Clinical Trials for Myotonic Dystrophy 1

Safety, Tolerability, PK, and PD Study of PGN-EDODM1 in Participants With Myotonic Dystrophy Type 1

NCT ID: NCT06204809

This clinical trial is studying a new treatment called PGN-EDODM1 for people with Myotonic Dystrophy Type 1 (DM1). The main goal is to see how safe the treatment is and how well people tolerate it ...

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

NCT ID: NCT03981575

The clinical trial titled "Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)" is investigating myotonic dystrophy type 1 (DM1), a genetic condition that affects muscle ...

Global Open-Label Extension Study of Del-desiran for the Treatment of DM1

NCT ID: NCT07008469

This clinical trial is studying a treatment called Del-desiran for people with Myotonic Dystrophy Type 1 (DM1), a genetic condition that affects muscle function and can lead to weakness and other h...

Global Study of Del-desiran for the Treatment of DM1

NCT ID: NCT06411288

This clinical trial is studying a new treatment called del-desiran for people with Myotonic Dystrophy Type 1 (DM1), a genetic condition that affects muscles and can cause weakness and stiffness. Th...

A Clinical Study of PGN-EDODM1 in People With Myotonic Dystrophy Type 1

NCT ID: NCT06667453

This clinical trial is studying a new medicine called PGN-EDODM1 to see how safe it is and how well it works for people with Myotonic Dystrophy Type 1 (DM1). Myotonic dystrophy is a genetic conditi...

Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next Study

NCT ID: NCT05982119

The ActiLiège Next study is looking to learn more about certain muscle disorders, including Duchenne Muscular Dystrophy (DMD), Fascioscapulohumeral Muscular Dystrophy (FSHD), Myotonic Dystrophy 1, ...

Study of ARO-DM1 in Subjects With Type 1 Myotonic Dystrophy

NCT ID: NCT06138743

This clinical trial is studying a new treatment called ARO-DM1 for people with Type 1 Myotonic Dystrophy (DM1), a genetic condition that affects muscle function. The trial is in its early stages an...

Study of ATX-01 in Participants With DM1

NCT ID: NCT06300307

This clinical trial is studying a new treatment called ATX-01 for people with myotonic dystrophy type 1 (DM1). The main goal is to find out if ATX-01 is safe and how well people can tolerate it. Pa...

Myotonic Dystrophy Family Registry

NCT ID: NCT02398786

The Myotonic Dystrophy Family Registry (MDFR) is an online program designed to gather information about myotonic dystrophy, a genetic condition that affects muscle function. By collecting data from...

Profile of Dysphagia in Myotonic Dystrophy Type 1 (DM1)

NCT ID: NCT05865483

This clinical trial, called the "Profile of Dysphagia in Myotonic Dystrophy Type 1," is focused on understanding swallowing difficulties, known as dysphagia, in people with myotonic dystrophy type ...

Myotonic Dystrophy Type 1 Congenital and Juvenile Form: From Diagnosis to Rehabilitation [MDCJ-NeuBeRe]

NCT ID: NCT06378216

The clinical trial titled "Myotonic Dystrophy Type 1 Congenital and Juvenile Form: From Diagnosis to Rehabilitation" aims to better understand how myotonic dystrophy affects children and young peop...

Evaluation of the Efficacy and Safety of Metformin in the Myotonic Dystrophy Type 1 (Steinert's Disease)

NCT ID: NCT05532813

This clinical trial is studying the effects of a medication called metformin on patients with Myotonic Dystrophy Type 1 (also known as Steinert's Disease). The researchers believe that metformin co...

A Multicenter Phenotype-Genotype Analysis of DM1 Patients in China

NCT ID: NCT06101940

Home-based Training and Supplementation in DM1 Patients

NCT ID: NCT05848830

This clinical trial is exploring how home-based exercise training, combined with a special supplement, can help improve the health and quality of life for people with myotonic dystrophy type 1 (DM1...