Orphan Drug Trial Shifts: How to Find Trials, Access & Telehealth
A mother's search for treatment led to a trial that balanced home life and research. Learn how to find rare disease trials, what to expect in orphan drug trials, and how decentralized trials and telehealth can change access and costs.
Robert Maxwell
Sep 19, 2025
gene therapy trials
orphan drug access
Inherited metabolic disorders
Rare pediatric conditions
