Clinical Trials for Duchenne Muscular Dystrophy (DMD)

Fear of Falling in Muscular Dystrophy

NCT ID: NCT07129954

This clinical trial is looking at the fear of falling in people with muscular dystrophy, a group of conditions that cause muscle weakness. The study aims to find out how common this fear is, how it...

The Baby Duchenne Study: Characterizing Developmental and Clinical Outcomes in the First Three Years in Children With Duchenne Muscular Dystrophy

NCT ID: NCT07092540

The Baby Duchenne Study is a research project that aims to learn more about how Duchenne muscular dystrophy (DMD) affects very young boys from birth up to three years old. DMD is a genetic conditio...

The Effect of Dual-tasking Program on Cognitive and Physical Functions and Independence in Activities of Daily Living in Children With Duchenne Muscular Dystrophy: A Single-blind Randomized Controlled Trial

NCT ID: NCT06887491

A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44

NCT ID: NCT07037862

This clinical trial is studying a new medicine called ENTR-601-44 for boys and young men with Duchenne muscular dystrophy (DMD), a rare genetic condition that weakens muscles over time. The goal is...

The Effect of Virtual Reality Applications on Upper Extremity Functions in Patients With Duchenne Muscular Dystrophy

NCT ID: NCT07039799

This clinical trial is studying whether using virtual reality (VR) games can help improve arm and hand function in boys and young men with Duchenne Muscular Dystrophy (DMD), a condition that causes...

A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45

NCT ID: NCT07038824

This clinical trial is studying a new medicine called ENTR-601-45 for boys and young men with Duchenne muscular dystrophy (DMD), a rare genetic muscle disease. The goal is to see if this medicine i...

A Long-term Follow-up Study for Participants That Completed the SAT-3247-CL-101 Study

NCT ID: NCT06867107

This clinical trial is looking at the long-term effects of a medication called SAT-3247 for boys who have Duchenne Muscular Dystrophy (DMD). If you or your child participated in a previous study ca...

DMD Voice: Qualitative Interviews With Patients and Caregivers

NCT ID: NCT06925269

The DMD Voice study is a research project aimed at understanding how Duchenne Muscular Dystrophy (DMD) affects the daily lives of boys with the condition and their caregivers. Through one-on-one in...

Evaluation of the Safety, Tolerability, and Efficacy of LE051 in Patients With Duchenne Muscular Dystrophy

NCT ID: NCT06900049

This clinical trial is studying a new treatment called LE051 for boys with Duchenne Muscular Dystrophy (DMD), a genetic condition that causes muscle weakness. The goal is to see if LE051 is safe an...

Evaluation of the Safety and Efficacy of BBM-D101 to Treat Patients with Duchenne Muscular Dystrophy

NCT ID: NCT06641895

This clinical trial is looking at a new treatment called BBM-D101 for boys with Duchenne Muscular Dystrophy (DMD), a genetic condition that causes muscle weakness. The main goals of the study are t...

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

NCT ID: NCT06839469

This clinical trial is looking to understand how walking patterns can help us learn more about the severity of two rare childhood muscle disorders: Spinal Muscular Atrophy Type 3 and Duchenne Muscu...

Follow-up of NIV At Home in Patients with Duchenne Muscular Dystrophy

NCT ID: NCT06773988

This clinical trial is exploring the use of a sleep study conducted at home to monitor the effectiveness of non-invasive ventilation (NIV) in patients with Duchenne Muscular Dystrophy (DMD). The re...

Research on the Relationship Between Scoliosis, Pain, Quality of Life, and Trunk Muscle Compensation Patterns Among Patients with Duchenne Muscular Dystrophy.

NCT ID: NCT06755138

This clinical trial is investigating how trunk muscle movements in patients with Duchenne Muscular Dystrophy (DMD) relate to scoliosis (curvature of the spine), pain, and overall quality of life. B...

Nutritional Status and Therapy in DMD Patients

NCT ID: NCT06682585

This clinical trial is looking at how a special diet can help improve the health and abilities of young boys with Duchenne Muscular Dystrophy (DMD), a condition that affects muscle strength. The st...

Effects of Lumbopelvic Stabilization-based Physiotherapy and Rehabilitation Training in Duchenne Muscular Dystrophy

NCT ID: NCT06643923

This clinical trial is looking at how effective a specific type of exercise therapy called lumbopelvic stabilization is for children with Duchenne Muscular Dystrophy (DMD) who also have issues with...