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Search / Trial NCT02510261

The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis in Participants Who Have Already Been Treated With ALN-TTR02 (Patisiran)

Launched by ALNYLAM PHARMACEUTICALS · Jul 27, 2015

Trial Information

Current as of May 05, 2025

Completed

Keywords

Rn Ai Therapeutic Fap Familial Amyloid Polyneuropathy Ttr Transthyretin Amyloidosis

ClinConnect Summary

No description provided

Gender

ALL

Eligibility criteria

  • Inclusion Criteria:
  • Have completed a patisiran study (i.e., completed the last efficacy visit in the parent study) and, in the opinion of the investigator, tolerated study drug
  • Be willing and able to comply with the protocol-required visit schedule and visit requirements and provide written informed consent
  • Exclusion Criteria:
  • Any new or uncontrolled condition that could make the participant unsuitable for participation

About Alnylam Pharmaceuticals

Alnylam Pharmaceuticals is a pioneering biopharmaceutical company focused on the development of innovative therapies based on RNA interference (RNAi) technology. Founded in 2002, Alnylam is dedicated to transforming the treatment landscape for patients with genetically defined diseases by leveraging its proprietary platform to discover and develop novel therapeutics. With a robust pipeline of clinical programs targeting a range of conditions, including rare genetic disorders and prevalent diseases, Alnylam is committed to advancing scientific research and improving patient outcomes through cutting-edge medicine and rigorous clinical trials. The company emphasizes collaboration and transparency in its operations, fostering partnerships within the scientific community to drive innovation and enhance healthcare solutions globally.

Locations

Sofia, , Bulgaria

Chicago, Illinois, United States

Vancouver, British Columbia, Canada

Boston, Massachusetts, United States

Rio De Janeiro, , Brazil

Le Kremlin Bicetre, , France

Marseille Cedex, , France

Lisbon, , Portugal

Porto, , Portugal

Barcelona, , Spain

Palma De Mallorca, , Spain

Umeå, , Sweden

La Mesa, California, United States

Baltimore, Maryland, United States

Detroit, Michigan, United States

Rochester, Minnesota, United States

Saint Louis, Missouri, United States

New York, New York, United States

Buenos Aires, , Argentina

Westmead, , Australia

Nicosia, , Cyprus

Creteil, , France

Heidelberg, , Germany

Muenster, , Germany

Pavia, , Italy

Rome, , Italy

Sicily, , Italy

Kumamoto, , Japan

Kuala Lumpur, , Malaysia

Groningen, , Netherlands

Huelva, , Spain

Madrid, , Spain

Istanbul, , Turkey

Seoul, , Korea, Republic Of

London, , United Kingdom

Aurora, Colorado, United States

Jacksonville, Florida, United States

Joplin, Missouri, United States

Cooperstown, New York, United States

Columbus, Ohio, United States

São Paulo, , Brazil

Fort De France, Martinique, France

Saint Pierre, Reunion Island, France

Lille, , France

Cologne, , Germany

Ehime, , Japan

Fukuoka, , Japan

Hiroshima, , Japan

Nagano, , Japan

Okawasuji, , Japan

Ono, , Japan

ōita, , Japan

Tlalpan, , Mexico

Taipei, , Taiwan

Patients applied

0 patients applied

Trial Officials

Medical Director

Study Director

Alnylam Pharmaceuticals

Timeline

First submit

Trial launched

Trial updated

Estimated completion

Not reported

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