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Search / Trial NCT03358147

Efficacy and Safety of PT001 to Placebo and Open-label Spiriva® Respimat® in Subjects With Persistant Asthma

Launched by PEARL THERAPEUTICS, INC. · Nov 29, 2017

Trial Information

Current as of May 19, 2025

Completed

Keywords

ClinConnect Summary

A Randomized, Double-Blind, Parallel Group, Multi-Center 24-Week Study Comparing the Efficacy and Safety of Three Doses of PT001 to Placebo and Open-label Spiriva® Respimat® in Subjects With Persistent Asthma

Gender

ALL

Eligibility criteria

  • Inclusion Criteria:
  • Have a documented history of physician-diagnosed asthma
  • Require inhaled asthma maintenance therapy: has been regularly using an ICS/LABA on a stable regimen for at least 4 weeks
  • Documented reversibility to albuterol
  • A pre-bronchodilator FEV1 \>40% and \<85% of predicted normal value for subjects 18 to 80 years of age or \>40% and \<90% of predicted for subjects 12 to \<18 years of age
  • Demonstrate acceptable spirometry performance
  • Willing and, in the opinion of the Investigator, able to adjust current asthma therapy, as required by the protocol
  • Compliance: must be willing to remain at the study center as required per protocol to complete all visit assessments
  • Exclusion Criteria:
  • Oral corticosteroid use (any dose) within 4 weeks
  • Current smokers, former smokers with \>10 pack-years history, or former smokers who stopped smoking \<6 months (including all forms of tobacco, e-cigarettes, and marijuana)
  • Life-threatening asthma as defined as a history of significant asthma episode(s) requiring intubation associated with hypercapnia, respiratory arrest, hypoxic seizures, or asthma-related syncopal episode(s)
  • Completed treatment for lower respiratory infection or asthma exacerbation within 4 weeks
  • Hospitalizations for asthma within 3 months
  • Historical or current evidence of a clinically significant disease
  • Cancer not in complete remission for at least 5 years
  • Treatment with investigational study drug (or device) in another clinical study within the last 30 days or 5 half-lives, whichever is longer
  • Previously randomized in any PT001 study

About Pearl Therapeutics, Inc.

Pearl Therapeutics, Inc. is a biopharmaceutical company focused on the development of innovative therapeutic solutions for respiratory diseases. Leveraging advanced drug delivery technologies, Pearl Therapeutics aims to enhance patient outcomes through the formulation of novel inhalation therapies. The company is committed to addressing unmet medical needs in the treatment of conditions such as chronic obstructive pulmonary disease (COPD) and asthma, with a robust pipeline of clinical programs designed to optimize efficacy and patient adherence. With a strong emphasis on scientific excellence and collaboration, Pearl Therapeutics is dedicated to advancing healthcare through the discovery and development of next-generation respiratory therapeutics.

Locations

Raleigh, North Carolina, United States

Smyrna, Tennessee, United States

Tulsa, Oklahoma, United States

Greenville, South Carolina, United States

Poway, California, United States

Kissimmee, Florida, United States

Wooster, Ohio, United States

Saint Louis, Missouri, United States

Medford, Oregon, United States

Tacoma, Washington, United States

Little Rock, Arkansas, United States

Mission Viejo, California, United States

Wheat Ridge, Colorado, United States

Jasper, Alabama, United States

Huntington Beach, California, United States

Stockton, California, United States

Tampa, Florida, United States

Ann Arbor, Michigan, United States

Minneapolis, Minnesota, United States

Albuquerque, New Mexico, United States

Charlotte, North Carolina, United States

Dallas, Texas, United States

Birmingham, Alabama, United States

Encinitas, California, United States

Colorado Springs, Colorado, United States

Cincinnati, Ohio, United States

Ocoee, Florida, United States

New York, New York, United States

Corona, California, United States

Fullerton, California, United States

Omaha, Nebraska, United States

Elizabeth City, North Carolina, United States

Waco, Texas, United States

South Burlington, Vermont, United States

Abingdon, Virginia, United States

Fargo, North Dakota, United States

Orange, California, United States

Anaheim, California, United States

Los Angeles, California, United States

North Dartmouth, Massachusetts, United States

Burlington, North Carolina, United States

Gastonia, North Carolina, United States

New Bern, North Carolina, United States

Winston Salem, North Carolina, United States

Wyomissing, Pennsylvania, United States

Anderson, South Carolina, United States

Bellingham, Washington, United States

Palmdale, California, United States

Savannah, Georgia, United States

Skillman, New Jersey, United States

Centennial, Colorado, United States

Aventura, Florida, United States

Ocala, Florida, United States

Tallahassee, Florida, United States

San Jose, California, United States

Greenfield, Wisconsin, United States

East Providence, Rhode Island, United States

Rancho Mirage, California, United States

Charleston, South Carolina, United States

Panama City, Florida, United States

Gaffney, South Carolina, United States

Johnson City, Tennessee, United States

San Antonio, Texas, United States

Morgantown, West Virginia, United States

Greensboro, North Carolina, United States

Murray, Utah, United States

Chandler, Arizona, United States

Winter Park, Florida, United States

Warwick, Rhode Island, United States

Franklin, Tennessee, United States

Tomball, Texas, United States

Michigan City, Indiana, United States

Sacramento, California, United States

Clearwater, Florida, United States

Hialeah, Florida, United States

Shreveport, Louisiana, United States

Amarillo, Texas, United States

Huntersville, North Carolina, United States

Mount Pleasant, South Carolina, United States

Austin, Texas, United States

Newport News, Virginia, United States

Phoenix, Arizona, United States

Chesterfield, Missouri, United States

Pembroke Pines, Florida, United States

Stockbridge, Georgia, United States

Chevy Chase, Maryland, United States

Miami, Florida, United States

Rock Hill, South Carolina, United States

Loxahatchee Groves, Florida, United States

Berlin, New Jersey, United States

Tucson, Arizona, United States

El Paso, Texas, United States

Scottsboro, Alabama, United States

Gainesville, Florida, United States

Evergreen Park, Illinois, United States

Flagstaff, Arizona, United States

Newport Beach, California, United States

Thousand Oaks, California, United States

Boise, Idaho, United States

Mooresville, North Carolina, United States

Kerrville, Texas, United States

Edina, Minnesota, United States

Woodbury, Minnesota, United States

Las Vegas, Nevada, United States

Tustin, California, United States

Bangor, Maine, United States

Oklahoma City, Oklahoma, United States

Spokane Valley, Washington, United States

Columbus, Georgia, United States

Rapid City, South Dakota, United States

Boerne, Texas, United States

Marion, Ohio, United States

Lawrenceville, Georgia, United States

North Hollywood, California, United States

Bakersfield, California, United States

Northridge, California, United States

Toms River, New Jersey, United States

Lufkin, Texas, United States

Fridley, Minnesota, United States

Plano, Texas, United States

Troy, Michigan, United States

Salt Lake City, Utah, United States

El Cajon, California, United States

Brandon, Florida, United States

Ocean City, New Jersey, United States

Rolling Hills Estates, California, United States

Dublin, Ohio, United States

Portland, Oregon, United States

San Diego, California, United States

Gold River, California, United States

Westminster, California, United States

Orlando, Florida, United States

Rincon, Georgia, United States

Meridian, Idaho, United States

O'fallon, Illinois, United States

Crowley, Louisiana, United States

Zachary, Louisiana, United States

Farmington Hills, Michigan, United States

Rochester, Michigan, United States

Saint Charles, Missouri, United States

Bellevue, Nebraska, United States

Monroe, North Carolina, United States

Dayton, Ohio, United States

Hodges, South Carolina, United States

Myrtle Beach, South Carolina, United States

Union, South Carolina, United States

Hendersonville, Tennessee, United States

Houston, Texas, United States

Richmond, Virginia, United States

Saint Cloud, Florida, United States

Lafayette, Colorado, United States

Fort Mitchell, Kentucky, United States

Tempe, Arizona, United States

Carrollton, Texas, United States

Riverside, California, United States

River Forest, Illinois, United States

White Marsh, Maryland, United States

Lampasas, Texas, United States

Fresno, California, United States

Brownsburg, Indiana, United States

Albany, Georgia, United States

Hickory, North Carolina, United States

Reno, Nevada, United States

Pearland, Texas, United States

Dothan, Alabama, United States

Quartz Hill, California, United States

Atlanta, Georgia, United States

Dacula, Georgia, United States

Norcross, Georgia, United States

Bronx, New York, United States

Edmond, Oklahoma, United States

Monroeville, Pennsylvania, United States

Pittsburgh, Pennsylvania, United States

Spartanburg, South Carolina, United States

Sherman, Texas, United States

Costa Mesa, California, United States

Lincoln, Nebraska, United States

Live Oak, Texas, United States

Hamden, Connecticut, United States

Lake City, Florida, United States

Clackamas, Oregon, United States

Fall River, Massachusetts, United States

Guntersville, Alabama, United States

Long Beach, California, United States

Adairsville, Georgia, United States

Columbia, Missouri, United States

Cortland, New York, United States

Watertown, New York, United States

Killeen, Texas, United States

Patients applied

0 patients applied

Timeline

First submit

Trial launched

Trial updated

Estimated completion

Not reported

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