Decentralized Trials for Rare Diagnoses: 2025 Readiness Report
A 2025 readiness report for decentralized trials with rare diagnoses: five practical steps — from participant-first protocols and trainee-led outreach to back-to-school planning, flu season care, and faster compassionate access.
Robert Maxwell
Sep 18, 2025
gene therapy trials
compassionate use access
ultra-rare disorders
decentralized rare trials