Pompe Disease Registry Protocol
Launched by GENZYME, A SANOFI COMPANY · Sep 30, 2005
Trial Information
Current as of July 26, 2025
Recruiting
Keywords
ClinConnect Summary
The Pompe Disease Registry is an international study that aims to learn more about Pompe disease, a rare genetic condition that affects how the body processes glycogen, a type of sugar stored in muscles. This study is designed for anyone diagnosed with Pompe disease, whether they are currently receiving treatment or not. By collecting and tracking health information from participants over time, researchers hope to better understand how the disease progresses and how it affects patients. This information will help improve care, develop new treatments, and ensure that patients receive the best possible support.
To take part in this study, participants need to have a confirmed diagnosis of Pompe disease, which means they should have specific test results showing low levels of a certain enzyme or mutations in the GAA gene. There are no age or gender restrictions, and anyone who meets the criteria can join. By participating, individuals will contribute valuable information that may help improve treatment options for themselves and others with Pompe disease.
Gender
ALL
Eligibility criteria
- Inclusion Criteria:
- • All patients with a confirmed diagnosis of Pompe disease who have signed the informed consent and authorization form(s) are eligible for inclusion. Confirmed diagnosis is defined as documented GAA enzyme deficiency from blood, skin, or muscle tissue and/or documentation of 2 GAA gene mutations.
- Exclusion Criteria:
- • There are no exclusion criteria in this Registry
About Genzyme, A Sanofi Company
Genzyme, a Sanofi company, is a global leader in biotechnology dedicated to developing innovative therapies for rare and complex diseases. With a strong focus on patient-centric solutions, Genzyme leverages advanced research and development capabilities to address unmet medical needs across various therapeutic areas, including neurology, oncology, and genetic disorders. Committed to scientific excellence and collaboration, Genzyme aims to improve patient outcomes through the discovery and commercialization of high-quality biopharmaceuticals, while upholding the highest standards of safety and efficacy in clinical trials.
Contacts
Jennifer Cobb
Immunology at National Institute of Allergy and Infectious Diseases (NIAID)
Locations
Phoenix, Arizona, United States
Little Rock, Arkansas, United States
Los Angeles, California, United States
Los Angeles, California, United States
Oakland, California, United States
Orange, California, United States
Sacramento, California, United States
San Bernardino, California, United States
San Diego, California, United States
San Francisco, California, United States
Aurora, Colorado, United States
New Haven, Connecticut, United States
Washington, District Of Columbia, United States
Jacksonville, Florida, United States
Miami, Florida, United States
Decatur, Georgia, United States
Chicago, Illinois, United States
Chicago, Illinois, United States
Indianapolis, Indiana, United States
Iowa City, Iowa, United States
Louisville, Kentucky, United States
New Orleans, Louisiana, United States
Baltimore, Maryland, United States
Boston, Massachusetts, United States
Springfield, Massachusetts, United States
Ann Arbor, Michigan, United States
Detroit, Michigan, United States
Minneapolis, Minnesota, United States
Minneapolis, Minnesota, United States
Saint Louis, Missouri, United States
Omaha, Nebraska, United States
Las Vegas, Nevada, United States
Hackensack, New Jersey, United States
Morristown, New Jersey, United States
New Brunswick, New Jersey, United States
Paterson, New Jersey, United States
Manhasset, New York, United States
New York, New York, United States
New York, New York, United States
Rochester, New York, United States
Syracuse, New York, United States
Durham, North Carolina, United States
Cincinnati, Ohio, United States
Cleveland, Ohio, United States
Columbus, Ohio, United States
Dublin, Ohio, United States
Philadelphia, Pennsylvania, United States
Philadelphia, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Providence, Rhode Island, United States
Greenville, South Carolina, United States
Dallas, Texas, United States
Charlottesville, Virginia, United States
Norfolk, Virginia, United States
Seattle, Washington, United States
Seattle, Washington, United States
Tacoma, Washington, United States
Milwaukee, Wisconsin, United States
Ciudad Autónoma De Buenos Aires, Buenos Aires, Argentina
Westmead, New South Wales, Australia
Brisbane, Queensland, Australia
Leuven, , Belgium
São Paulo, , Brazil
Calgary, Alberta, Canada
Edmonton, Alberta, Canada
Vancouver, British Columbia, Canada
Winnipeg, Manitoba, Canada
Moncton, New Brunswick, Canada
London, Ontario, Canada
Toronto, Ontario, Canada
Montreal, Quebec, Canada
Sherbrooke, Quebec, Canada
Zagreb, , Croatia
København ø, , Denmark
Marseille Cedex 05, , France
Mainz, , Germany
Ahmedabad, , India
Kolkata, , India
Secunderabad, , India
Vellore, , India
Jakarta, , Indonesia
Busan, , Korea, Republic Of
Daejeon, , Korea, Republic Of
Jeonnam, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Yangsan, , Korea, Republic Of
Kuwait, , Kuwait
Beirut, , Lebanon
Jalan Pahang, , Malaysia
Kuala Lumpur, , Malaysia
Rotterdam, , Netherlands
Lahore, , Pakistan
Manila, , Philippines
Warszawa, , Poland
Makkah, , Saudi Arabia
Qatif, , Saudi Arabia
Singapore, , Singapore
Bratislava, , Slovakia
Chiayi, , Taiwan
Hualien, , Taiwan
Kaohsiung Hsien,, , Taiwan
Kaohsiung, , Taiwan
New Taipei City, , Taiwan
Putz City, Chia Yi, , Taiwan
Taichung City, , Taiwan
Taichung, , Taiwan
Tainan, , Taiwan
Tainan, , Taiwan
Taipei, , Taiwan
Taipei, , Taiwan
Tao Yuan County, , Taiwan
Bangkok, , Thailand
Bangkok, , Thailand
Bangkok, , Thailand
Bangkok, , Thailand
Khon Kaen, , Thailand
Dubai, , United Arab Emirates
Birmingham, , United Kingdom
Birmingham, , United Kingdom
Glasgow, , United Kingdom
London, , United Kingdom
London, , United Kingdom
London, , United Kingdom
Hanoi, , Vietnam
Ho Chi Minh City, , Vietnam
Tucson, Arizona, United States
Little Rock, Arkansas, United States
Aurora, California, United States
Irvine, California, United States
Tampa, Florida, United States
Chicago, Illinois, United States
Portland, Maine, United States
Boston, Massachusetts, United States
Grand Rapids, Michigan, United States
Grand Rapids, Michigan, United States
Minneapolis, Minnesota, United States
Columibia, Missouri, United States
Camden, New Jersey, United States
Valhalla, New York, United States
Charlotte, North Carolina, United States
Cleveland, Ohio, United States
Portland, Oregon, United States
Nashville, Tennessee, United States
Fort Worth, Texas, United States
Salt Lake City, Utah, United States
Fairfax, Virginia, United States
Westmead, New South Wales, Australia
Adelaide, South Australia, Australia
Antwerpen, , Belgium
Sofia, , Bulgaria
Vancouver, British Columbia, Canada
Zagreb, , Croatia
Gießen, , Germany
Bucuresti, , Romania
Taipei, , Taiwan
Dubai, , United Arab Emirates
Cambridge, Cambridgeshire, United Kingdom
Birmingham, Alabama, United States
Phoenix, Arizona, United States
Loma Linda, California, United States
Stanford, California, United States
Gainesville, Florida, United States
Kansas City, Kansas, United States
Minneapolis, Minnesota, United States
Kansas City, Missouri, United States
New York, New York, United States
Portland, Oregon, United States
Portland, Oregon, United States
Hershey, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Caba, Buenos Aires, Argentina
Caba, Buenos Aires, Argentina
Herston, Queensland, Australia
Murdoch, Western Australia, Australia
Murdoch, Western Australia, Australia
Brugge, , Belgium
Bruxelles, , Belgium
Bruxelles, , Belgium
Edegem, , Belgium
Gent, , Belgium
Gosselies, , Belgium
Leuven, , Belgium
Fortaleza, Ceará, Brazil
Cuiabá, Mato Grosso, Brazil
Porto Alegre, Rio Grande Do Sul, Brazil
Ribeirão Preto, São Paulo, Brazil
Rio De Janeiro, , Brazil
São Paulo, , Brazil
São Paulo, , Brazil
São Paulo, , Brazil
Hamilton, Ontario, Canada
Montreal, Quebec, Canada
Punta Arenas, , Chile
Santiago, , Chile
Beijing, , China
Beijing, , China
Beijing, , China
Guangzhou, , China
Jinan, , China
Shanghai, , China
Shanghai, , China
Bogota, , Colombia
Praha 2, , Czechia
Bordeaux, , France
Brest, , France
Bron Cedex, , France
Bron Cedex, , France
Caen, , France
Grenoble Cedex, , France
Lille Cedex, , France
Nancy Cedex, , France
Nantes Cedex 1, , France
Nice Cedex 1, , France
Nimes Cedex 9, , France
Paris Cedex 13, , France
Paris, , France
St Etienne, , France
Strasbourg Cedex 2, , France
Toulouse, , France
Tours, , France
Vannes, , France
Berlin, , Germany
Berlin, , Germany
Berlin, , Germany
Bochum, , Germany
Bonn, , Germany
Freiburg, , Germany
Halle (Saale), , Germany
Hamburg, , Germany
München, , Germany
Münster, , Germany
Thessaloniki, , Greece
Debrecen, , Hungary
Nyíregyháza, , Hungary
Pécs, , Hungary
Székesfehérvár, , Hungary
Beer Sheva, , Israel
Haifa, , Israel
Tel Aviv, , Israel
Brescia, , Italy
Cagliari, , Italy
Ferrara, , Italy
Firenze, , Italy
Genova, , Italy
Messina, , Italy
Milano, , Italy
Milano, , Italy
Monza, , Italy
Napoli, , Italy
Napoli, , Italy
Padova, , Italy
Padova, , Italy
Pavia, , Italy
Roma, , Italy
Roma, , Italy
Torino, , Italy
Udine, , Italy
Sakyo Ku, Kyoto, Japan
Ginowan, Okinawa, Japan
Amman, , Jordan
Seoul, , Korea, Republic Of
Hazmieh, , Lebanon
Karachi, , Pakistan
Coimbra, , Portugal
Lisboa, , Portugal
Moscow, , Russian Federation
Belgrade, , Serbia
Cardiff, , United Kingdom
Manchester, , United Kingdom
Newcastle, , United Kingdom
Salford, , United Kingdom
Nyíregyháza, , Hungary
Phoenix, Arizona, United States
Little Rock, Arkansas, United States
Los Angeles, California, United States
Los Angeles, California, United States
Orange, California, United States
Sacramento, California, United States
San Bernardino, California, United States
San Diego, California, United States
San Francisco, California, United States
Aurora, Colorado, United States
Aurora, Colorado, United States
New Haven, Connecticut, United States
Washington, District Of Columbia, United States
Jacksonville, Florida, United States
Jacksonville, Florida, United States
Miami, Florida, United States
Decatur, Georgia, United States
Chicago, Illinois, United States
Chicago, Illinois, United States
Indianapolis, Indiana, United States
Iowa City, Iowa, United States
Louisville, Kentucky, United States
New Orleans, Louisiana, United States
Baltimore, Maryland, United States
Boston, Massachusetts, United States
Springfield, Massachusetts, United States
Ann Arbor, Michigan, United States
Detroit, Michigan, United States
Minneapolis, Minnesota, United States
Minneapolis, Minnesota, United States
Saint Louis, Missouri, United States
Omaha, Nebraska, United States
Las Vegas, Nevada, United States
Morristown, New Jersey, United States
New Brunswick, New Jersey, United States
Paterson, New Jersey, United States
Manhasset, New York, United States
New York, New York, United States
New York, New York, United States
Rochester, New York, United States
Syracuse, New York, United States
Durham, North Carolina, United States
Cincinnati, Ohio, United States
Cleveland, Ohio, United States
Columbus, Ohio, United States
Dublin, Ohio, United States
Philadelphia, Pennsylvania, United States
Philadelphia, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Providence, Rhode Island, United States
Greenville, South Carolina, United States
Dallas, Texas, United States
Charlottesville, Virginia, United States
Norfolk, Virginia, United States
Seattle, Washington, United States
Seattle, Washington, United States
Tacoma, Washington, United States
Milwaukee, Wisconsin, United States
Buenos Aires, , Argentina
Calgary, Alberta, Canada
København, , Denmark
Tucson, Arizona, United States
Little Rock, Arkansas, United States
Irvine, California, United States
Tampa, Florida, United States
Chicago, Illinois, United States
Portland, Maine, United States
Boston, Massachusetts, United States
Grand Rapids, Michigan, United States
Grand Rapids, Michigan, United States
Minneapolis, Minnesota, United States
Columibia, Missouri, United States
Camden, New Jersey, United States
Valhalla, New York, United States
Cleveland, Ohio, United States
Portland, Oregon, United States
Nashville, Tennessee, United States
Fort Worth, Texas, United States
Salt Lake City, Utah, United States
Fairfax, Virginia, United States
Birmingham, Alabama, United States
Phoenix, Arizona, United States
Irvine, California, United States
Loma Linda, California, United States
Oakland, California, United States
Stanford, California, United States
Gainesville, Florida, United States
Kansas City, Kansas, United States
Minneapolis, Minnesota, United States
Kansas City, Missouri, United States
Hackensack, New Jersey, United States
New York, New York, United States
Charlotte, North Carolina, United States
Portland, Oregon, United States
Portland, Oregon, United States
Hershey, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Cuiabá, , Brazil
Fortaleza, , Brazil
Ribeirão Preto, , Brazil
Vannes Cedex, , France
Debrecen, , Hungary
Pécs, , Hungary
Székesfehérvár, , Hungary
Tacoma, Washington, United States
Yangsan Si, Gyeongsangnam Do, Korea, Republic Of
Oakland, Virginia, United States
Ribeirao Preto, São Paulo, Brazil
New York, New York, United States
Irvine, California, United States
Kowloon, , Hong Kong
Nyíregyháza, , Hungary
Udine, , Italy
Zagreb, , Croatia
Zagreb, , Croatia
Belgrade, , Serbia
Birmingham, Alabama, United States
Little Rock, Arkansas, United States
Little Rock, Arkansas, United States
Loma Linda, California, United States
Los Angeles, California, United States
Oakland, California, United States
San Bernardino, California, United States
San Diego, California, United States
Aurora, Colorado, United States
New Haven, Connecticut, United States
Washington, District Of Columbia, United States
Gainesville, Florida, United States
Jacksonville, Florida, United States
Jacksonville, Florida, United States
Tampa, Florida, United States
Decatur, Georgia, United States
Chicago, Illinois, United States
Chicago, Illinois, United States
Chicago, Illinois, United States
Indianapolis, Indiana, United States
Kansas City, Kansas, United States
Louisville, Kentucky, United States
New Orleans, Louisiana, United States
Portland, Maine, United States
Baltimore, Maryland, United States
Boston, Massachusetts, United States
Boston, Massachusetts, United States
Springfield, Massachusetts, United States
Ann Arbor, Michigan, United States
Grand Rapids, Michigan, United States
Grand Rapids, Michigan, United States
Minneapolis, Minnesota, United States
Minneapolis, Minnesota, United States
Columibia, Missouri, United States
Kansas City, Missouri, United States
Saint Louis, Missouri, United States
Omaha, Nebraska, United States
Hackensack, New Jersey, United States
Morristown, New Jersey, United States
New Brunswick, New Jersey, United States
Paterson, New Jersey, United States
Manhasset, New York, United States
New York, New York, United States
New York, New York, United States
New York, New York, United States
Rochester, New York, United States
Syracuse, New York, United States
Valhalla, New York, United States
Charlotte, North Carolina, United States
Durham, North Carolina, United States
Cincinnati, Ohio, United States
Cleveland, Ohio, United States
Cleveland, Ohio, United States
Columbus, Ohio, United States
Dublin, Ohio, United States
Portland, Oregon, United States
Hershey, Pennsylvania, United States
Philadelphia, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Providence, Rhode Island, United States
Greenville, South Carolina, United States
Nashville, Tennessee, United States
Dallas, Texas, United States
Fort Worth, Texas, United States
Charlottesville, Virginia, United States
Fairfax, Virginia, United States
Norfolk, Virginia, United States
Tacoma, Washington, United States
Milwaukee, Wisconsin, United States
Caba, Buenos Aires, Argentina
Caba, Buenos Aires, Argentina
Ciudad Autónoma De Buenos Aires, Buenos Aires, Argentina
Westmead, New South Wales, Australia
Westmead, New South Wales, Australia
Herston, Queensland, Australia
Adelaide, South Australia, Australia
Murdoch, Western Australia, Australia
Antwerpen, , Belgium
Brugge, , Belgium
Bruxelles, , Belgium
Bruxelles, , Belgium
Edegem, , Belgium
Gent, , Belgium
Gosselies, , Belgium
Leuven, , Belgium
Leuven, , Belgium
Fortaleza, Ceará, Brazil
Porto Alegre, Rio Grande Do Sul, Brazil
Ribeirao Preto, São Paulo, Brazil
Rio De Janeiro, , Brazil
São Paulo, , Brazil
São Paulo, , Brazil
São Paulo, , Brazil
São Paulo, , Brazil
Sofia, , Bulgaria
Moncton, New Brunswick, Canada
Montreal, Quebec, Canada
Punta Arenas, , Chile
Santiago, , Chile
Beijing, , China
Bogota, , Colombia
København ø, , Denmark
Bordeaux, , France
Brest, , France
Bron Cedex, , France
Bron Cedex, , France
Caen, , France
Grenoble Cedex, , France
Lille Cedex, , France
Marseille Cedex 05, , France
Nancy Cedex, , France
Nantes Cedex 1, , France
Nice Cedex 1, , France
Nimes Cedex 9, , France
Paris Cedex 13, , France
Paris, , France
St Etienne, , France
Strasbourg Cedex 2, , France
Toulouse, , France
Tours, , France
Vannes Cedex, , France
Gießen, , Germany
Hamburg, , Germany
Thessaloniki, , Greece
Kowloon, , Hong Kong
Debrecen, , Hungary
Pécs, , Hungary
Székesfehérvár, , Hungary
Ahmedabad, , India
Kolkata, , India
Secunderabad, , India
Vellore, , India
Jakarta, , Indonesia
Tel Aviv, , Israel
Brescia, , Italy
Cagliari, , Italy
Ferrara, , Italy
Firenze, , Italy
Genova, , Italy
Messina, , Italy
Milano, , Italy
Milano, , Italy
Monza, , Italy
Napoli, , Italy
Napoli, , Italy
Padova, , Italy
Padova, , Italy
Pavia, , Italy
Roma, , Italy
Roma, , Italy
Torino, , Italy
Sakyo Ku, Kyoto, Japan
Ginowan, Okinawa, Japan
Amman, , Jordan
Yangsan Si, Gyeongsangnam Do, Korea, Republic Of
Daejeon, , Korea, Republic Of
Jeonnam, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Seoul, , Korea, Republic Of
Yangsan, , Korea, Republic Of
Kuwait, , Kuwait
Beirut, , Lebanon
Hazmieh, , Lebanon
Jalan Pahang, , Malaysia
Lembah Pantai, , Malaysia
Rotterdam, , Netherlands
Karachi, , Pakistan
Lahore, , Pakistan
Manila, , Philippines
Warszawa, , Poland
Coimbra, , Portugal
Lisboa, , Portugal
Bucuresti, , Romania
Moscow, , Russian Federation
Makkah, , Saudi Arabia
Qatif, , Saudi Arabia
Singapore, , Singapore
Bratislava, , Slovakia
Chiayi, , Taiwan
Hualien, , Taiwan
Kaohsiung Hsien,, , Taiwan
Kaohsiung, , Taiwan
New Taipei City, , Taiwan
Putz City, Chia Yi, , Taiwan
Taichung City, , Taiwan
Taichung, , Taiwan
Tainan, , Taiwan
Tainan, , Taiwan
Taipei, , Taiwan
Taipei, , Taiwan
Taipei, , Taiwan
Tao Yuan County, , Taiwan
Bangkok, , Thailand
Bangkok, , Thailand
Bangkok, , Thailand
Bangkok, , Thailand
Khon Kaen, , Thailand
Birmingham, , United Kingdom
Birmingham, , United Kingdom
Hanoi, , Vietnam
Ho Chi Minh City, , Vietnam
Brisbane, Queensland, Australia
Yangsan, Gyeongsangnam Do, Korea, Republic Of
Kuala Lumpur, , Malaysia
Calgary, Alberta, Canada
Edmonton, Alberta, Canada
Vancouver, British Columbia, Canada
Vancouver, British Columbia, Canada
Winnipeg, Manitoba, Canada
London, Ontario, Canada
Toronto, Ontario, Canada
Sherbrooke, Quebec, Canada
London, , United Kingdom
Praha 2, , Czechia
Berlin, , Germany
Mainz, , Germany
Montreal, Quebec, Canada
Glasgow, , United Kingdom
Phoenix, Arizona, United States
Little Rock, Arkansas, United States
Los Angeles, California, United States
Los Angeles, California, United States
Oakland, California, United States
Orange, California, United States
Sacramento, California, United States
San Bernardino, California, United States
San Diego, California, United States
San Francisco, California, United States
Aurora, Colorado, United States
New Haven, Connecticut, United States
Washington, District Of Columbia, United States
Jacksonville, Florida, United States
Jacksonville, Florida, United States
Miami, Florida, United States
Decatur, Georgia, United States
Chicago, Illinois, United States
Chicago, Illinois, United States
Indianapolis, Indiana, United States
Iowa City, Iowa, United States
Louisville, Kentucky, United States
New Orleans, Louisiana, United States
Baltimore, Maryland, United States
Boston, Massachusetts, United States
Springfield, Massachusetts, United States
Ann Arbor, Michigan, United States
Detroit, Michigan, United States
Minneapolis, Minnesota, United States
Minneapolis, Minnesota, United States
Saint Louis, Missouri, United States
Omaha, Nebraska, United States
Las Vegas, Nevada, United States
Morristown, New Jersey, United States
New Brunswick, New Jersey, United States
Paterson, New Jersey, United States
Manhasset, New York, United States
New York, New York, United States
New York, New York, United States
Rochester, New York, United States
Syracuse, New York, United States
Durham, North Carolina, United States
Cincinnati, Ohio, United States
Cleveland, Ohio, United States
Columbus, Ohio, United States
Dublin, Ohio, United States
Philadelphia, Pennsylvania, United States
Philadelphia, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Providence, Rhode Island, United States
Greenville, South Carolina, United States
Dallas, Texas, United States
Charlottesville, Virginia, United States
Norfolk, Virginia, United States
Seattle, Washington, United States
Seattle, Washington, United States
Tacoma, Washington, United States
Milwaukee, Wisconsin, United States
São Paulo, , Brazil
Moncton, New Brunswick, Canada
Seoul, Gyeonggi Do, Korea, Republic Of
Rotterdam, , Netherlands
Kaohsiung City, , Taiwan
Taichung, , Taiwan
Tainan City, , Taiwan
Tainan City, , Taiwan
Taipei City, , Taiwan
Taoyuan City, , Taiwan
Birmingham, , United Kingdom
London, , United Kingdom
London, , United Kingdom
Tucson, Arizona, United States
Little Rock, Arkansas, United States
Tampa, Florida, United States
Aurora, Illinois, United States
Chicago, Illinois, United States
Portland, Maine, United States
Boston, Massachusetts, United States
Grand Rapids, Michigan, United States
Grand Rapids, Michigan, United States
Minneapolis, Minnesota, United States
Columibia, Missouri, United States
Camden, New Jersey, United States
Valhalla, New York, United States
Cleveland, Ohio, United States
Portland, Oregon, United States
Nashville, Tennessee, United States
Fort Worth, Texas, United States
Salt Lake City, Utah, United States
Fairfax, Virginia, United States
Antwerp, , Belgium
Taipei City, , Taiwan
Cambridge, Cambridgeshire, United Kingdom
Birmingham, Alabama, United States
Phoenix, Arizona, United States
Irvine, California, United States
Loma Linda, California, United States
Stanford, California, United States
Gainesville, Florida, United States
Kansas City, Kansas, United States
Minneapolis, Minnesota, United States
Kansas City, Missouri, United States
Hackensack, New Jersey, United States
New York, New York, United States
Charlotte, North Carolina, United States
Portland, Oregon, United States
Portland, Oregon, United States
Hershey, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Brisbane, Queensland, Australia
Bruges, , Belgium
Brussels, , Belgium
Fortaleza, Ceará, Brazil
Cuiabá, Mato Grosso, Brazil
Porto Alegre, Rio Grande Do Sul, Brazil
Ribeirão Preto, São Paulo, Brazil
Rio De Janeiro, , Brazil
São Paulo, , Brazil
São Paulo, , Brazil
São Paulo, , Brazil
Hamilton, Ontario, Canada
Beijing, , China
Beijing, , China
Guangzhou, , China
Jinan, , China
Shanghai, , China
Shanghai, , China
Bordeaux, , France
Caen, , France
La Tronche, , France
Lille, , France
Nancy, , France
Nantes, , France
Nîmes, , France
Paris, , France
St Priest En Jarez, , France
Strasbourg, , France
Toulouse, , France
Tours, , France
Berlin, , Germany
Berlin, , Germany
Bochum, , Germany
Bonn, , Germany
Freiburg, , Germany
Halle (Saale), , Germany
München, , Germany
Münster, , Germany
Thessaloniki, , Greece
Pã©Cs, , Hungary
Beer Sheva, , Israel
Haifa, , Israel
Milan, , Italy
Padua, , Italy
Seoul, Seoul Teukbyeolsi, Korea, Republic Of
Beirut, , Lebanon
Cardiff, , United Kingdom
Manchester, , United Kingdom
Newcastle, , United Kingdom
Salford, , United Kingdom
San Francisco, California, United States
Aurora, Colorado, United States
Gainesville, Florida, United States
Baltimore, Maryland, United States
Boston, Massachusetts, United States
Columbia, Missouri, United States
Camden, New Jersey, United States
Cincinnati, Ohio, United States
Cleveland, Ohio, United States
Philadelphia, Pennsylvania, United States
São Paulo, , Brazil
São Paulo, , Brazil
São Paulo, , Brazil
Calgary, Alberta, Canada
Nice, , France
Milan, Milano, Italy
Padua, Padova, Italy
Seoul, Seoul Teukbyeolsi, Korea, Republic Of
Seoul, Seoul Teukbyeolsi, Korea, Republic Of
Hualian, , Taiwan
Taipei, , Taiwan
Birmingham, England, United Kingdom
London, London, City Of, United Kingdom
London, London, City Of, United Kingdom
Fortaleza, , Brazil
Ribeirão Preto, , Brazil
Patients applied
Trial Officials
Study Director
Study Director
Genzyme, a Sanofi Company
Timeline
First submit
Trial launched
Trial updated
Estimated completion
Not reported
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