Clinical Trials for Hemophilia B

A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B

NCT ID: NCT06379789

This clinical trial is studying a new treatment called REGV131-LNP1265 for people with Hemophilia B, a genetic condition that prevents blood from clotting properly. The goal is to see if this treat...

Long-term Follow-up Study of Male Adults With Hemophilia B Previously Treated With Etranacogene Dezaparvovec (CSL222)

NCT ID: NCT05962398

A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B)

NCT ID: NCT06349473

This clinical trial is studying a new treatment called SR604 to see how safe it is and how well it works for people with severe Hemophilia A or Hemophilia B, as well as healthy participants. The tr...

Study of the Safety, Pharmacodynamics and Efficacy of ANB-002 in Patients With Hemophilia B (SAFRAN)

NCT ID: NCT06120582

The SAFRAN clinical trial is studying a new treatment called ANB-002 for men with Hemophilia B, a genetic condition that affects blood clotting. This research aims to understand how safe the treatm...

An Open-Label, Comparative Study of the Efficacy, Safety and Pharmacodynamics of Single Dose of ANB-002 in Patients With Hemophilia B

NCT ID: NCT06700096

This clinical trial is studying a new treatment called ANB-002 for men with hemophilia B, a condition where the blood doesn’t clot properly. The goal is to see if a single dose of ANB-002 is as eff...

Needs Assessment of Knowledge, Beliefs, and Attitudes of Patients With Hemophilia B About Gene Therapy

NCT ID: NCT05044845

This clinical trial is focused on understanding what patients with hemophilia B know, believe, and feel about gene therapy, which is a new treatment option that could greatly improve their health. ...

Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs)

NCT ID: NCT06003387

This clinical trial is studying a new gene therapy called CSL222 (Etranacogene Dezaparvovec) for adults with Hemophilia B, a condition that affects blood clotting and can lead to excessive bleeding...

Baby Detect : Genomic Newborn Screening

NCT ID: NCT05687474

The Baby Detect trial is studying a new way to screen newborns for serious genetic conditions that can be treated early. By using a simple blood test from babies within their first 28 days of life,...

Liver Biopsy Following Gene Therapy For Hemophilia

NCT ID: NCT05932914

This clinical trial is studying the long-term effects of a specific type of gene therapy on the liver in adults with hemophilia A or hemophilia B. The researchers will collect liver tissue samples ...

Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

NCT ID: NCT05568719

This clinical trial is looking at the long-term safety and effectiveness of two treatments, giroctocogene fitelparvovec and fidanacogene elaparvovec, for men with hemophilia A and B, respectively. ...

Early Check: Expanded Screening in Newborns

NCT ID: NCT03655223

ATHNdataset Registry

NCT ID: NCT06820515

BeCoMe-9: a Clinical Study of BE-101 for the Treatment of Adults with Moderately Severe or Severe Hemophilia B

NCT ID: NCT06611436

The BeCoMe-9 clinical trial is studying a new treatment called BE-101 for adults with moderately severe or severe Hemophilia B, a condition where the blood doesn’t clot properly due to a lack of a ...

Patient Interview Study to Explore the Impact of Gene Therapy in Hemophilia A & B

NCT ID: NCT06634836

This clinical trial is designed to understand the experiences of patients with hemophilia A and B who have received gene therapy. The researchers want to learn how this treatment has affected their...

Gene Therapy for Hemophilia B Patients Aged 12-18 Years Old

NCT ID: NCT05709288

This clinical trial is studying a new gene therapy called BBM-H901 for young boys aged 12 to 18 years who have hemophilia B, a condition that affects blood clotting. The goal of the study is to see...

The Efficacy and Safety of ZS801 in Chinese Hemophilia B Patients.

NCT ID: NCT05630651

This clinical trial is studying a new treatment called ZS801 for men with hemophilia B, a condition where the blood does not clot properly. The trial aims to find out how safe and effective a singl...

A Study to Evaluate the Safety and Efficacy of ZS801 in Adult Hemophilia B Patients

NCT ID: NCT05641610

This clinical trial is studying a new treatment called ZS801 for adults with hemophilia B, a condition where the blood doesn't clot properly. The trial aims to find out if ZS801 is safe and effecti...

Safety and Tolerability of VGB-R04 in Patients With Haemophilia B

NCT ID: NCT05152732

This clinical trial is investigating a new treatment called VGB-R04 for men with Hemophilia B, a condition that affects blood clotting. The study aims to determine how safe the treatment is and how...

A Trial That Evaluates Disease Characteristics in Hemophilia B Adult Male Participants Receiving Prophylaxis With Standard of Care Factor IX Protein (FIX) Replacement Therapy

NCT ID: NCT05568459

This clinical trial is studying how men with Hemophilia B manage their condition while receiving regular treatment with factor IX (FIX) replacement therapy. The goal is to collect information over ...

Synovial Proliferation on Routine Ultrasound: Active or Inactive?

NCT ID: NCT06809972

This clinical trial is investigating a condition called subclinical synovial proliferation in patients with haemophilia, which means that some patients may have hidden inflammation in their joints ...