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Search / Trial NCT00196742

Fabry Disease Registry & Pregnancy Sub-registry

Launched by GENZYME, A SANOFI COMPANY · Sep 13, 2005

Trial Information

Current as of July 23, 2025

Recruiting

Keywords

Alpha Galactosidase A A Gal (Alpha Galactosidase) Fabry Gl3 (Globotriaosylceramide) Anderson Fabry Disease Angiokeratomas Gla Deficiency (Gene Deficiency) Errors In Metabolism

ClinConnect Summary

The Fabry Disease Registry and Pregnancy Sub-registry is an ongoing study that gathers information about people with Fabry disease, a genetic condition that affects how the body processes certain fats. This program is observational, meaning that it doesn’t involve any experimental treatments. Instead, patients receive regular medical care from their doctors, and their health outcomes are monitored over time. The main goals of the registry are to better understand how Fabry disease varies in different individuals, track its progression, and help improve patient care. For pregnant women with Fabry disease, the Pregnancy Sub-registry specifically looks at pregnancy outcomes, collecting information about their health and the health of their babies.

To participate in the Fabry Registry, individuals need to have a confirmed diagnosis of Fabry disease, which can be determined through specific enzyme tests or genetic testing. For the Pregnancy Sub-registry, women must be enrolled in the main registry and either currently pregnant or have been pregnant in the past. Participants can expect to provide information about their medical history and pregnancy, and if they agree, their baby's growth will be tracked for up to three years after birth. Overall, this research aims to improve understanding and care for those living with Fabry disease.

Gender

ALL

Eligibility criteria

  • Inclusion Criteria
  • Fabry Registry: All patients with a confirmed diagnosis of Fabry disease who have signed the informed consent and patient authorization form(s) are eligible for inclusion. Confirmed diagnosis is defined as a documented deficiency in plasma or leukocyte αGAL (alpha-galactosidase) enzyme activity and/or mutation(s) in the gene coding for αGAL.
  • * Fabry Pregnancy Sub-registry:
  • * Eligible women must:
  • be enrolled in the Fabry Registry.
  • be pregnant, or have been pregnant with appropriate medical documentation available.
  • provide a signed informed consent and authorization form(s) to participate in the Sub-Registry prior to any Sub-Registry-related data collection being performed.
  • Exclusion Criteria Fabry Registry: There are no exclusion criteria. Fabry Pregnancy Sub-registry: There are no exclusion criteria.

About Genzyme, A Sanofi Company

Genzyme, a Sanofi company, is a global leader in biotechnology dedicated to developing innovative therapies for rare and complex diseases. With a strong focus on patient-centric solutions, Genzyme leverages advanced research and development capabilities to address unmet medical needs across various therapeutic areas, including neurology, oncology, and genetic disorders. Committed to scientific excellence and collaboration, Genzyme aims to improve patient outcomes through the discovery and commercialization of high-quality biopharmaceuticals, while upholding the highest standards of safety and efficacy in clinical trials.

Locations

Phoenix, Arizona, United States

Little Rock, Arkansas, United States

Los Angeles, California, United States

Los Angeles, California, United States

Orange, California, United States

Palo Alto, California, United States

Sacramento, California, United States

San Bernardino, California, United States

San Diego, California, United States

San Francisco, California, United States

New Haven, Connecticut, United States

Washington, District Of Columbia, United States

Gainesville, Florida, United States

Jacksonville, Florida, United States

Miami, Florida, United States

Decatur, Georgia, United States

Chicago, Illinois, United States

Indianapolis, Indiana, United States

Iowa City, Iowa, United States

Louisville, Kentucky, United States

Baltimore, Maryland, United States

Boston, Massachusetts, United States

Springfield, Massachusetts, United States

Ann Arbor, Michigan, United States

Detroit, Michigan, United States

Minneapolis, Minnesota, United States

Minneapolis, Minnesota, United States

Saint Louis, Missouri, United States

Omaha, Nebraska, United States

Las Vegas, Nevada, United States

Hackensack, New Jersey, United States

Morristown, New Jersey, United States

New Brunswick, New Jersey, United States

Paterson, New Jersey, United States

Manhasset, New York, United States

New York, New York, United States

New York, New York, United States

Rochester, New York, United States

Syracuse, New York, United States

Cleveland, Ohio, United States

Columbus, Ohio, United States

Dublin, Ohio, United States

Philadelphia, Pennsylvania, United States

Philadelphia, Pennsylvania, United States

Pittsburgh, Pennsylvania, United States

Providence, Rhode Island, United States

Greenville, South Carolina, United States

Dallas, Texas, United States

Charlottesville, Virginia, United States

Norfolk, Virginia, United States

Seattle, Washington, United States

Seattle, Washington, United States

Tacoma, Washington, United States

Milwaukee, Wisconsin, United States

Ciudad Autónoma De Buenos Aires, Buenos Aires, Argentina

Buenos Aires, , Argentina

Westmead, New South Wales, Australia

Bruxelles, , Belgium

Leuven, , Belgium

Calgary, Alberta, Canada

Edmonton, Alberta, Canada

Vancouver, British Columbia, Canada

Winnipeg, Manitoba, Canada

Moncton, New Brunswick, Canada

London, Ontario, Canada

Toronto, Ontario, Canada

Sherbrooke, Quebec, Canada

Bogotá, , Colombia

København ø, , Denmark

Pécs, , Hungary

Ahmedabad, , India

Kolkata, , India

Secunderabad, , India

Vellore, , India

Jakarta, , Indonesia

Udine, , Italy

Busan, , Korea, Republic Of

Daejeon, , Korea, Republic Of

Jeonnam, , Korea, Republic Of

Seoul, , Korea, Republic Of

Seoul, , Korea, Republic Of

Seoul, , Korea, Republic Of

Seoul, , Korea, Republic Of

Seoul, , Korea, Republic Of

Seoul, , Korea, Republic Of

Yangsan, , Korea, Republic Of

Kuwait, , Kuwait

Jalan Pahang, , Malaysia

Kuala Lumpur, , Malaysia

Amsterdam, , Netherlands

Manila, , Philippines

Warszawa, , Poland

Singapore, , Singapore

Bratislava, , Slovakia

Chiayi, , Taiwan

Hualien, , Taiwan

Kaohsiung Hsien,, , Taiwan

Kaohsiung, , Taiwan

New Taipei City, , Taiwan

Putz City, Chia Yi, , Taiwan

Taichung City, , Taiwan

Tainan, , Taiwan

Tainan, , Taiwan

Taipei, , Taiwan

Taipei, , Taiwan

Tao Yuan County, , Taiwan

Bangkok, , Thailand

Bangkok, , Thailand

Bangkok, , Thailand

Khon Kaen, , Thailand

Dubai, , United Arab Emirates

Birmingham, , United Kingdom

London, , United Kingdom

London, , United Kingdom

London, , United Kingdom

Manchester, , United Kingdom

Salford, , United Kingdom

Hanoi, , Vietnam

Birmingham, Alabama, United States

Birmingham, Alabama, United States

Tucson, Arizona, United States

Little Rock, Arkansas, United States

Aurora, California, United States

Irvine, California, United States

Los Angeles, California, United States

Sacramento, California, United States

Coral Springs, Florida, United States

Oakland, Florida, United States

Tampa, Florida, United States

Chicago, Illinois, United States

Kansas City, Kansas, United States

Baton Rouge, Louisiana, United States

New Orleans, Louisiana, United States

Portland, Maine, United States

Boston, Massachusetts, United States

Boston, Massachusetts, United States

Grand Rapids, Michigan, United States

Grand Rapids, Michigan, United States

Minneapolis, Minnesota, United States

Columibia, Missouri, United States

Billings, Montana, United States

Helena, Montana, United States

Camden, New Jersey, United States

New York, New York, United States

Valhalla, New York, United States

Charlotte, North Carolina, United States

Durham, North Carolina, United States

Cincinnati, Ohio, United States

Cleveland, Ohio, United States

Columbus, Ohio, United States

Portland, Oregon, United States

Portland, Oregon, United States

Danville, Pennsylvania, United States

Hershey, Pennsylvania, United States

Nashville, Tennessee, United States

Fort Worth, Texas, United States

Salt Lake City, Utah, United States

Fairfax, Virginia, United States

Caba, Buenos Aires, Argentina

Catamarca, , Argentina

La Rioja, , Argentina

Santa Fe, , Argentina

Westmead, New South Wales, Australia

Herston, Queensland, Australia

Adelaide, South Australia, Australia

Parkville, Victoria, Australia

Perth, Western Australia, Australia

Antwerpen, , Belgium

Antwerpen, , Belgium

Brussels, , Belgium

Brussel, , Belgium

Liège, , Belgium

Seraing, , Belgium

Feira De Santana, Bahia, Brazil

Brasília, Distrito Federal, Brazil

Cuiabá, Mato Grosso, Brazil

Uberlândia, Minas Gerais, Brazil

Curitiba, Paraná, Brazil

Recife, Pernambuco, Brazil

Tapejara, Rio Grande Do Sul, Brazil

Florianopolis, Santa Catarina, Brazil

Campinas, São Paulo, Brazil

Ourinhos, São Paulo, Brazil

São Paulo, , Brazil

Sofia, , Bulgaria

Sofia, , Bulgaria

Vancouver, British Columbia, Canada

St. John's, Newfoundland And Labrador, Canada

Halifax, Nova Scotia, Canada

Halifax, Nova Scotia, Canada

Kingston, Ontario, Canada

Toronto, Ontario, Canada

Montreal, Quebec, Canada

Antofagasta, , Chile

Coquimbo, , Chile

Iquique, , Chile

Santiago, , Chile

Vallenar, , Chile

Beijing, , China

Shanghai, , China

Rijena, , Croatia

Zagreb, , Croatia

Praha 2, , Czechia

Copenhagen, , Denmark

Tartu, , Estonia

Turku, , Finland

Bordeaux, , France

Bron Cedex, , France

Garches, , France

Lille, , France

Limoges Cedex, , France

Marseille, , France

Saint Priest En Jarez, , France

Strasbourg, , France

Berlin, , Germany

Gießen, , Germany

Münster, , Germany

Würzburg, , Germany

Budapest, , Hungary

Létavértes, , Hungary

Pécs, , Hungary

Sopron, , Hungary

Bassano Del Grappa (Vi), , Italy

Firenze, , Italy

Firenze, , Italy

Genova, , Italy

Milano, , Italy

Milano, , Italy

Modena, , Italy

Monza (Mb), , Italy

Napoli, , Italy

Rimini, , Italy

Roma, , Italy

Torino, , Italy

Vittoria (Rg), , Italy

Nangoku Shi, Kochi, Japan

Abeno Ku, Osaka, Japan

Setagaya, Tokyo, Japan

Chiba, , Japan

Kobe Shi, Hyogo, , Japan

Niigata, , Japan

Busan, , Korea, Republic Of

Jeju Si, , Korea, Republic Of

Seoul, , Korea, Republic Of

Suwon Si, , Korea, Republic Of

Yangsan, , Korea, Republic Of

Vilnius, , Lithuania

Vilnius, , Lithuania

Amsterdam, , Netherlands

Bergen, , Norway

Callao, , Peru

Lisboa, , Portugal

Porto, , Portugal

Bucuresti, , Romania

Bucuresti, , Romania

Cluj Napoca, , Romania

Moscow, , Russian Federation

Nizhny Novgorod, , Russian Federation

Saint Peterburg, , Russian Federation

Al Mubarraz, , Saudi Arabia

Novi Sad, , Serbia

Slovenj Gradec, , Slovenia

Barakaldo, , Spain

Barcelona, , Spain

Barcelona, , Spain

Barcelona, , Spain

Barcelona, , Spain

Barcelona, , Spain

Barcelona, , Spain

La Coruña, , Spain

La Coruña, , Spain

Tarragona, , Spain

Vigo, , Spain

Göteborg, , Sweden

Stockholm, , Sweden

Kaohsiung City, , Taiwan

Taichung, , Taiwan

Taipei, , Taiwan

Dubai, , United Arab Emirates

Cambridge, Cambridgeshire, United Kingdom

Belfast, , United Kingdom

Létavértes, , Hungary

Hangzhou, , China

Phoenix, Arizona, United States

Little Rock, Arkansas, United States

Los Angeles, California, United States

Los Angeles, California, United States

Orange, California, United States

Palo Alto, California, United States

Sacramento, California, United States

San Bernardino, California, United States

San Diego, California, United States

San Francisco, California, United States

Aurora, Colorado, United States

New Haven, Connecticut, United States

Washington, District Of Columbia, United States

Gainesville, Florida, United States

Jacksonville, Florida, United States

Jacksonville, Florida, United States

Miami, Florida, United States

Oakland, Florida, United States

Decatur, Georgia, United States

Chicago, Illinois, United States

Indianapolis, Indiana, United States

Iowa City, Iowa, United States

Louisville, Kentucky, United States

Baltimore, Maryland, United States

Boston, Massachusetts, United States

Springfield, Massachusetts, United States

Ann Arbor, Michigan, United States

Detroit, Michigan, United States

Minneapolis, Minnesota, United States

Minneapolis, Minnesota, United States

Saint Louis, Missouri, United States

Omaha, Nebraska, United States

Las Vegas, Nevada, United States

Hackensack, New Jersey, United States

Morristown, New Jersey, United States

New Brunswick, New Jersey, United States

Paterson, New Jersey, United States

Manhasset, New York, United States

New York, New York, United States

New York, New York, United States

Rochester, New York, United States

Syracuse, New York, United States

Cleveland, Ohio, United States

Columbus, Ohio, United States

Dublin, Ohio, United States

Philadelphia, Pennsylvania, United States

Philadelphia, Pennsylvania, United States

Pittsburgh, Pennsylvania, United States

Providence, Rhode Island, United States

Greenville, South Carolina, United States

Dallas, Texas, United States

Charlottesville, Virginia, United States

Norfolk, Virginia, United States

Seattle, Washington, United States

Seattle, Washington, United States

Tacoma, Washington, United States

Milwaukee, Wisconsin, United States

Buenos Aires, , Argentina

Calgary, Alberta, Canada

København, , Denmark

Birmingham, Alabama, United States

Birmingham, Alabama, United States

Tucson, Arizona, United States

Little Rock, Arkansas, United States

Irvine, California, United States

Los Angeles, California, United States

Sacramento, California, United States

Coral Springs, Florida, United States

Tampa, Florida, United States

Chicago, Illinois, United States

Kansas City, Kansas, United States

Baton Rouge, Louisiana, United States

New Orleans, Louisiana, United States

Portland, Maine, United States

Boston, Massachusetts, United States

Boston, Massachusetts, United States

Grand Rapids, Michigan, United States

Grand Rapids, Michigan, United States

Minneapolis, Minnesota, United States

Columibia, Missouri, United States

Billings, Montana, United States

Helena, Montana, United States

Camden, New Jersey, United States

New York, New York, United States

Valhalla, New York, United States

Charlotte, North Carolina, United States

Durham, North Carolina, United States

Cincinnati, Ohio, United States

Cleveland, Ohio, United States

Columbus, Ohio, United States

Portland, Oregon, United States

Portland, Oregon, United States

Danville, Pennsylvania, United States

Hershey, Pennsylvania, United States

Nashville, Tennessee, United States

Fort Worth, Texas, United States

Salt Lake City, Utah, United States

Fairfax, Virginia, United States

Brasília, , Brazil

Campinas, , Brazil

Cuiabá, , Brazil

Curitiba, , Brazil

Ourinhos, , Brazil

Uberlândia, , Brazil

Sopron, , Hungary

La Coruna, , Spain

La Coruna, , Spain

Irvine, California, United States

Oakland, California, United States

Tacoma, Washington, United States

Yangsan Si, Gyeongsangnam Do, Korea, Republic Of

Nanjing, , China

Niigata Shi, Niigata, Japan

Oakland, Virginia, United States

New York, New York, United States

Jette, , Belgium

Jinan, , China

Irvine, California, United States

Denver, Colorado, United States

Kowloon, , Hong Kong

L'hospitalet De Llobregat, Cataluña, Spain

Hangzhou, , China

Pécs, , Hungary

Udine, , Italy

Zagreb, , Croatia

Little Rock, Arkansas, United States

Little Rock, Arkansas, United States

Los Angeles, California, United States

Oakland, California, United States

San Bernardino, California, United States

San Diego, California, United States

New Haven, Connecticut, United States

Washington, District Of Columbia, United States

Jacksonville, Florida, United States

Jacksonville, Florida, United States

Tampa, Florida, United States

Decatur, Georgia, United States

Chicago, Illinois, United States

Chicago, Illinois, United States

Indianapolis, Indiana, United States

Louisville, Kentucky, United States

Portland, Maine, United States

Baltimore, Maryland, United States

Boston, Massachusetts, United States

Boston, Massachusetts, United States

Springfield, Massachusetts, United States

Ann Arbor, Michigan, United States

Grand Rapids, Michigan, United States

Grand Rapids, Michigan, United States

Minneapolis, Minnesota, United States

Minneapolis, Minnesota, United States

Columibia, Missouri, United States

Saint Louis, Missouri, United States

Omaha, Nebraska, United States

Morristown, New Jersey, United States

New Brunswick, New Jersey, United States

Paterson, New Jersey, United States

Manhasset, New York, United States

New York, New York, United States

New York, New York, United States

Rochester, New York, United States

Syracuse, New York, United States

Valhalla, New York, United States

Cleveland, Ohio, United States

Cleveland, Ohio, United States

Columbus, Ohio, United States

Dublin, Ohio, United States

Philadelphia, Pennsylvania, United States

Pittsburgh, Pennsylvania, United States

Providence, Rhode Island, United States

Greenville, South Carolina, United States

Nashville, Tennessee, United States

Dallas, Texas, United States

Fort Worth, Texas, United States

Charlottesville, Virginia, United States

Fairfax, Virginia, United States

Norfolk, Virginia, United States

Tacoma, Washington, United States

Milwaukee, Wisconsin, United States

Ciudad Autónoma De Buenos Aires, Buenos Aires, Argentina

Westmead, New South Wales, Australia

Westmead, New South Wales, Australia

Adelaide, South Australia, Australia

Antwerpen, , Belgium

Leuven, , Belgium

Sofia, , Bulgaria

Moncton, New Brunswick, Canada

København ø, , Denmark

Gießen, , Germany

Kowloon, , Hong Kong

Ahmedabad, , India

Kolkata, , India

Secunderabad, , India

Vellore, , India

Jakarta, , Indonesia

Yangsan Si, Gyeongsangnam Do, Korea, Republic Of

Daejeon, , Korea, Republic Of

Jeonnam, , Korea, Republic Of

Seoul, , Korea, Republic Of

Seoul, , Korea, Republic Of

Seoul, , Korea, Republic Of

Seoul, , Korea, Republic Of

Seoul, , Korea, Republic Of

Seoul, , Korea, Republic Of

Kuwait, , Kuwait

Jalan Pahang, , Malaysia

Manila, , Philippines

Warszawa, , Poland

Bucuresti, , Romania

Singapore, , Singapore

Bratislava, , Slovakia

Chiayi, , Taiwan

Hualien, , Taiwan

Kaohsiung Hsien,, , Taiwan

Kaohsiung, , Taiwan

New Taipei City, , Taiwan

Putz City, Chia Yi, , Taiwan

Taichung City, , Taiwan

Tainan, , Taiwan

Tainan, , Taiwan

Taipei, , Taiwan

Taipei, , Taiwan

Taipei, , Taiwan

Tao Yuan County, , Taiwan

Bangkok, , Thailand

Bangkok, , Thailand

Bangkok, , Thailand

Khon Kaen, , Thailand

Birmingham, , United Kingdom

Hanoi, , Vietnam

Gainesville, Florida, United States

Iowa City, Iowa, United States

Hackensack, New Jersey, United States

Buenos Aires, , Argentina

Bruxelles, , Belgium

Bogotá, , Colombia

Udine, , Italy

Yangsan, Gyeongsangnam Do, Korea, Republic Of

Kuala Lumpur, , Malaysia

Amsterdam, , Netherlands

London, , United Kingdom

Birmingham, Alabama, United States

Birmingham, Alabama, United States

Phoenix, Arizona, United States

Tucson, Arizona, United States

Irvine, California, United States

Los Angeles, California, United States

Los Angeles, California, United States

Orange, California, United States

Palo Alto, California, United States

Sacramento, California, United States

Sacramento, California, United States

San Francisco, California, United States

Denver, Colorado, United States

Coral Springs, Florida, United States

Miami, Florida, United States

Kansas City, Kansas, United States

Baton Rouge, Louisiana, United States

New Orleans, Louisiana, United States

Boston, Massachusetts, United States

Detroit, Michigan, United States

Minneapolis, Minnesota, United States

Billings, Montana, United States

Helena, Montana, United States

Las Vegas, Nevada, United States

New York, New York, United States

Charlotte, North Carolina, United States

Durham, North Carolina, United States

Cincinnati, Ohio, United States

Columbus, Ohio, United States

Portland, Oregon, United States

Danville, Pennsylvania, United States

Hershey, Pennsylvania, United States

Philadelphia, Pennsylvania, United States

Salt Lake City, Utah, United States

Seattle, Washington, United States

Seattle, Washington, United States

Caba, Buenos Aires, Argentina

Catamarca, , Argentina

La Rioja, , Argentina

Santa Fe, , Argentina

Herston, Queensland, Australia

Parkville, Victoria, Australia

Perth, Western Australia, Australia

Antwerpen, , Belgium

Brussels, , Belgium

Jette, , Belgium

Liège, , Belgium

Seraing, , Belgium

Feira De Santana, Bahia, Brazil

Brasília, Distrito Federal, Brazil

Cuiabá, Mato Grosso, Brazil

Uberlândia, Minas Gerais, Brazil

Curitiba, Paraná, Brazil

Recife, Pernambuco, Brazil

Tapejara, Rio Grande Do Sul, Brazil

Florianopolis, Santa Catarina, Brazil

Campinas, São Paulo, Brazil

Ourinhos, São Paulo, Brazil

São Paulo, , Brazil

Sofia, , Bulgaria

Calgary, Alberta, Canada

Edmonton, Alberta, Canada

Vancouver, British Columbia, Canada

Vancouver, British Columbia, Canada

Winnipeg, Manitoba, Canada

St. John's, Newfoundland And Labrador, Canada

Halifax, Nova Scotia, Canada

London, Ontario, Canada

Toronto, Ontario, Canada

Toronto, Ontario, Canada

Montreal, Quebec, Canada

Sherbrooke, Quebec, Canada

Antofagasta, , Chile

Coquimbo, , Chile

Iquique, , Chile

Vallenar, , Chile

Jinan, , China

Nanjing, , China

Rijena, , Croatia

Praha 2, , Czechia

Copenhagen, , Denmark

Tartu, , Estonia

Turku, , Finland

Bordeaux, , France

Bron Cedex, , France

Garches, , France

Lille, , France

Limoges Cedex, , France

Marseille, , France

Saint Priest En Jarez, , France

Strasbourg, , France

Berlin, , Germany

Münster, , Germany

Würzburg, , Germany

Budapest, , Hungary

Létavértes, , Hungary

Sopron, , Hungary

Bassano Del Grappa (Vi), , Italy

Firenze, , Italy

Firenze, , Italy

Genova, , Italy

Milano, , Italy

Milano, , Italy

Modena, , Italy

Monza (Mb), , Italy

Napoli, , Italy

Rimini, , Italy

Roma, , Italy

Torino, , Italy

Vittoria (Rg), , Italy

Nangoku Shi, Kochi, Japan

Niigata Shi, Niigata, Japan

Abeno Ku, Osaka, Japan

Setagaya, Tokyo, Japan

Chiba, , Japan

Kobe Shi, Hyogo, , Japan

Busan, , Korea, Republic Of

Seoul, , Korea, Republic Of

Suwon Si, , Korea, Republic Of

Vilnius, , Lithuania

Vilnius, , Lithuania

Bergen, , Norway

Callao, , Peru

Lisboa, , Portugal

Porto, , Portugal

Bucuresti, , Romania

Cluj Napoca, , Romania

Moscow, , Russian Federation

Nizhny Novgorod, , Russian Federation

Saint Peterburg, , Russian Federation

Al Mubarraz, , Saudi Arabia

Novi Sad, , Serbia

Slovenj Gradec, , Slovenia

Barakaldo, , Spain

Barcelona, , Spain

Barcelona, , Spain

Barcelona, , Spain

Barcelona, , Spain

Barcelona, , Spain

Barcelona, , Spain

La Coruña, , Spain

La Coruña, , Spain

Tarragona, , Spain

Vigo, , Spain

Göteborg, , Sweden

Stockholm, , Sweden

Kaohsiung City, , Taiwan

Taichung, , Taiwan

Cambridge, Cambridgeshire, United Kingdom

Belfast, , United Kingdom

London, , United Kingdom

London, , United Kingdom

Manchester, , United Kingdom

Salford, , United Kingdom

Phoenix, Arizona, United States

Little Rock, Arkansas, United States

Los Angeles, California, United States

Los Angeles, California, United States

Oakland, California, United States

Orange, California, United States

Palo Alto, California, United States

Sacramento, California, United States

San Bernardino, California, United States

San Diego, California, United States

San Francisco, California, United States

New Haven, Connecticut, United States

Washington, District Of Columbia, United States

Gainesville, Florida, United States

Jacksonville, Florida, United States

Jacksonville, Florida, United States

Miami, Florida, United States

Decatur, Georgia, United States

Chicago, Illinois, United States

Indianapolis, Indiana, United States

Iowa City, Iowa, United States

Louisville, Kentucky, United States

Baltimore, Maryland, United States

Boston, Massachusetts, United States

Springfield, Massachusetts, United States

Ann Arbor, Michigan, United States

Detroit, Michigan, United States

Minneapolis, Minnesota, United States

Minneapolis, Minnesota, United States

Saint Louis, Missouri, United States

Omaha, Nebraska, United States

Las Vegas, Nevada, United States

Hackensack, New Jersey, United States

Morristown, New Jersey, United States

New Brunswick, New Jersey, United States

Paterson, New Jersey, United States

Manhasset, New York, United States

New York, New York, United States

New York, New York, United States

Rochester, New York, United States

Syracuse, New York, United States

Cleveland, Ohio, United States

Columbus, Ohio, United States

Dublin, Ohio, United States

Philadelphia, Pennsylvania, United States

Philadelphia, Pennsylvania, United States

Pittsburgh, Pennsylvania, United States

Providence, Rhode Island, United States

Greenville, South Carolina, United States

Dallas, Texas, United States

Charlottesville, Virginia, United States

Norfolk, Virginia, United States

Seattle, Washington, United States

Seattle, Washington, United States

Tacoma, Washington, United States

Milwaukee, Wisconsin, United States

Brussels, , Belgium

Moncton, New Brunswick, Canada

Seoul, Gyeonggi Do, Korea, Republic Of

Kaohsiung City, , Taiwan

Taichung, , Taiwan

Tainan City, , Taiwan

Tainan City, , Taiwan

Taipei City, , Taiwan

Taoyuan City, , Taiwan

Birmingham, , United Kingdom

London, , United Kingdom

London, , United Kingdom

Manchester, , United Kingdom

Birmingham, Alabama, United States

Birmingham, Alabama, United States

Tucson, Arizona, United States

Little Rock, Arkansas, United States

Irvine, California, United States

Los Angeles, California, United States

Sacramento, California, United States

Coral Springs, Florida, United States

Tampa, Florida, United States

Aurora, Illinois, United States

Chicago, Illinois, United States

Kansas City, Kansas, United States

Baton Rouge, Louisiana, United States

New Orleans, Louisiana, United States

Portland, Maine, United States

Boston, Massachusetts, United States

Boston, Massachusetts, United States

Grand Rapids, Michigan, United States

Grand Rapids, Michigan, United States

Minneapolis, Minnesota, United States

Columibia, Missouri, United States

Billings, Montana, United States

Helena, Montana, United States

Camden, New Jersey, United States

New York, New York, United States

Valhalla, New York, United States

Charlotte, North Carolina, United States

Durham, North Carolina, United States

Cincinnati, Ohio, United States

Cleveland, Ohio, United States

Columbus, Ohio, United States

Portland, Oregon, United States

Portland, Oregon, United States

Danville, Pennsylvania, United States

Hershey, Pennsylvania, United States

Nashville, Tennessee, United States

Fort Worth, Texas, United States

Salt Lake City, Utah, United States

Fairfax, Virginia, United States

Buenos Aires, , Argentina

Brisbane, Queensland, Australia

Antwerp, , Belgium

Antwerp, , Belgium

Brussels, , Belgium

Feira De Santana, Bahia, Brazil

Brasília, Distrito Federal, Brazil

Cuiabá, Mato Grosso, Brazil

Uberlândia, Minas Gerais, Brazil

Curitiba, Paraná, Brazil

Recife, Pernambuco, Brazil

Tapejara, Rio Grande Do Sul, Brazil

Florianopolis, Santa Catarina, Brazil

Campinas, São Paulo, Brazil

Ourinhos, São Paulo, Brazil

São Paulo, , Brazil

Kingston, Ontario, Canada

Santiago, , Chile

Beijing, , China

Jinan, , China

Shanghai, , China

Turku, , Finland

Limoges, , France

Marseille, , France

St Priest En Jarez, , France

Strasbourg, , France

Kobe, , Japan

Niigata, , Japan

Tokyo, , Japan

Yangsan, Gyeongsangnam Do, Korea, Republic Of

Jeju Si, , Korea, Republic Of

Vilnius, , Lithuania

Amsterdam, , Netherlands

A Coruña, , Spain

A Coruña, , Spain

Tarragona, , Spain

Taipei City, , Taiwan

Cambridge, Cambridgeshire, United Kingdom

Cleveland, Ohio, United States

Calgary, Alberta, Canada

Seoul, Seoul Teukbyeolsi, Korea, Republic Of

Seoul, Seoul Teukbyeolsi, Korea, Republic Of

Birmingham, England, United Kingdom

Curitiba, , Brazil

Campinas, , Brazil

Ourinhos, , Brazil

São Paulo, , Brazil

Kobe, Hyogo, Japan

Barakaldo, Pais Vasco, Spain

Salford, Manchester, United Kingdom

Manchester, , United Kingdom

Patients applied

0 patients applied

Trial Officials

Study Director

Study Director

Genzyme, a Sanofi Company

Timeline

First submit

Trial launched

Trial updated

Estimated completion

Not reported

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