A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Launched by CENTER FOR INTERNATIONAL BLOOD AND MARROW TRANSPLANT RESEARCH · May 10, 2011
Trial Information
Current as of June 26, 2025
Recruiting
Keywords
ClinConnect Summary
This clinical trial is looking at how to provide access to special cord blood units (CBUs) that have not yet been licensed for use. These CBUs are frozen and can be used to help treat various blood-related diseases, such as leukemia, lymphoma, and certain inherited disorders. The study is open to both children and adults who have specific conditions affecting their blood or immune system. To participate, individuals need to give their consent, and if they are minors, their parents or guardians will need to agree as well.
Eligible participants must have a medical condition that affects their blood, either inherited or caused by previous treatments. However, those who are already receiving licensed cord blood units or are part of other related studies cannot join this trial. If you decide to participate, you will be part of a group helping to explore how these unlicensed cord blood units can be safely and effectively used in treatment, potentially paving the way for new options for patients in the future.
Gender
ALL
Eligibility criteria
- Inclusion Criteria:
- • Disorders affecting the hematopoietic system that are inherited, acquired, or result from myeloablative treatment
- • Signed informed consent (and signed assent, if applicable) obtained prior to study enrollment
- • Pediatric and adult patients of any age
- Exclusion Criteria:
- • Patients who are receiving only licensed CBUs
- • Cord blood transplant recipients at international transplant centers
- • Patients who are enrolled on another IND protocol to access the unlicensed CBU(s)
- • Patients whose selected unlicensed CBU(s) will be more than minimally manipulated
About Center For International Blood And Marrow Transplant Research
The Center for International Blood and Marrow Transplant Research (CIBMTR) is a leading organization dedicated to advancing the field of hematopoietic cell transplantation through robust research and data analysis. As a collaborative partnership between the National Marrow Donor Program and the Medical College of Wisconsin, CIBMTR collects and analyzes data from a global network of transplant centers, facilitating groundbreaking research that informs clinical practices and improves patient outcomes. With a commitment to enhancing the understanding of blood and marrow transplant procedures, CIBMTR plays a pivotal role in shaping treatment protocols, optimizing patient care, and fostering innovation in transplant medicine.
Contacts
Jennifer Cobb
Immunology at National Institute of Allergy and Infectious Diseases (NIAID)
Locations
Ann Arbor, Michigan, United States
Boston, Massachusetts, United States
New York, New York, United States
Durham, North Carolina, United States
Durham, North Carolina, United States
Milwaukee, Wisconsin, United States
Rochester, Minnesota, United States
Charleston, South Carolina, United States
Chicago, Illinois, United States
Winston Salem, North Carolina, United States
Nashville, Tennessee, United States
Charlottesville, Virginia, United States
Philadelphia, Pennsylvania, United States
Iowa City, Iowa, United States
Buffalo, New York, United States
Seattle, Washington, United States
Jacksonville, Florida, United States
Detroit, Michigan, United States
Maywood, Illinois, United States
Chicago, Illinois, United States
New York, New York, United States
Zion, Illinois, United States
Hackensack, New Jersey, United States
Washington, District Of Columbia, United States
St. Petersburg, Florida, United States
Chicago, Illinois, United States
Omaha, Nebraska, United States
Saint Petersburg, Florida, United States
Chicago, Illinois, United States
Phoenix, Arizona, United States
La Jolla, California, United States
Boston, Massachusetts, United States
Augusta, Georgia, United States
Duarte, California, United States
Worcester, Massachusetts, United States
Detroit, Michigan, United States
Birmingham, Alabama, United States
Aurora, Colorado, United States
Orlando, Florida, United States
Boston, Massachusetts, United States
New York, New York, United States
Cleveland, Ohio, United States
Washington, District Of Columbia, United States
Honolulu, Hawaii, United States
Dallas, Texas, United States
Aurora, Colorado, United States
Park Ridge, Illinois, United States
Saint Louis, Missouri, United States
Columbus, Ohio, United States
Los Angeles, California, United States
Chapel Hill, North Carolina, United States
Milwaukee, Wisconsin, United States
San Diego, California, United States
Chapel Hill, North Carolina, United States
Houston, Texas, United States
Tampa, Florida, United States
Richmond, Virginia, United States
Bronx, New York, United States
Atlanta, Georgia, United States
Little Rock, Arkansas, United States
Honolulu, Hawaii, United States
Grand Rapids, Michigan, United States
Providence, Rhode Island, United States
Detroit, Michigan, United States
La Jolla, California, United States
Atlanta, Georgia, United States
Chicago, Illinois, United States
Boston, Massachusetts, United States
St. Louis, Missouri, United States
Saint Louis, Missouri, United States
Baltimore, Maryland, United States
Boston, Massachusetts, United States
Cincinnati, Ohio, United States
Dallas, Texas, United States
Pittsburgh, Pennsylvania, United States
New Orleans, Louisiana, United States
Atlanta, Georgia, United States
Stony Brook, New York, United States
Fort Worth, Texas, United States
Salt Lake City, Utah, United States
Pittsburgh, Pennsylvania, United States
Kansas City, Missouri, United States
St. Louis, Missouri, United States
Cleveland, Ohio, United States
Pittsburgh, Pennsylvania, United States
Lake Success, New York, United States
Dallas, Texas, United States
Lajolla, California, United States
Madison, Wisconsin, United States
Jackson, Mississippi, United States
Milwaukee, Wisconsin, United States
New Haven, Connecticut, United States
Sacramento, California, United States
Charlotte, North Carolina, United States
Nashville, Tennessee, United States
Stanford, California, United States
Memphis, Tennessee, United States
St. Louis, Missouri, United States
Grand Rapids, Michigan, United States
Saint Louis, Missouri, United States
Saint Louis, Missouri, United States
Washington Dc, District Of Columbia, United States
Orange, California, United States
Bethesda, Maryland, United States
New Hyde Park, New York, United States
Loma Linda, California, United States
Baltimore, Maryland, United States
Seattle, Washington, United States
Westwood, Kansas, United States
Indianapolis, Indiana, United States
Oakland, California, United States
Gilbert, Arizona, United States
Salt Lake City, Utah, United States
Omaha, Nebraska, United States
Phoenix, Arizona, United States
Tucson, Arizona, United States
Glendale, California, United States
San Francisco, California, United States
San Francisco, California, United States
Denver, Colorado, United States
Brandywine, Delaware, United States
Gainesville, Florida, United States
Jacksonville, Florida, United States
Miami, Florida, United States
Miami, Florida, United States
Miami, Florida, United States
Orlando, Florida, United States
Orlando, Florida, United States
Beech Grove, Indiana, United States
Louisville, Kentucky, United States
New Orleans, Louisiana, United States
Bethesda, Maryland, United States
Bethesda, Maryland, United States
New Brunswick, New Jersey, United States
New York, New York, United States
New York, New York, United States
New York, New York, United States
Rochester, New York, United States
Akron, Ohio, United States
Cincinnati, Ohio, United States
Columbus, Ohio, United States
Oklahoma City, Oklahoma, United States
Portland, Oregon, United States
Hershey, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Pittsburgh, Pennsylvania, United States
Sioux Falls, South Dakota, United States
Memphis, Tennessee, United States
Nashville, Tennessee, United States
Amarillo, Texas, United States
Fort Sam Houston, Texas, United States
Houston, Texas, United States
Lubbock, Texas, United States
San Antonio, Texas, United States
San Antonio, Texas, United States
Richmond, Virginia, United States
Morgantown, West Virginia, United States
St. Louis, Missouri, United States
Orlando, Florida, United States
Lake Sucess, New York, United States
New Hyde, New York, United States
Pittsburg, Pennsylvania, United States
Pittsburg, Pennsylvania, United States
Patients applied
Trial Officials
John Miller, MD, PhD
Study Chair
NMDP/CIBMTR
Timeline
First submit
Trial launched
Trial updated
Estimated completion
Not reported
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