallas, Texas, United States
Charlottesville, Virginia, United States
Norfolk, Virginia, United States
Seattle, Washington, United States
Seattle, Washington, United States
Tacoma, Washington, United States
Milwaukee, Wisconsin, United States
Buenos Aires, , Argentina
Calgary, Alberta, Canada
København, , Denmark
Birmingham, Alabama, United States
Birmingham, Alabama, United States
Tucson, Arizona, United States
Little Rock, Arkansas, United States
Irvine, California, United States
Los Angeles, California, United States
Sacramento, California, United States
Coral Springs, Florida, United States
Tampa, Florida, United States
Chicago, Illinois, United States
Kansas City, Kansas, United States
Baton Rouge, Louisiana, United States
New Orleans, Louisiana, United States
Portland, Maine, United States
Boston, Massachusetts, United States
Boston, Massachusetts, United States
Grand Rapids, Michigan, United States
Grand Rapids, Michigan, United States
Minneapolis, Minnesota, United States
Columibia, Missouri, United States
Billings, Montana, United States
Helena, Montana, United States
Camden, New Jersey, United States
New York, New York, United States
Valhalla, New York, United States
Charlotte, North Carolina, United States
Durham, North Carolina, United States
Cincinnati, Ohio, United States
Cleveland, Ohio, United States
Columbus, Ohio, United States
Portland, Oregon, United States
Portland, Oregon, United States
Danville, Pennsylvania, United States
Hershey, Pennsylvania, United States
Nashville, Tennessee, United States
Fort Worth, Texas, United States
Salt Lake City, Utah, United States
Fairfax, Virginia, United States
Brasília, , Brazil
Campinas, , Brazil
Cuiabá, , Brazil
Curitiba, , Brazil
Ourinhos, , Brazil
Uberlândia, , Brazil
Sopron, , Hungary
La Coruna, , Spain
La Coruna, , Spain
Irvine, California, United States
Oakland, California, United States
Tacoma, Washington, United States
Yangsan Si, Gyeongsangnam Do, Korea, Republic Of
Nanjing, , China
Niigata Shi, Niigata, Japan
Oakland, Virginia, United States
New York, New York, United States
Jette, , Belgium
Jinan, , China
Irvine, California, United States
Denver, Colorado, United States
Kowloon, , Hong Kong
L'hospitalet De Llobregat, Cataluña, Spain
Hangzhou, , China
Pécs, , Hungary
Udine, , Italy
Zagreb, , Croatia
Little Rock, Arkansas, United States
Little Rock, Arkansas, United States
Los Angeles, California, United States
Oakland, California, United States
San Bernardino, California, United States
San Diego, California, United States
New Haven, Connecticut, United States
Washington, District Of Columbia, United States
Jacksonville, Florida, United States
Jacksonville, Florida, United States
Tampa, Florida, United States
Decatur, Georgia, United States
Chicago, Illinois, United States
Chicago, Illinois, United States
Indianapolis, Indiana, United States
Louisville, Kentucky, United States
Portland, Maine, United States
Baltimore, Maryland, United States
Boston, Massachusetts, United States
Boston, Massachusetts, United States
Springfield, Massachusetts, United States
Ann Arbor, Michigan, United States
Grand Rapids, Michigan, United States
Grand Rapids, Michigan, United States
Minneapolis, Minnesota, United States
Minneapolis, Minnesota, United States
Columibia, Missouri, United States
Saint Louis, Missouri, United States
Omaha, Nebraska, United States
Morristown, New Jersey, United States
New Brunswick, New Jersey, United States
Paterson, New Jersey, United States
Manhasset, New York, United States
New York, New York, United States
New York, New York, United States
Rochester, New York, United States
Syracuse, New York, United States
Valhalla, New York, United States
Cleveland, Ohio, United States
Cleveland, Ohio, United States
Columbus, Ohio, United States
Dublin, Ohio, United States
Philadelphia, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Providence, Rhode Island, United States
Greenville, South Carolina, United States
Nashville, Tennessee, United States
Dallas, Texas, United States
Fort Worth, Texas, United States
Charlottesville, Virginia, United States
Fairfax, Virginia, United States
Norfolk, Virginia, United States
Tacoma, Washington, United States
Milwaukee, Wisconsin, United States
Ciudad Autónoma De Buenos Aires, Buenos Aires, Argentina
Westmead, New South Wales, Australia
Westmead, New South Wales, Australia
Adelaide, South Australia, Australia
Antwerpen, , Belgium
Leuven, , Belgium
Sofia, , Bulgaria
Moncton, New Brunswick, Canada
København ø, , Denmark
Gießen, , Germany
Kowloon, , Hong Kong
Ahmedabad, , India
Kolkata, , India
Secunderabad, , India
Vellore, , India
Jakarta, , Indonesia
Yangsan Si, Gyeongsangnam Do, Korea, Republic Of
Daejeon, , Korea, Republic Of
Jeonnam, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Kuwait, , Kuwait
Jalan Pahang, , Malaysia
Manila, , Philippines
Warszawa, , Poland
Bucuresti, , Romania
Singapore, , Singapore
Bratislava, , Slovakia
Chiayi, , Taiwan
Hualien, , Taiwan
Kaohsiung Hsien,, , Taiwan
Kaohsiung, , Taiwan
New Taipei City, , Taiwan
Putz City, Chia Yi, , Taiwan
Taichung City, , Taiwan
Tainan, , Taiwan
Tainan, , Taiwan
Taipei, , Taiwan
Taipei, , Taiwan
Taipei, , Taiwan
Tao Yuan County, , Taiwan
Bangkok, , Thailand
Bangkok, , Thailand
Bangkok, , Thailand
Khon Kaen, , Thailand
Birmingham, , United Kingdom
Hanoi, , Vietnam
Gainesville, Florida, United States
Iowa City, Iowa, United States
Hackensack, New Jersey, United States
Buenos Aires, , Argentina
Bruxelles, , Belgium
Bogotá, , Colombia
Udine, , Italy
Yangsan, Gyeongsangnam Do, Korea, Republic Of
Kuala Lumpur, , Malaysia
Amsterdam, , Netherlands
London, , United Kingdom
Birmingham, Alabama, United States
Birmingham, Alabama, United States
Phoenix, Arizona, United States
Tucson, Arizona, United States
Irvine, California, United States
Los Angeles, California, United States
Los Angeles, California, United States
Orange, California, United States
Palo Alto, California, United States
Sacramento, California, United States
Sacramento, California, United States
San Francisco, California, United States
Denver, Colorado, United States
Coral Springs, Florida, United States
Miami, Florida, United States
Kansas City, Kansas, United States
Baton Rouge, Louisiana, United States
New Orleans, Louisiana, United States
Boston, Massachusetts, United States
Detroit, Michigan, United States
Minneapolis, Minnesota, United States
Billings, Montana, United States
Helena, Montana, United States
Las Vegas, Nevada, United States
New York, New York, United States
Charlotte, North Carolina, United States
Durham, North Carolina, United States
Cincinnati, Ohio, United States
Columbus, Ohio, United States
Portland, Oregon, United States
Danville, Pennsylvania, United States
Hershey, Pennsylvania, United States
Philadelphia, Pennsylvania, United States
Salt Lake City, Utah, United States
Seattle, Washington, United States
Seattle, Washington, United States
Caba, Buenos Aires, Argentina
Catamarca, , Argentina
La Rioja, , Argentina
Santa Fe, , Argentina
Herston, Queensland, Australia
Parkville, Victoria, Australia
Perth, Western Australia, Australia
Antwerpen, , Belgium
Brussels, , Belgium
Jette, , Belgium
Liège, , Belgium
Seraing, , Belgium
Feira De Santana, Bahia, Brazil
Brasília, Distrito Federal, Brazil
Cuiabá, Mato Grosso, Brazil
Uberlândia, Minas Gerais, Brazil
Curitiba, Paraná, Brazil
Recife, Pernambuco, Brazil
Tapejara, Rio Grande Do Sul, Brazil
Florianopolis, Santa Catarina, Brazil
Campinas, São Paulo, Brazil
Ourinhos, São Paulo, Brazil
São Paulo, , Brazil
Sofia, , Bulgaria
Calgary, Alberta, Canada
Edmonton, Alberta, Canada
Vancouver, British Columbia, Canada
Vancouver, British Columbia, Canada
Winnipeg, Manitoba, Canada
St. John's, Newfoundland And Labrador, Canada
Halifax, Nova Scotia, Canada
London, Ontario, Canada
Toronto, Ontario, Canada
Toronto, Ontario, Canada
Montreal, Quebec, Canada
Sherbrooke, Quebec, Canada
Antofagasta, , Chile
Coquimbo, , Chile
Iquique, , Chile
Vallenar, , Chile
Jinan, , China
Nanjing, , China
Rijena, , Croatia
Praha 2, , Czechia
Copenhagen, , Denmark
Tartu, , Estonia
Turku, , Finland
Bordeaux, , France
Bron Cedex, , France
Garches, , France
Lille, , France
Limoges Cedex, , France
Marseille, , France
Saint Priest En Jarez, , France
Strasbourg, , France
Berlin, , Germany
Münster, , Germany
Würzburg, , Germany
Budapest, , Hungary
Létavértes, , Hungary
Sopron, , Hungary
Bassano Del Grappa (Vi), , Italy
Firenze, , Italy
Firenze, , Italy
Genova, , Italy
Milano, , Italy
Milano, , Italy
Modena, , Italy
Monza (Mb), , Italy
Napoli, , Italy
Rimini, , Italy
Roma, , Italy
Torino, , Italy
Vittoria (Rg), , Italy
Nangoku Shi, Kochi, Japan
Niigata Shi, Niigata, Japan
Abeno Ku, Osaka, Japan
Setagaya, Tokyo, Japan
Chiba, , Japan
Kobe Shi, Hyogo, , Japan
Busan, , Korea, Republic Of
Seoul, , Korea, Republic Of
Suwon Si, , Korea, Republic Of
Vilnius, , Lithuania
Vilnius, , Lithuania
Bergen, , Norway
Callao, , Peru
Lisboa, , Portugal
Porto, , Portugal
Bucuresti, , Romania
Cluj Napoca, , Romania
Moscow, , Russian Federation
Nizhny Novgorod, , Russian Federation
Saint Peterburg, , Russian Federation
Al Mubarraz, , Saudi Arabia
Novi Sad, , Serbia
Slovenj Gradec, , Slovenia
Barakaldo, , Spain
Barcelona, , Spain
Barcelona, , Spain
Barcelona, , Spain
Barcelona, , Spain
Barcelona, , Spain
Barcelona, , Spain
La Coruña, , Spain
La Coruña, , Spain
Tarragona, , Spain
Vigo, , Spain
Göteborg, , Sweden
Stockholm, , Sweden
Kaohsiung City, , Taiwan
Taichung, , Taiwan
Cambridge, Cambridgeshire, United Kingdom
Belfast, , United Kingdom
London, , United Kingdom
London, , United Kingdom
Manchester, , United Kingdom
Salford, , United Kingdom
Phoenix, Arizona, United States
Little Rock, Arkansas, United States
Los Angeles, California, United States
Los Angeles, California, United States
Oakland, California, United States
Orange, California, United States
Palo Alto, California, United States
Sacramento, California, United States
San Bernardino, California, United States
San Diego, California, United States
San Francisco, California, United States
New Haven, Connecticut, United States
Washington, District Of Columbia, United States
Gainesville, Florida, United States
Jacksonville, Florida, United States
Jacksonville, Florida, United States
Miami, Florida, United States
Decatur, Georgia, United States
Chicago, Illinois, United States
Indianapolis, Indiana, United States
Iowa City, Iowa, United States
Louisville, Kentucky, United States
Baltimore, Maryland, United States
Boston, Massachusetts, United States
Springfield, Massachusetts, United States
Ann Arbor, Michigan, United States
Detroit, Michigan, United States
Minneapolis, Minnesota, United States
Minneapolis, Minnesota, United States
Saint Louis, Missouri, United States
Omaha, Nebraska, United States
Las Vegas, Nevada, United States
Hackensack, New Jersey, United States
Morristown, New Jersey, United States
New Brunswick, New Jersey, United States
Paterson, New Jersey, United States
Manhasset, New York, United States
New York, New York, United States
New York, New York, United States
Rochester, New York, United States
Syracuse, New York, United States
Cleveland, Ohio, United States
Columbus, Ohio, United States
Dublin, Ohio, United States
Philadelphia, Pennsylvania, United States
Philadelphia, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Providence, Rhode Island, United States
Greenville, South Carolina, United States
Dallas, Texas, United States
Charlottesville, Virginia, United States
Norfolk, Virginia, United States
Seattle, Washington, United States
Seattle, Washington, United States
Tacoma, Washington, United States
Milwaukee, Wisconsin, United States
Brussels, , Belgium
Moncton, New Brunswick, Canada
Seoul, Gyeonggi Do, Korea, Republic Of
Kaohsiung City, , Taiwan
Taichung, , Taiwan
Tainan City, , Taiwan
Tainan City, , Taiwan
Taipei City, , Taiwan
Taoyuan City, , Taiwan
Birmingham, , United Kingdom
London, , United Kingdom
London, , United Kingdom
Manchester, , United Kingdom
Birmingham, Alabama, United States
Birmingham, Alabama, United States
Tucson, Arizona, United States
Little Rock, Arkansas, United States
Irvine, California, United States
Los Angeles, California, United States
Sacramento, California, United States
Coral Springs, Florida, United States
Tampa, Florida, United States
Aurora, Illinois, United States
Chicago, Illinois, United States
Kansas City, Kansas, United States
Baton Rouge, Louisiana, United States
New Orleans, Louisiana, United States
Portland, Maine, United States
Boston, Massachusetts, United States
Boston, Massachusetts, United States
Grand Rapids, Michigan, United States
Grand Rapids, Michigan, United States
Minneapolis, Minnesota, United States
Columibia, Missouri, United States
Billings, Montana, United States
Helena, Montana, United States
Camden, New Jersey, United States
New York, New York, United States
Valhalla, New York, United States
Charlotte, North Carolina, United States
Durham, North Carolina, United States
Cincinnati, Ohio, United States
Cleveland, Ohio, United States
Columbus, Ohio, United States
Portland, Oregon, United States
Portland, Oregon, United States
Danville, Pennsylvania, United States
Hershey, Pennsylvania, United States
Nashville, Tennessee, United States
Fort Worth, Texas, United States
Salt Lake City, Utah, United States
Fairfax, Virginia, United States
Buenos Aires, , Argentina
Brisbane, Queensland, Australia
Antwerp, , Belgium
Antwerp, , Belgium
Brussels, , Belgium
Feira De Santana, Bahia, Brazil
Brasília, Distrito Federal, Brazil
Cuiabá, Mato Grosso, Brazil
Uberlândia, Minas Gerais, Brazil
Curitiba, Paraná, Brazil
Recife, Pernambuco, Brazil
Tapejara, Rio Grande Do Sul, Brazil
Florianopolis, Santa Catarina, Brazil
Campinas, São Paulo, Brazil
Ourinhos, São Paulo, Brazil
São Paulo, , Brazil
Kingston, Ontario, Canada
Santiago, , Chile
Beijing, , China
Jinan, , China
Shanghai, , China
Turku, , Finland
Limoges, , France
Marseille, , France
St Priest En Jarez, , France
Strasbourg, , France
Kobe, , Japan
Niigata, , Japan
Tokyo, , Japan
Yangsan, Gyeongsangnam Do, Korea, Republic Of
Jeju Si, , Korea, Republic Of
Vilnius, , Lithuania
Amsterdam, , Netherlands
A Coruña, , Spain
A Coruña, , Spain
Tarragona, , Spain
Taipei City, , Taiwan
Cambridge, Cambridgeshire, United Kingdom
Cleveland, Ohio, United States
Calgary, Alberta, Canada
Seoul, Seoul Teukbyeolsi, Korea, Republic Of
Seoul, Seoul Teukbyeolsi, Korea, Republic Of
Birmingham, England, United Kingdom
Curitiba, , Brazil
Campinas, , Brazil
Ourinhos, , Brazil
São Paulo, , Brazil
Kobe, Hyogo, Japan
Barakaldo, Pais Vasco, Spain
Salford, Manchester, United Kingdom
Manchester, , United Kingdom
Patients applied
Trial Officials
Study Director
Study Director
Genzyme, a Sanofi Company
Timeline
First submit
Trial launched
Trial updated
Estimated completion
Not reported
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