ClinConnect ClinConnect Logo
Search / Trial NCT06254482

An Extension Study to Evaluate the Long-Term Safety and Efficacy of PTC518 in Participants With Huntington's Disease (HD)

Launched by PTC THERAPEUTICS · Feb 2, 2024

Trial Information

Current as of June 26, 2025

Enrolling by invitation

Keywords

Neurodegenerative Disorder Rare Disease

ClinConnect Summary

Participants who completed the Treatment Period in the parent Phase 2a Study PTC518-CNS-002-HD (NCT05358717), fulfilled the enrollment criteria, and chose to enroll in this extension study will undergo baseline evaluations and be assessed for 30 additional months.

All participants will receive active PTC518 in this extension study. Participants who received PTC518 in the parent Study PTC518-CNS-002-HD will continue at the same dose level they received in that study in a blinded fashion (5, 10, or 20 milligrams \[mg\]). Participants who received placebo in the parent Study PTC518-CNS-002-HD...

Gender

ALL

Eligibility criteria

  • Inclusion Criteria:
  • Participant who has completed the Treatment Period in Study PTC518-CNS-002-HD.
  • Exclusion Criteria:
  • Participants who have not previously completed the Treatment Period in Study PTC518-CNS-002-HD.
  • Note: Other inclusion and exclusion criteria may apply.

About Ptc Therapeutics

PTC Therapeutics is a biotechnology company dedicated to the discovery and development of innovative medicines for the treatment of rare diseases and cancer. With a strong focus on advancing its proprietary drug development pipeline, PTC Therapeutics employs cutting-edge science and technology to address unmet medical needs. The company collaborates with a network of academic institutions, patient advocacy groups, and industry partners to drive research initiatives and clinical trials aimed at improving patient outcomes. Committed to patient-centered care, PTC Therapeutics strives to bring transformative therapies to market that enhance the quality of life for individuals affected by challenging health conditions.

Locations

Innsbruck, , Austria

Leiden, , Netherlands

Madrid, , Spain

Cardiff, , United Kingdom

Barcelona, , Spain

Berlin, , Germany

Manchester, , United Kingdom

Westmead, , Australia

Angers, , France

Münster, , Germany

Barakaldo, , Spain

Clayton, , Australia

Bologna, , Italy

Barcelona, Cataluña, Spain

Marseille, , France

Paris, , France

Bochum, , Germany

Ulm, , Germany

London, , United Kingdom

Montreal, , Canada

Ottawa, , Canada

Vancouver, , Canada

Milan, , Italy

San Giovanni Rotondo, , Italy

Christchurch, , New Zealand

Burgos, , Spain

Birmingham, , United Kingdom

Patients applied

0 patients applied

Timeline

First submit

Trial launched

Trial updated

Estimated completion

Not reported