Clinical Trials for Duchenne Muscular Dystrophy

Psychoeducation Program for Parents of Children with Duchenne Muscular Dystrophy

NCT ID: NCT06412328

Trial of Cell Based Therapy for DMD

NCT ID: NCT06692426

This clinical trial is studying a new treatment for Duchenne Muscular Dystrophy (DMD), a condition that causes muscle weakness and loss over time. The researchers want to see if injecting special m...

Investigation of the Relationship Between Executive Functions and Occupational Performance of Children with Duchenne Muscular Dystrophy

NCT ID: NCT06868784

Gamified Occupational Therapy for Adolescents with Duchenne Muscular Dystrophy

NCT ID: NCT06402942

This clinical trial is studying a new type of occupational therapy for young boys with Duchenne muscular dystrophy, a condition that affects muscle strength and movement. The researchers want to se...

A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) Following Imlifidase Infusion in Participants With Duchenne Muscular Dystrophy (DMD) Determined to Have Pre-existing Antibodies to Recombinant Adeno-Associated Virus Serotype (rAAVrh74)

NCT ID: NCT06241950

A Gene Transfer Therapy to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) Following Therapeutic Plasma Exchange (Plasmapheresis) in Participants With Duchenne Muscular Dystrophy (DMD) and Pre-existing Antibodies to AAVrh74

NCT ID: NCT06597656

This clinical trial is testing a new gene therapy called delandistrogene moxeparvovec (also known as SRP-9001) for boys with Duchenne Muscular Dystrophy (DMD), a serious condition that affects musc...

Estimation of Non-Reimbursable Costs for Patients With Duchenne Muscular Dystrophy in France

NCT ID: NCT06861270

This clinical trial, called CouDuMyo, is looking into the costs that families face when caring for someone with Duchenne Muscular Dystrophy (DMD) in France. DMD is a serious condition that primaril...

Once Weekly Infant Corticosteroid Trial for DMD

NCT ID: NCT05412394

The Once Weekly Infant Corticosteroid Trial for Duchenne Muscular Dystrophy (DMD) is a study that aims to find out if a lower dose of oral corticosteroids (5 mg/kg per week) is just as effective as...

The Duchenne Registry

NCT ID: NCT02069756

The Duchenne Registry is an online program designed to support individuals with Duchenne and Becker muscular dystrophy, as well as their families. The main goal of the Registry is to connect patien...

Pharmacokinetics and Safety of Givinostat in DMD Patients Ages From at Least 2 Years to Less Then 6 Years Old

NCT ID: NCT06769633

This clinical trial is studying a medication called Givinostat to see how it works and whether it is safe for young boys with Duchenne Muscular Dystrophy (DMD), a condition that affects muscle stre...

A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study

NCT ID: NCT05967351

Respiratory Functions, Thoracoabdominal Movements and Exercise Capacity in Neuromuscular Diseases

NCT ID: NCT06756633

This clinical trial, titled "Investigation of Respiratory Functions, Thoracoabdominal Movements, and Exercise Capacity in Neuromuscular Diseases," is designed to understand how certain neuromuscula...

NS-050/NCNP-03 in Boys With DMD (Meteor50)

NCT ID: NCT06053814

The NS-050/NCNP-03 trial, also known as Meteor50, is a study aimed at finding out if a new treatment called NS-050/NCNP-03 can help boys with Duchenne Muscular Dystrophy (DMD). This trial is lookin...

Evaluation of Brain Dysfunction in Patients with Duchene Muscular Dystrophy

NCT ID: NCT06732011

This clinical trial is focused on understanding how Duchenne Muscular Dystrophy (DMD) affects the brain and overall mental health of male patients aged 18 to 74. The researchers want to explore how...

A Study on Safety and Effectiveness of Long-term Treatment With Vamorolone in Boys With Duchenne Muscular Dystrophy

NCT ID: NCT06713135

This clinical trial is studying the long-term safety and effectiveness of a medication called vamorolone in boys diagnosed with Duchenne Muscular Dystrophy (DMD). DMD is a muscle-wasting condition ...

The U.K. NorthStar Clinical Network

NCT ID: NCT06711692

The U.K. NorthStar Clinical Network is a study aimed at understanding how Duchenne Muscular Dystrophy (DMD) affects individuals over time. This study will include children and adults in the United ...

FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases

NCT ID: NCT06539169

The FLOWER trial is a nationwide study that aims to gather important information about rare diseases, such as Alpha-Thalassemia, Beta-Thalassemia, and many others. This study is completely virtual,...

phenotypeS in Non Ambulant Duchenne Muscular Dystrophy

NCT ID: NCT06366815

This clinical trial is looking at boys with Duchenne Muscular Dystrophy (DMD) who can no longer walk independently. The main goal is to gather information about how this condition affects their mot...

A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical Practice

NCT ID: NCT06606340

Wearable Technology to Evaluate Hyperglycemia and HRV in DMD - Longitudinal Aim

NCT ID: NCT06093100

This clinical trial is exploring how wearable technology can help us understand the relationship between glucose levels and heart health in boys with Duchenne Muscular Dystrophy (DMD). DMD is a ser...