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Search / Trial NCT00196742

Fabry Disease Registry & Pregnancy Sub-registry

Launched by GENZYME, A SANOFI COMPANY · Sep 13, 2005

Trial Information

Current as of July 24, 2025

Recruiting

Keywords

Alpha Galactosidase A A Gal (Alpha Galactosidase) Fabry Gl3 (Globotriaosylceramide) Anderson Fabry Disease Angiokeratomas Gla Deficiency (Gene Deficiency) Errors In Metabolism

ClinConnect Summary

The Fabry Disease Registry and Pregnancy Sub-registry is an ongoing study that gathers information about people with Fabry disease, a genetic condition that affects how the body processes certain fats. This program is observational, meaning that it doesn’t involve any experimental treatments. Instead, patients receive regular medical care from their doctors, and their health outcomes are monitored over time. The main goals of the registry are to better understand how Fabry disease varies in different individuals, track its progression, and help improve patient care. For pregnant women with Fabry disease, the Pregnancy Sub-registry specifically looks at pregnancy outcomes, collecting information about their health and the health of their babies.

To participate in the Fabry Registry, individuals need to have a confirmed diagnosis of Fabry disease, which can be determined through specific enzyme tests or genetic testing. For the Pregnancy Sub-registry, women must be enrolled in the main registry and either currently pregnant or have been pregnant in the past. Participants can expect to provide information about their medical history and pregnancy, and if they agree, their baby's growth will be tracked for up to three years after birth. Overall, this research aims to improve understanding and care for those living with Fabry disease.

Gender

ALL

Eligibility criteria

  • Inclusion Criteria
  • Fabry Registry: All patients with a confirmed diagnosis of Fabry disease who have signed the informed consent and patient authorization form(s) are eligible for inclusion. Confirmed diagnosis is defined as a documented deficiency in plasma or leukocyte αGAL (alpha-galactosidase) enzyme activity and/or mutation(s) in the gene coding for αGAL.
  • * Fabry Pregnancy Sub-registry:
  • * Eligible women must:
  • be enrolled in the Fabry Registry.
  • be pregnant, or have been pregnant with appropriate medical documentation available.
  • provide a signed informed consent and authorization form(s) to participate in the Sub-Registry prior to any Sub-Registry-related data collection being performed.
  • Exclusion Criteria Fabry Registry: There are no exclusion criteria. Fabry Pregnancy Sub-registry: There are no exclusion criteria.

About Genzyme, A Sanofi Company

Genzyme, a Sanofi company, is a global leader in biotechnology dedicated to developing innovative therapies for rare and complex diseases. With a strong focus on patient-centric solutions, Genzyme leverages advanced research and development capabilities to address unmet medical needs across various therapeutic areas, including neurology, oncology, and genetic disorders. Committed to scientific excellence and collaboration, Genzyme aims to improve patient outcomes through the discovery and commercialization of high-quality biopharmaceuticals, while upholding the highest standards of safety and efficacy in clinical trials.

Locations

Sofia, , Bulgaria

Taichung, , Taiwan

L'hospitalet De Llobregat, Cataluña, Spain

New Orleans, Louisiana, United States

Minneapolis, Minnesota, United States

Rochester, New York, United States

Caba, Buenos Aires, Argentina

Turku, , Finland

Nizhny Novgorod, , Russian Federation

Pécs, , Hungary

Minneapolis, Minnesota, United States

New York, New York, United States

Irvine, California, United States

Birmingham, Alabama, United States

Birmingham, Alabama, United States

Phoenix, Arizona, United States

Tucson, Arizona, United States

Little Rock, Arkansas, United States

Little Rock, Arkansas, United States

Aurora, California, United States

Irvine, California, United States

Los Angeles, California, United States

Los Angeles, California, United States

Los Angeles, California, United States

Orange, California, United States

Palo Alto, California, United States

Sacramento, California, United States

Sacramento, California, United States

San Bernardino, California, United States

San Diego, California, United States

San Francisco, California, United States

New Haven, Connecticut, United States

Washington, District Of Columbia, United States

Coral Springs, Florida, United States

Gainesville, Florida, United States

Jacksonville, Florida, United States

Miami, Florida, United States

Oakland, Florida, United States

Tampa, Florida, United States

Decatur, Georgia, United States

Chicago, Illinois, United States

Chicago, Illinois, United States

Indianapolis, Indiana, United States

Iowa City, Iowa, United States

Kansas City, Kansas, United States

Louisville, Kentucky, United States

Baton Rouge, Louisiana, United States

New Orleans, Louisiana, United States

Portland, Maine, United States

Baltimore, Maryland, United States

Boston, Massachusetts, United States

Boston, Massachusetts, United States

Boston, Massachusetts, United States

Springfield, Massachusetts, United States

Ann Arbor, Michigan, United States

Detroit, Michigan, United States

Grand Rapids, Michigan, United States

Grand Rapids, Michigan, United States

Minneapolis, Minnesota, United States

Minneapolis, Minnesota, United States

Minneapolis, Minnesota, United States

Columibia, Missouri, United States

Saint Louis, Missouri, United States

Billings, Montana, United States

Helena, Montana, United States

Omaha, Nebraska, United States

Las Vegas, Nevada, United States

Camden, New Jersey, United States

Hackensack, New Jersey, United States

Morristown, New Jersey, United States

New Brunswick, New Jersey, United States

Paterson, New Jersey, United States

Manhasset, New York, United States

New York, New York, United States

New York, New York, United States

New York, New York, United States

Rochester, New York, United States

Syracuse, New York, United States

Valhalla, New York, United States

Charlotte, North Carolina, United States

Durham, North Carolina, United States

Cincinnati, Ohio, United States

Cleveland, Ohio, United States

Cleveland, Ohio, United States

Columbus, Ohio, United States

Columbus, Ohio, United States

Dublin, Ohio, United States

Portland, Oregon, United States

Portland, Oregon, United States

Danville, Pennsylvania, United States

Hershey, Pennsylvania, United States

Philadelphia, Pennsylvania, United States

Philadelphia, Pennsylvania, United States

Pittsburgh, Pennsylvania, United States

Providence, Rhode Island, United States

Greenville, South Carolina, United States

Nashville, Tennessee, United States

Dallas, Texas, United States

Fort Worth, Texas, United States

Salt Lake City, Utah, United States

Charlottesville, Virginia, United States

Fairfax, Virginia, United States

Norfolk, Virginia, United States

Seattle, Washington, United States

Seattle, Washington, United States

Tacoma, Washington, United States

Milwaukee, Wisconsin, United States

Calgary, Alberta, Canada

Halifax, Nova Scotia, Canada

Létavértes, , Hungary

Pécs, , Hungary

Sopron, , Hungary

Niigata, , Japan

Busan, , Korea, Republic Of

Dubai, , United Arab Emirates

Yangsan, , Korea, Republic Of

Indianapolis, Indiana, United States

Boston, Massachusetts, United States

Slovenj Gradec, , Slovenia

Kingston, Ontario, Canada

Létavértes, , Hungary

Columibia, Missouri, United States

Sopron, , Hungary

Curitiba, Paraná, Brazil

Calgary, Alberta, Canada

Würzburg, , Germany

Seoul, , Korea, Republic Of

Slovenj Gradec, , Slovenia

New Haven, Connecticut, United States

Syracuse, New York, United States

Columbus, Ohio, United States

Dublin, Ohio, United States

Chicago, Illinois, United States

Portland, Maine, United States

La Coruña, , Spain

Seattle, Washington, United States

Santiago, , Chile

Kuala Lumpur, , Malaysia

Secunderabad, , India

Birmingham, Alabama, United States

Sacramento, California, United States

San Bernardino, California, United States

San Francisco, California, United States

Jacksonville, Florida, United States

Chicago, Illinois, United States

Kansas City, Kansas, United States

Baton Rouge, Louisiana, United States

Portland, Maine, United States

Boston, Massachusetts, United States

Ann Arbor, Michigan, United States

Tao Yuan County, , Taiwan

Saint Louis, Missouri, United States

Detroit, Michigan, United States

Morristown, New Jersey, United States

New Brunswick, New Jersey, United States

Manhasset, New York, United States

New York, New York, United States

New York, New York, United States

Rochester, New York, United States

Las Vegas, Nevada, United States

Dublin, Ohio, United States

Philadelphia, Pennsylvania, United States

Salt Lake City, Utah, United States

Charlottesville, Virginia, United States

Tacoma, Washington, United States

Buenos Aires, , Argentina

Westmead, New South Wales, Australia

Brisbane, Queensland, Australia

Antwerp, , Belgium

Antwerp, , Belgium

Brussels, , Belgium

Liège, , Belgium

Cuiabá, Mato Grosso, Brazil

Florianopolis, Santa Catarina, Brazil

São Paulo, , Brazil

Toronto, Ontario, Canada

Santiago, , Chile

Shanghai, , China

Turku, , Finland

Bordeaux, , France

Gießen, , Germany

Kowloon, , Hong Kong

Firenze, , Italy

Yangsan, Gyeongsangnam Do, Korea, Republic Of

Busan, , Korea, Republic Of

Jeju Si, , Korea, Republic Of

Bergen, , Norway

A Coruña, , Spain

Barcelona, , Spain

Tarragona, , Spain

Göteborg, , Sweden

Tainan City, , Taiwan

Tainan City, , Taiwan

Taipei City, , Taiwan

London, , United Kingdom

London, , United Kingdom

Salford, , United Kingdom

Marseille, , France

Charlotte, North Carolina, United States

Barakaldo, , Spain

Birmingham, Alabama, United States

Jacksonville, Florida, United States

Irvine, California, United States

Chicago, Illinois, United States

Recife, Pernambuco, Brazil

Kobe, , Japan

Niigata, , Japan

Tampa, Florida, United States

Las Vegas, Nevada, United States

Sherbrooke, Quebec, Canada

Abeno Ku, Osaka, Japan

Bassano Del Grappa (Vi), , Italy

Firenze, , Italy

Dubai, , United Arab Emirates

Kaohsiung Hsien,, , Taiwan

Los Angeles, California, United States

Taichung City, , Taiwan

Orange, California, United States

Kowloon, , Hong Kong

Roma, , Italy

Setagaya, Tokyo, Japan

Putz City, Chia Yi, , Taiwan

Philadelphia, Pennsylvania, United States

Bruxelles, , Belgium

Aurora, Colorado, United States

Saint Louis, Missouri, United States

New Orleans, Louisiana, United States

Fort Worth, Texas, United States

Antwerpen, , Belgium

Niigata Shi, Niigata, Japan

La Coruña, , Spain

Tarragona, , Spain

Los Angeles, California, United States

Ann Arbor, Michigan, United States

New Brunswick, New Jersey, United States

Philadelphia, Pennsylvania, United States

Nashville, Tennessee, United States

Jette, , Belgium

Leuven, , Belgium

Uberlândia, Minas Gerais, Brazil

Bron Cedex, , France

Coral Springs, Florida, United States

Decatur, Georgia, United States

Daejeon, , Korea, Republic Of

Seoul, , Korea, Republic Of

Putz City, Chia Yi, , Taiwan

Coral Springs, Florida, United States

Washington, District Of Columbia, United States

Firenze, , Italy

Milano, , Italy

Chiba, , Japan

Washington, District Of Columbia, United States

Tampa, Florida, United States

Berlin, , Germany

Kolkata, , India

Cleveland, Ohio, United States

Bangkok, , Thailand

Herston, Queensland, Australia

Porto, , Portugal

Seattle, Washington, United States

Kuala Lumpur, , Malaysia

Phoenix, Arizona, United States

Providence, Rhode Island, United States

Beijing, , China

Indianapolis, Indiana, United States

Marseille, , France

Manchester, , United Kingdom

Minneapolis, Minnesota, United States

Rimini, , Italy

Udine, , Italy

Providence, Rhode Island, United States

Ahmedabad, , India

Vellore, , India

Niigata Shi, Niigata, Japan

Tainan, , Taiwan

Birmingham, Alabama, United States

Jacksonville, Florida, United States

Baton Rouge, Louisiana, United States

Boston, Massachusetts, United States

Springfield, Massachusetts, United States

San Bernardino, California, United States

Minneapolis, Minnesota, United States

New York, New York, United States

Charlotte, North Carolina, United States

Danville, Pennsylvania, United States

Hershey, Pennsylvania, United States

Pittsburgh, Pennsylvania, United States

Dallas, Texas, United States

Catamarca, , Argentina

La Rioja, , Argentina

Parkville, Victoria, Australia

Bruxelles, , Belgium

Cuiabá, Mato Grosso, Brazil

Vancouver, British Columbia, Canada

Vancouver, British Columbia, Canada

London, Ontario, Canada

Antofagasta, , Chile

Morristown, New Jersey, United States

Bogotá, , Colombia

Rijena, , Croatia

Tartu, , Estonia

Turku, , Finland

Berlin, , Germany

Budapest, , Hungary

Secunderabad, , India

Monza (Mb), , Italy

Vittoria (Rg), , Italy

Seoul, , Korea, Republic Of

Seoul, , Korea, Republic Of

Vilnius, , Lithuania

Manila, , Philippines

Warszawa, , Poland

Lisboa, , Portugal

Moscow, , Russian Federation

Novi Sad, , Serbia

Barcelona, , Spain

Barcelona, , Spain

Coquimbo, , Chile

New Taipei City, , Taiwan

Taipei, , Taiwan

Bangkok, , Thailand

Bangkok, , Thailand

London, , United Kingdom

Chiayi, , Taiwan

Hanoi, , Vietnam

Palo Alto, California, United States

Saint Louis, Missouri, United States

Hualien, , Taiwan

Ciudad Autónoma De Buenos Aires, Buenos Aires, Argentina

Jinan, , China

Portland, Oregon, United States

Modena, , Italy

Nanjing, , China

Morristown, New Jersey, United States

Vilnius, , Lithuania

Barakaldo, , Spain

Antwerpen, , Belgium

Nangoku Shi, Kochi, Japan

Callao, , Peru

San Diego, California, United States

Washington, District Of Columbia, United States

Greenville, South Carolina, United States

Vellore, , India

San Diego, California, United States

Little Rock, Arkansas, United States

Little Rock, Arkansas, United States

New Haven, Connecticut, United States

Paterson, New Jersey, United States

Antwerpen, , Belgium

Manhasset, New York, United States

Campinas, São Paulo, Brazil

Halifax, Nova Scotia, Canada

Montreal, Quebec, Canada

Copenhagen, , Denmark

Ahmedabad, , India

Udine, , Italy

Setagaya, Tokyo, Japan

Chiba, , Japan

Callao, , Peru

Bucuresti, , Romania

Barcelona, , Spain

Tainan, , Taiwan

Belfast, , United Kingdom

Birmingham, , United Kingdom

Sherbrooke, Quebec, Canada

Kolkata, , India

Louisville, Kentucky, United States

New York, New York, United States

Durham, North Carolina, United States

Brussels, , Belgium

Buenos Aires, , Argentina

Moncton, New Brunswick, Canada

Tainan, , Taiwan

Bucuresti, , Romania

Edmonton, Alberta, Canada

St Priest En Jarez, , France

Jakarta, , Indonesia

Cluj Napoca, , Romania

Brasília, Distrito Federal, Brazil

Jacksonville, Florida, United States

Boston, Massachusetts, United States

Seattle, Washington, United States

Cleveland, Ohio, United States

Seattle, Washington, United States

København ø, , Denmark

Little Rock, Arkansas, United States

Jacksonville, Florida, United States

Iowa City, Iowa, United States

Louisville, Kentucky, United States

Gainesville, Florida, United States

Ann Arbor, Michigan, United States

Camden, New Jersey, United States

Manhasset, New York, United States

New York, New York, United States

Dallas, Texas, United States

Parkville, Victoria, Australia

Cuiabá, Mato Grosso, Brazil

Edmonton, Alberta, Canada

Halifax, Nova Scotia, Canada

Toronto, Ontario, Canada

Beijing, , China

Rijena, , Croatia

Bordeaux, , France

Limoges Cedex, , France

Strasbourg, , France

Gießen, , Germany

Montreal, Quebec, Canada

Würzburg, , Germany

Genova, , Italy

Milano, , Italy

Monza (Mb), , Italy

Vittoria (Rg), , Italy

Seoul, , Korea, Republic Of

Amsterdam, , Netherlands

Amsterdam, , Netherlands

Manila, , Philippines

Yangsan, , Korea, Republic Of

Porto, , Portugal

Barcelona, , Spain

Barcelona, , Spain

Tarragona, , Spain

Stockholm, , Sweden

Chiayi, , Taiwan

Bucuresti, , Romania

Detroit, Michigan, United States

Barcelona, , Spain

Sacramento, California, United States

Iquique, , Chile

Vilnius, , Lithuania

La Coruña, , Spain

Bangkok, , Thailand

Oakland, Florida, United States

Tacoma, Washington, United States

Buenos Aires, , Argentina

Tampa, Florida, United States

La Coruña, , Spain

Irvine, California, United States

Portland, Maine, United States

Baltimore, Maryland, United States

Grand Rapids, Michigan, United States

Tacoma, Washington, United States

Adelaide, South Australia, Australia

Recife, Pernambuco, Brazil

São Paulo, , Brazil

Zagreb, , Croatia

London, , United Kingdom

Manchester, , United Kingdom

Hangzhou, , China

Kaohsiung City, , Taiwan

Oakland, California, United States

Irvine, California, United States

New York, New York, United States

St. John's, Newfoundland And Labrador, Canada

Kobe Shi, Hyogo, , Japan

Little Rock, Arkansas, United States

San Bernardino, California, United States

Brasília, , Brazil

Campinas, , Brazil

Cuiabá, , Brazil

Curitiba, , Brazil

Ourinhos, , Brazil

Uberlândia, , Brazil

København, , Denmark

La Coruna, , Spain

La Coruna, , Spain

Kansas City, Kansas, United States

Grand Rapids, Michigan, United States

Omaha, Nebraska, United States

Las Vegas, Nevada, United States

Cleveland, Ohio, United States

Philadelphia, Pennsylvania, United States

Salt Lake City, Utah, United States

Norfolk, Virginia, United States

La Rioja, , Argentina

Santa Fe, , Argentina

Westmead, New South Wales, Australia

Curitiba, Paraná, Brazil

Herston, Queensland, Australia

Recife, Pernambuco, Brazil

Florianopolis, Santa Catarina, Brazil

Calgary, Alberta, Canada

São Paulo, , Brazil

Moncton, New Brunswick, Canada

Toronto, Ontario, Canada

Antofagasta, , Chile

Coquimbo, , Chile

Copenhagen, , Denmark

Kobe Shi, Hyogo, , Japan

Yangsan Si, Gyeongsangnam Do, Korea, Republic Of

Busan, , Korea, Republic Of

Seoul, , Korea, Republic Of

Seoul, , Korea, Republic Of

Kuwait, , Kuwait

Vilnius, , Lithuania

Bergen, , Norway

Lisboa, , Portugal

Novi Sad, , Serbia

Vancouver, British Columbia, Canada

Göteborg, , Sweden

Kaohsiung Hsien,, , Taiwan

Vallenar, , Chile

Taichung City, , Taiwan

Singapore, , Singapore

Bangkok, , Thailand

Taipei, , Taiwan

Taipei, , Taiwan

Manchester, , United Kingdom

London, , United Kingdom

Hanoi, , Vietnam

Sofia, , Bulgaria

St. John's, Newfoundland And Labrador, Canada

Los Angeles, California, United States

Tapejara, Rio Grande Do Sul, Brazil

London, , United Kingdom

Daejeon, , Korea, Republic Of

Salford, , United Kingdom

Miami, Florida, United States

Decatur, Georgia, United States

Boston, Massachusetts, United States

Barcelona, , Spain

Garches, , France

Orange, California, United States

Taipei, , Taiwan

Udine, , Italy

Firenze, , Italy

Torino, , Italy

Belfast, , United Kingdom

Palo Alto, California, United States

Cleveland, Ohio, United States

Providence, Rhode Island, United States

Nizhny Novgorod, , Russian Federation

New Taipei City, , Taiwan

Seoul, , Korea, Republic Of

Baton Rouge, Louisiana, United States

Catamarca, , Argentina

Liège, , Belgium

Valhalla, New York, United States

Charlotte, North Carolina, United States

London, , United Kingdom

Columbus, Ohio, United States

Fort Worth, Texas, United States

Westmead, New South Wales, Australia

Uberlândia, Minas Gerais, Brazil

Winnipeg, Manitoba, Canada

Bucuresti, , Romania

Barcelona, , Spain

Palo Alto, California, United States

Omaha, Nebraska, United States

Budapest, , Hungary

Sacramento, California, United States

Grand Rapids, Michigan, United States

Garches, , France

Seoul, , Korea, Republic Of

Hualien, , Taiwan

Cincinnati, Ohio, United States

Feira De Santana, Bahia, Brazil

London, , United Kingdom

Dallas, Texas, United States

Paterson, New Jersey, United States

Taipei, , Taiwan

Vallenar, , Chile

Little Rock, Arkansas, United States

Los Angeles, California, United States

Los Angeles, California, United States

Sacramento, California, United States

New Haven, Connecticut, United States

Gainesville, Florida, United States

Miami, Florida, United States

Aurora, Illinois, United States

Iowa City, Iowa, United States

Louisville, Kentucky, United States

Baltimore, Maryland, United States

Bratislava, , Slovakia

Boston, Massachusetts, United States

Grand Rapids, Michigan, United States

Minneapolis, Minnesota, United States

Columibia, Missouri, United States

Billings, Montana, United States

Helena, Montana, United States

Syracuse, New York, United States

Cincinnati, Ohio, United States

Columbus, Ohio, United States

Portland, Oregon, United States

Portland, Oregon, United States

Danville, Pennsylvania, United States

Pittsburgh, Pennsylvania, United States

Greenville, South Carolina, United States

Nashville, Tennessee, United States

Fairfax, Virginia, United States

Seattle, Washington, United States

Milwaukee, Wisconsin, United States

Curitiba, Paraná, Brazil

Tapejara, Rio Grande Do Sul, Brazil

Ourinhos, São Paulo, Brazil

Moncton, New Brunswick, Canada

Kingston, Ontario, Canada

Jinan, , China

Limoges, , France

Strasbourg, , France

Tokyo, , Japan

Seoul, Gyeonggi Do, Korea, Republic Of

Amsterdam, , Netherlands

Amsterdam, , Netherlands

A Coruña, , Spain

Kaohsiung City, , Taiwan

Taipei City, , Taiwan

Taoyuan City, , Taiwan

Dublin, Ohio, United States

Danville, Pennsylvania, United States

Kaohsiung City, , Taiwan

Khon Kaen, , Thailand

Cambridge, Cambridgeshire, United Kingdom

Little Rock, Arkansas, United States

Münster, , Germany

Springfield, Massachusetts, United States

Modena, , Italy

Chicago, Illinois, United States

Napoli, , Italy

Los Angeles, California, United States

Birmingham, Alabama, United States

Oakland, California, United States

Sacramento, California, United States

San Francisco, California, United States

Phoenix, Arizona, United States

Tucson, Arizona, United States

Decatur, Georgia, United States

Chicago, Illinois, United States

Detroit, Michigan, United States

Denver, Colorado, United States

Helena, Montana, United States

Hackensack, New Jersey, United States

Columbus, Ohio, United States

Philadelphia, Pennsylvania, United States

Salt Lake City, Utah, United States

Caba, Buenos Aires, Argentina

Westmead, New South Wales, Australia

Florianopolis, Santa Catarina, Brazil

Limoges Cedex, , France

Marseille, , France

Saint Priest En Jarez, , France

Grand Rapids, Michigan, United States

Stockholm, , Sweden

Milano, , Italy

Seoul, Seoul Teukbyeolsi, Korea, Republic Of

Seoul, Seoul Teukbyeolsi, Korea, Republic Of

Manchester, , United Kingdom

Tucson, Arizona, United States

Grand Rapids, Michigan, United States

Philadelphia, Pennsylvania, United States

Fort Worth, Texas, United States

Seoul, , Korea, Republic Of

Gainesville, Florida, United States

Indianapolis, Indiana, United States

Feira De Santana, Bahia, Brazil

New York, New York, United States

Kaohsiung, , Taiwan

Chicago, Illinois, United States

Charlottesville, Virginia, United States

Hershey, Pennsylvania, United States

Al Mubarraz, , Saudi Arabia

Denver, Colorado, United States

Brasília, Distrito Federal, Brazil

Ourinhos, São Paulo, Brazil

San Francisco, California, United States

Helena, Montana, United States

Portland, Oregon, United States

Portland, Oregon, United States

Tapejara, Rio Grande Do Sul, Brazil

Suwon Si, , Korea, Republic Of

Warszawa, , Poland

Vancouver, British Columbia, Canada

Bratislava, , Slovakia

New York, New York, United States

Minneapolis, Minnesota, United States

Rochester, New York, United States

Oakland, California, United States

Orange, California, United States

Boston, Massachusetts, United States

Camden, New Jersey, United States

Cleveland, Ohio, United States

São Paulo, , Brazil

Columbus, Ohio, United States

Sofia, , Bulgaria

Calgary, Alberta, Canada

Létavértes, , Hungary

Sopron, , Hungary

Milano, , Italy

Kobe, Hyogo, Japan

Seoul, , Korea, Republic Of

Suwon Si, , Korea, Republic Of

Kuwait, , Kuwait

Saint Peterburg, , Russian Federation

Kaohsiung, , Taiwan

Taichung, , Taiwan

Taichung, , Taiwan

Campinas, São Paulo, Brazil

Birmingham, England, United Kingdom

Salford, Manchester, United Kingdom

New York, New York, United States

Cambridge, Cambridgeshire, United Kingdom

Birmingham, , United Kingdom

Valhalla, New York, United States

Cleveland, Ohio, United States

Billings, Montana, United States

Toronto, Ontario, Canada

Jeonnam, , Korea, Republic Of

Seoul, , Korea, Republic Of

Coral Springs, Florida, United States

Miami, Florida, United States

Valhalla, New York, United States

Fairfax, Virginia, United States

New Orleans, Louisiana, United States

Los Angeles, California, United States

Norfolk, Virginia, United States

Abeno Ku, Osaka, Japan

Greenville, South Carolina, United States

Hackensack, New Jersey, United States

Cleveland, Ohio, United States

Hershey, Pennsylvania, United States

Uberlândia, Minas Gerais, Brazil

Yangsan, Gyeongsangnam Do, Korea, Republic Of

Barakaldo, Pais Vasco, Spain

Khon Kaen, , Thailand

Münster, , Germany

San Diego, California, United States

Springfield, Massachusetts, United States

Birmingham, Alabama, United States

Taipei, , Taiwan

Columibia, Missouri, United States

Billings, Montana, United States

Columbus, Ohio, United States

Pittsburgh, Pennsylvania, United States

Seattle, Washington, United States

Tacoma, Washington, United States

Ciudad Autónoma De Buenos Aires, Buenos Aires, Argentina

Adelaide, South Australia, Australia

Antwerpen, , Belgium

Phoenix, Arizona, United States

Tucson, Arizona, United States

Baltimore, Maryland, United States

Boston, Massachusetts, United States

Jalan Pahang, , Malaysia

Cluj Napoca, , Romania

Moscow, , Russian Federation

Barcelona, , Spain

Tainan, , Taiwan

Jacksonville, Florida, United States

Irvine, California, United States

Barcelona, , Spain

Birmingham, , United Kingdom

Hackensack, New Jersey, United States

Leuven, , Belgium

Seraing, , Belgium

Campinas, São Paulo, Brazil

Saint Priest En Jarez, , France

Jakarta, , Indonesia

New Brunswick, New Jersey, United States

Fairfax, Virginia, United States

Perth, Western Australia, Australia

Brussels, , Belgium

Los Angeles, California, United States

Minneapolis, Minnesota, United States

Rimini, , Italy

Torino, , Italy

Jeju Si, , Korea, Republic Of

Los Angeles, California, United States

Lille, , France

Vigo, , Spain

Pécs, , Hungary

Milwaukee, Wisconsin, United States

Brussel, , Belgium

København ø, , Denmark

Tartu, , Estonia

Birmingham, Alabama, United States

Jette, , Belgium

Bron Cedex, , France

Nanjing, , China

Bangkok, , Thailand

Syracuse, New York, United States

Durham, North Carolina, United States

Oakland, Virginia, United States

Shanghai, , China

Bogotá, , Colombia

Zagreb, , Croatia

Praha 2, , Czechia

Jeonnam, , Korea, Republic Of

Seoul, , Korea, Republic Of

Seoul, , Korea, Republic Of

Saint Peterburg, , Russian Federation

Boston, Massachusetts, United States

Brasília, Distrito Federal, Brazil

Strasbourg, , France

Santa Fe, , Argentina

Perth, Western Australia, Australia

Barcelona, , Spain

Buenos Aires, , Argentina

Cincinnati, Ohio, United States

Nashville, Tennessee, United States

Charlottesville, Virginia, United States

Minneapolis, Minnesota, United States

Norfolk, Virginia, United States

Curitiba, , Brazil

London, Ontario, Canada

Campinas, , Brazil

Ourinhos, , Brazil

Roma, , Italy

Vilnius, , Lithuania

Al Mubarraz, , Saudi Arabia

Kansas City, Kansas, United States

Praha 2, , Czechia

Milwaukee, Wisconsin, United States

Ourinhos, São Paulo, Brazil

Napoli, , Italy

Tao Yuan County, , Taiwan

Sacramento, California, United States

Iowa City, Iowa, United States

Hangzhou, , China

Jinan, , China

Nangoku Shi, Kochi, Japan

Cambridge, Cambridgeshire, United Kingdom

Omaha, Nebraska, United States

Paterson, New Jersey, United States

Brussels, , Belgium

Feira De Santana, Bahia, Brazil

Vigo, , Spain

Minneapolis, Minnesota, United States

Durham, North Carolina, United States

Seraing, , Belgium

Yangsan Si, Gyeongsangnam Do, Korea, Republic Of

Singapore, , Singapore

Sofia, , Bulgaria

Winnipeg, Manitoba, Canada

Iquique, , Chile

Lille, , France

Bassano Del Grappa (Vi), , Italy

Genova, , Italy

Jalan Pahang, , Malaysia

Patients applied

0 patients applied

Trial Officials

Study Director

Study Director

Genzyme, a Sanofi Company

Timeline

First submit

Trial launched

Trial updated

Estimated completion

Not reported

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