Clinical Trials for Mucopolysaccharidosis III

Find clinical trials for mucopolysaccharidosis iii. Discover research opportunities and treatment options in your area.

3 Active Trials Found

Showing 3 trials on this page

Page 1 of 1

Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH

NCT ID: NCT02716246

This clinical trial is studying a new treatment called UX111 for children with MPS IIIA, also known as Sanfilippo Syndrome. This condition affects how the body breaks down certain sugars, which can...

Recruiting

Phase: PHASE2 Type: interventional Locations: North Adelaide, South Australia, Australia, Columbus, Ohio, United States +3 more

Study of Cannabidiol in Sanfilippo Syndrome

NCT ID: NCT06333041

This clinical trial is studying a medication called cannabidiol, also known as Epidiolex, to see if it is safe and helpful for children with Sanfilippo Syndrome, a rare genetic condition that affec...

Not yet recruiting

Phase: PHASE2 Type: interventional Locations: Torrance, California, United States

MPS (RaDiCo Cohort) (RaDiCo-MPS)

NCT ID: NCT06036693

The RaDiCo-MPS trial is an observational study aimed at understanding the different types of Mucopolysaccharidosis (MPS) diseases, which are genetic disorders that affect how the body breaks down c...

Recruiting

Type: observational Locations: Rennes, , France, Rouen, , France +21 more

Related Conditions

Breast Cancer View clinical trials → Stroke View clinical trials → Obesity View clinical trials → Cancer View clinical trials → Healthy View clinical trials → Prostate Cancer View clinical trials →

Search All Trials Browse All Conditions