Clinical Trials for Myotonic Dystrophy Type 1 (DM1)

Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-101 in Participants With Myotonic Dystrophy Type 1

NCT ID: NCT05481879

This clinical trial is investigating a new treatment called DYNE-101 for people with Myotonic Dystrophy Type 1 (DM1), a genetic condition that affects muscle function. The main goal of the study is...

A Study of Long-term Safety and Efficacy of VX-670 in Participants With Myotonic Dystrophy Type I

NCT ID: NCT06926621

This clinical trial is studying a new treatment called VX-670 for people with Myotonic Dystrophy Type I (DM1), a condition that affects muscle function. The main goals of the study are to find out ...

A Registered Observational Cohort Study of Myotonic Dystrophy Type 1

NCT ID: NCT06979024

Personalized Training for People With Rare Neuromuscular Disorders

NCT ID: NCT06708468

This clinical trial is looking at how personalized exercise programs can help improve balance and physical function in adults with certain rare neuromuscular disorders, such as Charcot-Marie-Tooth ...

A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1)

NCT ID: NCT06185764

This clinical trial is studying a new medication called VX-670 to see how safe it is and how well it works for adults with Myotonic Dystrophy Type 1 (DM1). DM1 is a genetic condition that affects m...

Music Intervention for Brain-Heart Disease in Myotonic Dystrophy Type 1 (DM1)

NCT ID: NCT06809049

This clinical trial, called the "Music Intervention for Brain-Heart Disease in Myotonic Dystrophy Type 1," is exploring whether music education can help children with a condition called myotonic dy...