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Using Biomarkers to Help Guide Safe Immunotherapy Discontinuation in Patients With Unresectable Stage IIIB-IV Melanoma, The PET-Stop Trial

Launched by ECOG-ACRIN CANCER RESEARCH GROUP · Jul 6, 2020

Trial Information

Current as of June 26, 2025

Recruiting

Keywords

ClinConnect Summary

The PET-Stop Trial is a study looking at how doctors can use special tests called biomarkers from PET/CT scans to decide if patients with advanced melanoma can safely stop their anti-PD-1 treatment earlier. Anti-PD-1 therapy is a common treatment for melanoma that cannot be surgically removed. The goal of this trial is to see if these biomarkers can help identify patients who are responding well to treatment and might not need to continue for the full duration.

To be part of this trial, patients should have advanced melanoma that cannot be removed by surgery and must have been receiving anti-PD-1 therapy for about a year. They need to show positive results from their scans and meet other health criteria, such as having a certain level of blood cells. During the trial, participants will undergo scans and possibly biopsies to assess their condition. This study aims to improve treatment strategies for patients with melanoma, making it safer and more effective.

Gender

ALL

Eligibility criteria

  • Inclusion Criteria:
  • STEP 0 PRE-REGISTRATION INCLUSION CRITERIA
  • Patient must have active advanced melanoma, defined as unresectable stage IIIB-IV by American Joint Committee on Cancer (AJCC) 8th edition
  • Patient must have melanoma originating from cutaneous, acral-lentiginous, or mucosal primary sites. Patients with melanoma of unknown primary site are eligible. Patients must not have melanoma from an ocular primary site
  • Patient must have had measurable disease by immune related Response Evaluation Criteria in Solid Tumors (imRECIST) prior to start of initial anti-PD-1 therapy
  • * Patient must be actively receiving standard of care anti-PD-1 therapy, currently be 52 weeks (+/- 2 weeks) from start of anti-PD-1 therapy, and have not experienced a toxicity that prevents them from continuing on therapy. Permitted systemic anti-PD-1 therapy regimens include:
  • Nivolumab 240 mg IV every (Q)2weeks or 480 mg IV Q4weeks
  • Pembrolizumab 200 mg IV Q3weeks or 400 mg IV Q6weeks
  • Nivolumab 1 mg/kg plus ipilimumab 3 mg/kg IV Q3weeks induction x 4 doses, followed by nivolumab 240 mg IV Q2weeks or 480 mg IV Q4weeks maintenance
  • Nivolumab 3 mg/kg plus Ipilimumab 1 mg/kg IV Q3weeks induction x 4 doses, followed by nivolumab 240 mg IV Q2weeks or 480 mg IV Q4weeks maintenance
  • Pembrolizumab 2 mg/kg (or 200 mg flat dose) plus Ipilimumab 1 mg/kg IV Q3weeks induction x 4 doses, followed by pembrolizumab 200 mg IV Q3weeks or 400 mg IV Q6weeks maintenance
  • Patient must have an Eastern Cooperative Oncology Group (ECOG) performance status of 0-2
  • Human immunodeficiency virus (HIV)-infected patients on effective anti-retroviral therapy with undetectable viral load within 6 months are eligible for this trial. Patients with detectable viral loads are excluded as it is unclear if these patients have a low risk of melanoma progression off anti-PD-1 treatment
  • For patients with evidence of chronic hepatitis B virus (HBV) infection, the HBV viral load must be undetectable on suppressive therapy, if indicated
  • Patients with a history of hepatitis C virus (HCV) infection must have been treated and cured. For patients with HCV infection who are currently on treatment, they are eligible if they have an undetectable HCV viral load
  • Patients with a prior or concurrent malignancy whose natural history or treatment does not have the potential to interfere with the safety or efficacy assessment of the investigational regimen are eligible for this trial
  • Patients with known history or current symptoms of cardiac disease, or history of treatment with cardiotoxic agents, should have a clinical risk assessment of cardiac function using the New York Heart Association Functional Classification. To be eligible for this trial, patients should be class 2B or better
  • Patient must have experienced complete response, partial response, or stable disease on restaging CT scans by imRECIST that is maintained on restaging scans obtained at week 52 (+/- 2 weeks) from start of initial anti-PD-1 therapy
  • Patient must have completed an FDG-PET/CT scan at week 52 (+/- 2 weeks) from start of initial anti-PD-1 therapy
  • * Patients with PET/CT positive for hypermetabolic lesions: If a core needle, punch or excisional biopsy and pathological review of a representative lesion was not performed prior to pre-registration (Step 0) must either:
  • Be amenable to undergo a biopsy. Patient must not be on anticoagulation therapy or, if on anti-coagulation therapy, patient must be able to hold treatment for a biopsy procedure (core needle, punch or excisional biopsy). Anti-coagulation therapy is defined as low molecular weight heparin, warfarin, factor Xa inhibitor, or direct thrombin inhibitor
  • Have documentation of inability to perform the biopsy due to feasibility or safety concerns
  • Leukocytes \>= 3,000/mcL (obtained =\< 4 weeks prior to protocol registration)
  • Absolute neutrophil count \>= 1,500/mcL (obtained =\< 4 weeks prior to protocol registration)
  • Platelets \>= 100,000/mcL (obtained =\< 4 weeks prior to protocol registration)
  • Total bilirubin =\< institutional upper limit of normal (ULN) (patients with history of Gilbert's syndrome are permitted to have a total bilirubin \> 1.5 x institutional ULN) (obtained =\< 4 weeks prior to protocol registration)
  • Aspartate aminotransferase (AST) (serum glutamic-oxaloacetic transaminase \[SGOT\])/alanine aminotransferase (ALT) (serum glutamate pyruvate transaminase \[SGPT\]) =\< 2.5 x institutional ULN (obtained =\< 4 weeks prior to protocol registration)
  • Creatinine =\< 1.5 x institutional ULN (obtained =\< 4 weeks prior to protocol registration)
  • STEP 1 REGISTRATION INCLUSION CRITERIA
  • Patient met all eligibility criteria outlined above
  • Patient must register to Step 1 within 4 weeks of registration to Step 0
  • * Patients must meet one of the following criteria:
  • Patient had no positive hypermetabolic lesions on the week 52 FDG-PET/CT.
  • * Patients with positive hypermetabolic lesion(s) on the week 52 FDG-PET/CT (positive hypermetabolic = standard uptake volume \[SUV\] \> pooled mediastinal blood), one of the following must have occurred:
  • A representative lesion was biopsied (core needle, punch or excisional biopsy) within 14 days of registration to Step 0 and subsequent pathology review performed to determine the presence or absence of viable tumor
  • Documentation is present that the patient is not able to undergo biopsy of a hypermetabolic lesion due to feasibility or safety concerns, i.e., the lesion location that is not amenable to biopsy
  • Exclusion Criteria:
  • STEP 0 PRE-REGISTRATION EXCLUSION CRITERIA
  • Patient must not be receiving concurrent anti-tumor therapies in addition to the standard of care anti-PD-1 regimens. Patients who are receiving bisphosphonates and RANKL inhibitors for management of bone metastases are eligible
  • Patient must not have brain metastases
  • Women must not be pregnant or breast-feeding due to potential harm to an unborn fetus and possible risk for adverse events in nursing infants with the anti-PD-1 regimens being used. All females of childbearing potential must have a blood test or urine study within 14 days prior to registration to rule out pregnancy. A female of childbearing potential is defined as any woman, regardless of sexual orientation or whether they have undergone tubal ligation, who meets the following criteria: 1) has achieved menarche at some point, 2) has not undergone a hysterectomy or bilateral oophorectomy; or 3) has not been naturally postmenopausal (amenorrhea following cancer therapy does not rule out childbearing potential) for at least 24 consecutive months (i.e., has had menses at any time in the preceding 24 consecutive months)
  • Women of childbearing potential and sexually active males must not conceive or father children by using accepted and effective method(s) of contraception or by abstaining from sexual intercourse from the time of study registration and continuing until at least 5 months after the last dose of anti-PD-1 treatment for female patients and for at least 7 months after the last dose of anti-PD-1 treatment for male patients who are sexually active with a women of childbearing potential (WOCBP)

About Ecog Acrin Cancer Research Group

The ECOG-ACRIN Cancer Research Group is a prominent clinical trial sponsor dedicated to advancing cancer research through innovative clinical trials and rigorous scientific inquiry. As a collaborative network of researchers, healthcare professionals, and institutions, ECOG-ACRIN focuses on improving cancer treatment and patient outcomes by conducting high-quality, multicenter studies. Their research spans various cancer types and includes a wide array of therapeutic approaches, emphasizing the integration of cutting-edge methodologies and patient-centered care. Committed to fostering collaboration and sharing knowledge, ECOG-ACRIN plays a vital role in transforming cancer care and enhancing the understanding of cancer biology.

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Muskegon, Michigan, United States

Troy, Ohio, United States

Nampa, Idaho, United States

Grove City, Ohio, United States

Pontiac, Michigan, United States

Ann Arbor, Michigan, United States

Brighton, Michigan, United States

Canton, Michigan, United States

Chelsea, Michigan, United States

Centralia, Illinois, United States

Paducah, Kentucky, United States

Danville, Illinois, United States

New Albany, Ohio, United States

Greenville, Ohio, United States

Boone, Iowa, United States

Fort Dodge, Iowa, United States

Jefferson, Iowa, United States

Marshalltown, Iowa, United States

Ames, Iowa, United States

Merced, California, United States

Ladysmith, Wisconsin, United States

Osage Beach, Missouri, United States

Ankeny, Iowa, United States

Sunset Hills, Missouri, United States

Marysville, Ohio, United States

Niles, Michigan, United States

Reed City, Michigan, United States

Saint Joseph, Michigan, United States

O'fallon, Illinois, United States

Des Moines, Iowa, United States

Clive, Iowa, United States

Lansing, Michigan, United States

Carmichael, California, United States

Grand Rapids, Michigan, United States

Saint Joseph, Michigan, United States

Jefferson City, Missouri, United States

Pontiac, Michigan, United States

Wilmington, Ohio, United States

Silverdale, Washington, United States

Dayton, Ohio, United States

Dayton, Ohio, United States

Grand Rapids, Michigan, United States

Sandpoint, Idaho, United States

Baker City, Oregon, United States

Ontario, Oregon, United States

Walnut Creek, California, United States

Patients applied

0 patients applied

Trial Officials

Geoffrey T Gibney

Principal Investigator

ECOG-ACRIN Cancer Research Group

Timeline

First submit

Trial launched

Trial updated

Estimated completion

Not reported

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