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Search / Trial NCT05812807

Pembrolizumab vs. Observation in People With Triple-negative Breast Cancer Who Had a Pathologic Complete Response After Chemotherapy Plus Pembrolizumab

Launched by ALLIANCE FOR CLINICAL TRIALS IN ONCOLOGY · Apr 12, 2023

Trial Information

Current as of June 27, 2025

Recruiting

Keywords

ClinConnect Summary

This clinical trial is studying whether the immunotherapy drug pembrolizumab is more effective than simply observing patients after surgery for early-stage triple-negative breast cancer. The trial focuses on patients who have had a complete response to chemotherapy and pembrolizumab before surgery, meaning no signs of cancer were found after treatment. Researchers want to see if using pembrolizumab after surgery can lower the chance of cancer returning compared to just keeping an eye on the patients.

To be eligible for this trial, participants must be at least 18 years old and diagnosed with early-stage triple-negative breast cancer. They should have completed their chemotherapy and surgery with no remaining invasive cancer in their breast or lymph nodes. Participants can expect to be randomly assigned to receive either pembrolizumab or just regular follow-up care. It's important to know that those who have had severe reactions to pembrolizumab in the past or have certain medical conditions may not qualify for the study. Overall, this trial aims to find out the best way to help prevent cancer from coming back after initial treatment.

Gender

ALL

Eligibility criteria

  • Inclusion Criteria:
  • Age \>= 18 years
  • Eastern Cooperative Oncology Group (ECOG) Performance Status 0-2
  • * Triple Negative Breast Cancer:
  • Patients with a history of stage T1cN1-2 or T2-4N0-2 breast cancer according to the primary tumor-regional lymph node anatomic staging criteria of the American Joint Committee on Cancer (AJCC), 8th edition as determined by the investigator in radiologic assessment, clinical assessment or both
  • Patients must have no residual invasive disease in the breast or lymph nodes after the completion of neoadjuvant therapy. Residual ductal carcinoma in situ (DCIS) is allowed. Isolated tumor cells are considered node-negative
  • Estrogen (ER) and progesterone (PR) =\< 10%; HER2-negative by American Society of Clinical Oncology (ASCO)/College of American Pathologists (CAP) guidelines (immunohistochemistry \[IHC\] and fluorescence in situ hybridization \[FISH\])
  • If invasive disease was present in both breasts, participation in the study is permitted as long as the eligibility criteria are met for both tumors/breasts
  • Patients must have received neoadjuvant chemotherapy in combination with pembrolizumab for a minimum of 6 cycles. All systemic chemotherapy and ICI therapy should have been completed preoperatively
  • An interval of no more than 12 weeks between the completion date of the final surgery and the date of randomization
  • \* Note: Adjuvant radiation can be given on study. If given, it is encouraged to be given concurrently with pembrolizumab, per investigator discretion. Treatment with adjuvant pembrolizumab is strongly discouraged prior to participation in this trial, but if administered (e.g., if patients are awaiting pathology results), pembrolizumab may be administered for up to 6 weeks post-surgery and must be completed prior to registration
  • Use of investigational anti-cancer agents must be discontinued at time of registration
  • * Adequate excision: Surgical removal of all clinically evident disease in the breast and lymph nodes as follows:
  • Breast surgery: Total mastectomy or breast-conserving surgery with histologically negative margins, including no ink on tumor for DCIS, at the time of excision
  • \*\* For patients who undergo breast-conserving surgery, the margins of the resected specimen must be histologically free of ductal carcinoma in-situ (DCIS) as determined by the local pathologist. If pathologic examination demonstrates DCIS at the line of resection, additional operative procedures may be performed to obtain clear margins. If DCIS is still present at the resected margin after re-excision(s), the patient must undergo total mastectomy to be eligible. Patients with margins positive for classic lobular carcinoma in situ (LCIS) are eligible without additional resection
  • * Lymph node surgery:
  • For a patient with clinically N0 disease, a sentinel lymph node biopsy should have been performed at time of surgical evaluation, and if pathologically node positive, the patient is no longer eligible. Isolated tumor cells are considered node-negative
  • For a patient with clinically N1 disease at diagnosis (with positive results from a fine-needle aspiration, core biopsy, or sentinel node biopsy performed prior to preoperative therapy) additional surgical evaluation of the axilla following preoperative therapy is required
  • \*\*\* If they become cN0 (no palpable adenopathy), then a sentinel lymph node biopsy could have been performed at time of surgery (axillary dissection would also be permitted); if the sentinel lymph node biopsy is positive, the patient is no longer eligible
  • If sentinel node biopsy performed before preoperative therapy was negative, no additional surgical evaluation of the axilla is required after preoperative therapy. If sentinel node biopsy performed before preoperative therapy was positive, an ALND is required after preoperative therapy
  • If the only sentinel node identified by isotope scan is in the internal mammary chain, surgical evaluation of the axilla is still required
  • If sentinel node evaluation after preoperative therapy is negative, no further additional surgical evaluation of the axilla is required
  • Axillary dissection without sentinel node evaluation is permitted as the initial or sole axillary evaluation after preoperative therapy
  • If breast-conserving surgery was performed but patient will not be receiving breast radiation, the patient is not eligible
  • Not pregnant and not nursing, because this study involves an agent whose genotoxic, mutagenic and teratogenic effects on the developing fetus and newborn are unknown. Therefore, for women of childbearing potential only, a negative serum or urine pregnancy test done =\< 7 days prior to randomization is required
  • Absolute neutrophil count (ANC) \>= 1,000/mm\^3
  • Platelet Count \>= 100,000/mm\^3
  • Estimated glomerular filtration rate (eGFR) \>= 15 mL/min/1.73m\^2
  • Total Bilirubin =\<1.5 x upper limit of normal (ULN)
  • \* Patients with Gilbert's disease with a total bilirubin =\< 2.5 x ULN and direct bilirubin within normal limits are permitted
  • Aspartate aminotransferase (AST) serum aspartate aminotransferase \[SGOT\] / alanine aminotransferase (ALT) serum glutamic pyruvic transaminase \[SGPT\] =\< 3 x institutional ULN
  • Patients must be willing to provide tumor tissue from the diagnostic core biopsy. If inadequate tumor tissue is available, patients are still eligible to participate in the trial
  • Patients with a prior or concurrent malignancy whose natural history or treatment does not have the potential to interfere with the safety or efficacy assessment of the investigational regimen are eligible for this trial
  • Patients with known history or current symptoms of cardiac disease, or history of treatment with cardiotoxic agents, should have a clinical risk assessment of cardiac function using the New York Heart Association Functional Classification. To be eligible for this trial, patients should be class 2B or better
  • Human immunodeficiency virus (HIV)-infected patients on effective anti-retroviral therapy with undetectable viral load within 6 months prior to registration are eligible for this trial
  • Exclusion Criteria:
  • No stage IV (metastatic) breast cancer
  • No history of any prior (ipsi- or contralateral) invasive breast cancer. Prior DCIS is allowed
  • No evidence of recurrent disease following preoperative therapy and surgery
  • No known active liver disease, e.g. due to hepatitis B virus (HBV), hepatitis C virus (HCV), autoimmune hepatic disorders, or sclerosing cholangitis
  • No history of intolerance, including Grade 3 or 4 infusion reaction or hypersensitivity to pembrolizumab or murine proteins or any components of the product
  • \* Note: Prior immune-related adverse events (irAEs) are allowed if they resolved and the patient tolerated subsequent therapy without requiring chronic steroids for the irAE
  • No medical conditions that require chronic systemic steroids (\>10 mg prednisone daily or equivalent) or any other form of immunosuppressive medications and has required such therapy in the last two years. Replacement therapy (e.g. thyroxine, insulin, or physiologic corticosteroid replacement therapy for adrenal or pituitary insufficiency, etc.) is not considered a form of systemic therapy
  • Patients who are unable or unwilling to comply with the requirements of the protocol per investigator assessment are not eligible

About Alliance For Clinical Trials In Oncology

The Alliance for Clinical Trials in Oncology is a prominent cooperative group dedicated to conducting high-quality, innovative clinical research aimed at improving cancer treatment and patient outcomes. Comprising a diverse network of institutions and investigators, the Alliance focuses on developing and implementing clinical trials that evaluate new therapies, treatment combinations, and prevention strategies across various cancer types. By fostering collaboration among oncologists, researchers, and healthcare professionals, the Alliance aims to accelerate the translation of scientific discoveries into effective clinical practices, ultimately enhancing the standard of care for cancer patients.

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Stamford, Connecticut, United States

'Ewa Beach, Hawaii, United States

Barrington, Illinois, United States

Crystal Lake, Illinois, United States

Crown Point, Indiana, United States

Dyer, Indiana, United States

Hobart, Indiana, United States

Hobart, Indiana, United States

Indianapolis, Indiana, United States

Munster, Indiana, United States

New Albany, Indiana, United States

Valparaiso, Indiana, United States

Council Bluffs, Iowa, United States

Kalamazoo, Michigan, United States

Omaha, Nebraska, United States

Omaha, Nebraska, United States

Sleepy Hollow, New York, United States

Greensboro, North Carolina, United States

Dublin, Ohio, United States

Chambersburg, Pennsylvania, United States

Baytown, Texas, United States

Houston, Texas, United States

Nassau Bay, Texas, United States

Richardson, Texas, United States

The Woodlands, Texas, United States

Goodyear, Arizona, United States

Frederick, Maryland, United States

Paramus, New Jersey, United States

Glastonbury, Connecticut, United States

Neenah, Wisconsin, United States

New London, Wisconsin, United States

Shawano, Wisconsin, United States

Waupaca, Wisconsin, United States

Ocoee, Florida, United States

New York, New York, United States

Westerly, Rhode Island, United States

Vancouver, Washington, United States

Highlands Ranch, Colorado, United States

Raleigh, North Carolina, United States

Missoula, Montana, United States

Torrance, California, United States

Lone Tree, Colorado, United States

Greenlawn, New York, United States

Oshkosh, Wisconsin, United States

Pierre, South Dakota, United States

Annapolis, Maryland, United States

Cary, North Carolina, United States

Brooklyn, New York, United States

Baton Rouge, Louisiana, United States

'Aiea, Hawaii, United States

Nampa, Idaho, United States

Springfield, Illinois, United States

Asheboro, North Carolina, United States

Perrysburg, Ohio, United States

Santa Monica, California, United States

Denver, Colorado, United States

Aurora, Colorado, United States

Sheboygan, Wisconsin, United States

Meadville, Pennsylvania, United States

Safety Harbor, Florida, United States

Fort Worth, Texas, United States

Berlin, Wisconsin, United States

Mineola, New York, United States

Raleigh, North Carolina, United States

Kansas City, Missouri, United States

Seattle, Washington, United States

Bellevue, Washington, United States

Des Moines, Iowa, United States

Kalispell, Montana, United States

Dallas, Texas, United States

Lebanon, New Hampshire, United States

Cameron Park, California, United States

Wyoming, Michigan, United States

Grand Rapids, Michigan, United States

Muskegon, Michigan, United States

Nampa, Idaho, United States

Grove City, Ohio, United States

Pontiac, Michigan, United States

Ann Arbor, Michigan, United States

Brighton, Michigan, United States

Chelsea, Michigan, United States

Foxboro, Massachusetts, United States

Dayton, Ohio, United States

Webster, New York, United States

San Juan, , Puerto Rico

Danville, Illinois, United States

Guilford, Connecticut, United States

Orland Park, Illinois, United States

Greenville, Ohio, United States

Decatur, Georgia, United States

Canton, Michigan, United States

Rhinelander, Wisconsin, United States

Stevens Point, Wisconsin, United States

Minocqua, Wisconsin, United States

Columbia, Missouri, United States

Asheboro, North Carolina, United States

Glenview, Illinois, United States

Grayslake, Illinois, United States

Ankeny, Iowa, United States

Sunset Hills, Missouri, United States

Marysville, Ohio, United States

Niles, Michigan, United States

Reed City, Michigan, United States

Saint Joseph, Michigan, United States

Des Moines, Iowa, United States

Clive, Iowa, United States

Woodbridge, Virginia, United States

Lansing, Michigan, United States

Carmichael, California, United States

Grand Rapids, Michigan, United States

Rockford, Illinois, United States

Hays, Kansas, United States

Saint Joseph, Michigan, United States

Jefferson City, Missouri, United States

Council Bluffs, Iowa, United States

Madison, Wisconsin, United States

Lynchburg, Virginia, United States

Ridgewood, New Jersey, United States

Washington, North Carolina, United States

Kirkland, Washington, United States

Dayton, Ohio, United States

Dayton, Ohio, United States

Johnson Creek, Wisconsin, United States

Sandpoint, Idaho, United States

Ontario, Oregon, United States

Irvine, California, United States

Lexington, Kentucky, United States

Hastings, Nebraska, United States

Millville, Delaware, United States

Saginaw, Michigan, United States

Tawas City, Michigan, United States

Crown Point, Indiana, United States

Athens, Ohio, United States

Pickerington, Ohio, United States

Westerville, Ohio, United States

Camillus, New York, United States

Southfield, Michigan, United States

Novi, Michigan, United States

Madison, Wisconsin, United States

Detroit, Michigan, United States

Grosse Pointe Woods, Michigan, United States

Grosse Pointe Woods, Michigan, United States

Macomb, Michigan, United States

Warren, Michigan, United States

Flint, Michigan, United States

Warren, Michigan, United States

East China Township, Michigan, United States

Macomb, Michigan, United States

Warren, Michigan, United States

Olathe, Kansas, United States

Grosse Pointe Woods, Michigan, United States

Mount Vernon, Illinois, United States

Ankeny, Iowa, United States

Clive, Iowa, United States

Des Moines, Iowa, United States

Des Moines, Iowa, United States

Denver, Colorado, United States

Asheboro, North Carolina, United States

Littleton, Colorado, United States

Parker, Colorado, United States

Cherry Hill, New Jersey, United States

Kearney, Nebraska, United States

Patients applied

0 patients applied

Timeline

First submit

Trial launched

Trial updated

Estimated completion

Not reported

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